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Clinical Trials Sponsored by Silence Therapeutics plc
Total 662 results
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Silence Therapeutics plcCompletedNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic Syndrome | Very-Low Risk Myelodysplastic SyndromeThailand, Israel, Jordan, United Kingdom, Germany, Italy, Malaysia
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Silence Therapeutics plcCompletedHealthy VolunteersUnited Kingdom
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Silence Therapeutics plcRecruitingPolycythemia VeraUnited States, Australia, Malaysia, Bulgaria, Poland
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Silence Therapeutics plcActive, not recruitingCardiovascular Diseases | Atherosclerosis | Lipoprotein(a)Australia, Czechia, Denmark, Netherlands, Slovakia, South Africa, United Kingdom
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Silence Therapeutics plcWithdrawnNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic SyndromeUnited Kingdom, Bulgaria
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Silence Therapeutics plcMedpace, Inc.CompletedDyslipidemias | Hyperlipidemias | Elevated Lp(a)United States, Australia, United Kingdom, Netherlands
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Silence Therapeutics GmbHCompleted
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Celsus Therapeutics PLCTerminatedAtopic DermatitisIsrael
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e-Therapeutics PLCCompleted
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e-Therapeutics PLCCompletedMajor Depressive DisorderUnited Kingdom
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e-Therapeutics PLCCompletedCancer | Pharmacokinetics | Tolerability | SafetyUnited Kingdom
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e-Therapeutics PLCUnknownHepatocellular Carcinoma | Pancreatic CancerGermany, Poland, Spain, United Kingdom
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PTC TherapeuticsAxio Research. LLCCompleted
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsActive, not recruitingAADC DeficiencyUnited States, Israel, Taiwan
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedLeiomyosarcomaUnited States
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompleted
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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PTC TherapeuticsWithdrawnDuchenne Muscular Dystrophy
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PTC TherapeuticsCompletedHepatic ImpairmentUnited States
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PTC TherapeuticsCompletedHealthy VolunteersUnited States
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PTC TherapeuticsNot yet recruitingPhenylketonuriaUnited States
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PTC TherapeuticsRecruitingHuntington DiseaseAustralia, France, Germany, Netherlands, United Kingdom, Spain, Austria, Canada, Italy, New Zealand
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PYC TherapeuticsRecruitingRetinal Dystrophy | PRPF31 Mutationassociated Retinal Dystrophy | RP11United States
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PTC TherapeuticsActive, not recruitingLeiomyosarcomaUnited States, United Kingdom, France, Italy, Netherlands, Spain, Australia, Canada, Brazil, Germany, Hungary, Poland
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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PTC TherapeuticsCompletedAniridiaUnited States, Canada
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PTC TherapeuticsTerminatedLeukemia, Myeloid, Acute | AMLUnited States
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PTC TherapeuticsCompletedAmyotrophic Lateral SclerosisUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedRenal ImpairmentUnited States
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PYC TherapeuticsNot yet recruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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PTC TherapeuticsRecruitingA Study to Evaluate the Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)Huntington DiseaseUnited States, Austria, Spain, United Kingdom, Australia, France, Germany, Netherlands, Italy, New Zealand, Canada
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PTC TherapeuticsCompletedNonsene Mutation Duchenne Muscular DystrophyUnited States
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PTC TherapeuticsEnrolling by invitationInherited Mitochondrial DiseaseUnited States, France, Spain, United Kingdom, Italy, Poland, Japan
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PTC TherapeuticsActive, not recruitingAmyotrophic Lateral SclerosisUnited States, Belgium, Spain, Australia, Germany, Italy, Czechia, France, Netherlands, Japan, Poland, Argentina, Sweden
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan