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Search clinical trials for: Compassionate Use
Total 20949 results
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French Innovative Leukemia OrganisationAcute Leukemia French AssociationNot yet recruiting
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Hunan Province Tumor HospitalRecruitingAdvanced Solid Tumors or LymphomasChina
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NWTraumatherapiesWorld Health OrganizationNot yet recruitingTrauma, Nervous SystemUnited States
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Children's Mercy Hospital Kansas CityRecruitingGastroesophageal Reflux | GERD | GastroparesisUnited States
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Melanoma Institute AustraliaNovartisRecruiting
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Sequenom, Inc.RecruitingNon-hematologic CancerUnited States
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National Institute of Diabetes and Digestive and...RecruitingDiabetes | Hyperlipidemia | LipodystrophyUnited States
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Daiichi SankyoAstraZenecaAvailableAdvanced Non-Small Cell Lung Cancer | Metastatic Non Small Cell Lung CancerUnited States
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AbbVieAvailableAcute Spinal Cord Injury (SCI) | Acute Ischemic Stroke
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AbbVieAvailableMyelofibrosis | Lymphoblastic Lymphoma | Acute Lymphocytic Leukemia (ALL)United States
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AbbVieAvailableMultiple Myeloma | Non-Hodgkin's Lymphoma | Amyloidosis | Chronic Lymphocytic Leukemia (CLL) | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Plasma Cell Leukemia
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AbbVieAvailableNon-Small Cell Lung Cancer (NSCLC)Australia, Hong Kong, Israel, United States, Germany
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Epizyme, Inc.WEP ClinicalNo longer availableEpithelioid Sarcoma
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SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
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SpringWorks Therapeutics, Inc.AvailableDesmoid Tumor | NOTCH Gene Mutation Positive Tumors
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Ultragenyx Pharmaceutical IncAvailableGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)
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Ultragenyx Pharmaceutical IncAvailableSly Syndrome | Mucopolysaccharidosis VII | MPS VII
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Ultragenyx Pharmaceutical IncKyowa Kirin Co., Ltd.AvailableX-linked Hypophosphatemia | Tumor-Induced Osteomalacia
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National Institute of Diabetes and Digestive and...Active, not recruitingDiabetes | Hyperlipidemia | LipodystrophyUnited States
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Novo Nordisk A/SAvailableCongenital HaemophiliaUnited States, Bulgaria, Sweden
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Boston Children's HospitalSterileCare Inc.Enrolling by invitationCentral Line Complication | Central Line-associated Bloodstream Infection (CLABSI)United States
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Novartis PharmaceuticalsAvailable
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Novartis PharmaceuticalsAvailableSickle Cell Disease
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Novartis PharmaceuticalsAvailable
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Marinus PharmaceuticalsNo longer availableCDKL5 Disorder
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Merus N.V.AvailableRenal Cell Carcinoma | Breast Cancer | Head and Neck Cancer | Colorectal Cancer | Pancreatic Cancer | Prostate Cancer | Non Small Cell Lung Cancer | Cholangiocarcinoma | Solid Tumor, Unspecified, Adult | Unknown Primary Tumors | NRG1 Fusion
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New Mexico Cancer Care AllianceNo longer available
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University of NebraskaChildren's Hospital and Medical Center, Omaha, NebraskaApproved for marketingTotal Parenteral Nutrition-Induced CholestasisUnited States
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Endospan Ltd.CompletedAortic Arch AneurysmSwitzerland, Italy, New Zealand
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University of California, San FranciscoNo longer availableLeishmaniasis, Cutaneous | Leishmaniasis, MucocutaneousUnited States
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PfizerMerck KGaA, Darmstadt, Germany; Ono Pharmaceutical Co. Ltd; Pierre Fabre MedicamentCompletedBRAF V600E-mutant Metastatic Colorectal CancerUnited States, Spain, Korea, Republic of, United Kingdom, Australia, Czechia, Taiwan, Belgium, France, Hungary, Canada, Japan, Russian Federation, Netherlands, Israel, Germany, Turkey, Austria, Brazil, Poland, Italy, Argentina, Chile, Denmar... and more
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Ridgeback Biotherapeutics, LPInstitut National de Recherche Biomédicale. Kinshasa, République Démocratique...AvailableHemorrhagic Fever, EbolaCongo, The Democratic Republic of the, Sierra Leone
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ViiV HealthcareAvailable
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PfizerIn Expanded Access, treating physicians are the SponsorsAvailable
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GlaxoSmithKlineAvailable
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Regeneron PharmaceuticalsAvailableBullous Pemphigoid | Pediatric Asthma | Pediatric Eosinophilic Esophagitis (EoE) | Pediatric and Adolescent Chronic Rhinosinusitis With Nasal Polyps (CRSwNP)
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Eli Lilly and CompanyNo longer availableChronic Atypical Neutrophilic Dermatosis With Lipodystrophy and Elevated Temperature (CANDLE) | Juvenile Dermatomyositis (JDM) | Stimulator of Interferon Genes (STING)-Associated Vasculopathy With Onset During Infancy (SAVI) | Aicardi-Goutières Syndrome (AGS)United States, United Kingdom
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Regeneron PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria (PNH) | CD55-deficient Protein-losing Enteropathy (PLE) | CD59 Deficiency
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Eli Lilly and CompanyNo longer availableGeneralized Anxiety Disorder | Fibromyalgia | Major Depressive Disorder | Diabetic Peripheral Neuropathic PainAustralia
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Regeneron PharmaceuticalsAvailablePartial Lipodystrophy | Generalized Lipodystrophy | Monogenic Obesity Due to LEP or LEPR Loss of Function
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Novartis PharmaceuticalsAvailable
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Regeneron PharmaceuticalsSanofiAvailableBullous Pemphigoid
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Mirum Pharmaceuticals, Inc.Children's Hospital Medical Center, CincinnatiCompletedCholestasis | Peroxisomal Disorders | Adrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's DiseaseUnited States
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Regeneron PharmaceuticalsNo longer available
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Regeneron PharmaceuticalsAvailableParoxysmal Nocturnal Hemoglobinuria
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Invivyd, Inc.In Expanded Access, treating physicians are the SponsorsNo longer available