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Search clinical trials for: GENETIC DISEASE
Total 379169 results
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Ray Therapeutics, Inc.The Vision Research and Assessment Institute (VRAI)RecruitingRetinitis PigmentosaUnited States
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Clinic for Special ChildrenRecruitingMyopathy | Myopathy; Hereditary | Myopathies, Nemaline | TNNT1-associated Myopathy | Infantile-onset Nemaline Rod Myopathy | Myopathy, Rod | Amish Nemaline Myopathy | Nemaline Myopathy 5 | NEM5 | Genetic Muscle Disease | Recessive Hereditary Disorder (Autosomal) | ANMUnited States
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingPain | Sickle Cell Disease
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Apollo Therapeutics LtdNot yet recruitingMyelodysplastic Syndrome With Excess Blasts | Acute Myeloid Leukemia, in Relapse | Acute Myeloid Leukemia Refractory | Myelodysplastic Syndrome Acute Myeloid Leukemia
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Enzyre B.V.Indiana Hemophilia & Thrombosis CenterNot yet recruiting
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan
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SensorionNot yet recruitingOtorhinolaryngologic Diseases | Ear Diseases | Hearing Disorders | Deafness | Hearing Loss, Sensorineural | Congenital Deafness | DFNB9 | OTOF Gene MutationFrance
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Hospices Civils de LyonNot yet recruiting
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Massachusetts General Hospitaln-Lorem FoundationNot yet recruiting
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Centre Hospitalier Universitaire de la RéunionRecruiting
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Eilean TherapeuticsNot yet recruiting
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Medical University of WarsawRecruitingThyroid Eye Disease | Ophthalmopathy | Orbitopathy, GravesPoland
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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Harmony Biosciences, LLCRecruiting
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell DiseaseUnited States
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Instituto de Investigación Hospital Universitario...Recruiting
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University of Kansas Medical CenterNot yet recruitingCystic FibrosisUnited States
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Children's Hospital of PhiladelphiaNot yet recruiting
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Dan BingNot yet recruitingCongenital Hearing Loss | Congenital Deafness
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AstraZenecaRecruiting
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National Cancer Institute (NCI)Not yet recruitingLeukemia, Lymphocytic, Chronic, B-Cell | B-Cell Chronic Lymphocytic Leukemia | B-Lymphocytic Leukemia, ChronicUnited States
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Editas Medicine, Inc.Not yet recruitingSickle Cell Disease | Hemoglobinopathies | Transfusion-dependent Beta-Thalassemia
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Beijing Tiantan HospitalWest China Hospital; The First Affiliated Hospital of Zhengzhou University; Capital... and other collaboratorsRecruiting
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OctapharmaNot yet recruiting
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University Hospital, ToulouseNot yet recruiting
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West China HospitalNot yet recruitingArtificial Intelligence | Atopic Dermatitis
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Chang Gung UniversityRecruiting
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University of MalagaNot yet recruitingMuscular Dystrophy | Duchenne Muscular Dystrophy | Becker Muscular DystrophySpain
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Fondazione SISA (Societa Italiana per lo Studio...RecruitingFamilial Hypercholesterolemia | Genetic DisorderItaly
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Seoul National University HospitalNot yet recruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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Technoderma Medicines Inc.Therapeutics, Inc.Not yet recruiting
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AstraZenecaNot yet recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform
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Cliniques universitaires Saint-Luc- Université...RecruitingRare Diseases | Inborn Errors of MetabolismBelgium
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Xuanwu Hospital, BeijingNot yet recruiting
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Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis, Transthyretin-Related | Asymptomatic Carrier StateFrance
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Peking University Third HospitalRecruitingThyroid Eye DiseaseChina
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Children's National Research InstituteThe Hospital for Sick Children; Ann & Robert H Lurie Children's Hospital of... and other collaboratorsRecruitingSickle Cell DiseaseUnited States
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Rigshospitalet, DenmarkNot yet recruitingInfertilityDenmark
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Azienda Ospedaliera Universitaria Integrata VeronaAbbott Medical DevicesRecruitingHeart Failure | Left Ventricular Dysfunction | Idiopathic Dilated CardiomyopathyItaly
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Assistance Publique - Hôpitaux de ParisVaincre la MucoviscidoseNot yet recruiting
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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University Hospital, Basel, SwitzerlandNot yet recruitingThoracic Aortic Aneurysm | Acute Aortic DissectionSwitzerland
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingNoonan Syndrome | Costello Syndrome | RASopathy | Cardio-Facio-Cutaneous SyndromeItaly
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CHU de ReimsRecruitingPrimary Immunodeficiency | Common Variable Immunodeficiency | Igg Subclass Deficiency | Selective IgM DeficiencyFrance
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SensorionNot yet recruitingSensorineural Hearing Loss, BilateralFrance
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Hasan Kalyoncu UniversityRecruitingDown SyndromeTurkey
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PfizerNot yet recruitingSkin Diseases | Immune System Diseases | Dermatitis | Eczema | Dermatitis, Atopic | Janus Kinase Inhibitors
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University Hospital, BonnSwedish Orphan BiovitrumRecruitingHaemophilia A | Synovitis | Hemophilia Arthropathy | SonographyGermany