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Search clinical trials for: Cystinosis
Total 41 results
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Nacuity Pharmaceuticals, Inc.Recruiting
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Cystinose StiftungCystinosis Research Network; Leben eben! Cystinose-Selbsthilfe e.V.Recruiting
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Institut National de la Santé Et de la Recherche...Recruiting
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Cystinose StiftungScreening Laboratory Hannover; Pediatry Kastanienhof Koeln; Medical Genetics... and other collaboratorsRecruitingCystinosis | Primary HyperoxaluriaGermany
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Centre Hospitalier Régional de la CitadelleSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Universitaire... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Assistance Publique - Hôpitaux de ParisCystinosis Research FoundationRecruiting
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Alice BertainaCalifornia Institute for Regenerative Medicine (CIRM)RecruitingCKD Stage 4 | Cystinosis | FSGS | SLE Nephritis | SIODUnited States
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Stanford UniversityRecruiting
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Hospices Civils de LyonRecruiting
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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National Human Genome Research Institute (NHGRI)Recruiting
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Recordati Rare DiseasesCompletedCystinosisBelgium, France, United Kingdom, Germany, Italy
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University of California, San DiegoEnrolling by invitationCystinosisUnited States
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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University of California, San DiegoCalifornia Institute for Regenerative Medicine (CIRM); Cystinosis Research...Active, not recruiting
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CENTOGENE GmbH RostockWithdrawnHypophosphatemia | Photophobia | Renal Fanconi SyndromeGermany, India, Sri Lanka
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Hospices Civils de LyonCompleted
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Chiesi SA/NVEnrolling by invitationNephropathic CystinosisBelgium
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Eloxx Pharmaceuticals, Inc.TerminatedGenetic Disease | Cystinosis | Nonsense MutationCanada
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, United Kingdom, Belgium, Italy, Netherlands
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
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Horizon Pharma USA, Inc.Completed
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National Human Genome Research Institute (NHGRI)Withdrawn
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National Institute of Diabetes and Digestive and...Completed
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National Institute of Dental and Craniofacial Research...CompletedDiabetes Mellitus | Head and Neck Neoplasms | Dental Caries | Sarcoidosis | Cystinosis | Sjorgren's SyndromeUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedPseudotumor Cerebri | CystinosisUnited States
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
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Horizon Pharma USA, Inc.Completed
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The Eye Center and The Eye Foundation for Research...CompletedNephropathic Cyctinosis | Corneal Cystine Crystals
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Universitaire Ziekenhuizen KU LeuvenCompleted
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FDA Office of Orphan Products DevelopmentLeadiant Biosciences, Inc.Completed
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National Eye Institute (NEI)Completed
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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University of California, San DiegoRaptor Pharmaceuticals Corp.CompletedCystinosis | Nephropathic CystinosisUnited States
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University of Sao PauloFundação de Amparo à Pesquisa do Estado de São PauloCompletedRenal Disease | Cystinosis
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Centre Hospitalier Universitaire de NiceCompleted
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National Eye Institute (NEI)CompletedCystinosisUnited States
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National Center for Research Resources (NCRR)Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCystinosisUnited States
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis