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Search clinical trials for: Homozygous Sitosterolemia
Total 130 results
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Organon and CoCompletedHeart Disease | Lipid Metabolism, Inborn Errors
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Organon and CoBayerCompletedHypercholesterolemia | Familial Hypercholesterolemia | Homozygous Sitosterolemia
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Organon and CoCompletedHeart Disease | Lipid Metabolism, Inborn Errors
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Organon and CoBayerCompletedHypercholesterolemia | Familial Hypercholesterolemia | Homozygous Sitosterolemia
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Metabolism, Inborn ErrorsUnited States
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AmgenNot yet recruitingAdvanced Gastrointestinal, Biliary Tract, and Pancreatic CancersUnited States
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AmgenNot yet recruitingNon-small Cell Lung Cancer | Thoracic Tumors
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
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Regeneron PharmaceuticalsNot yet recruitingNonalcoholic Steatohepatitis (NASH) | Nonalcoholic Fatty Liver Disease (NAFLD) | Genetic Risk Factor
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Beijing Suncadia Pharmaceuticals Co., LtdNot yet recruitingHomozygous Familial Hypercholesterolemia
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Novartis PharmaceuticalsRecruitingHeterozygous or Homozygous Familial HypercholesterolemiaNetherlands, Israel, Hungary, Italy, Germany, Spain, France, Norway, South Africa, Turkey, United Kingdom, Canada, Switzerland, Brazil, Lebanon, Slovenia, United States, Russian Federation, Taiwan
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Shenzhen People's HospitalRecruitingEvaluate the Efficacy and Safety of IBI306 in Subjects With Homozygous Familial HypercholesterolemiaLipid Metabolism Disorders | Familial Hypercholesterolemia - Homozygous | Proprotein Convertase Subtilisin/Kexin 9China
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Instituto de Investigación Sanitaria AragónHospital Clínico Universitario Lozano Blesa; FEIRACO LACTEOS SLRecruiting
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University of PennsylvaniaUniversity of Amsterdam; University of Cape Town; University of Witwatersrand...RecruitingHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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Institut Investigacio Sanitaria Pere VirgiliRecruitingFamilial Hypercholesterolemia | Familial Hypercholesterolemia - Homozygous | Familial Hypercholesterolemia - HeterozygousSpain
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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Icahn School of Medicine at Mount SinaiRecruiting
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The Rogosin InstituteRecruitingHomozygous Familial HypercholesterolemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHomozygous Familial HypercholesterolemicUnited States
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HomozygousGreece, Lebanon, Turkey, France, Canada, Malaysia, Netherlands, United States
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Novartis PharmaceuticalsCompletedElevated Cholesterol | Homozygous Familial Hypercholesterolemia | Heterozygous Familial Hypercholesterolemia | ASCVDUnited States, Canada, Czechia, Denmark, Germany, Hungary, Netherlands, Poland, South Africa, Spain, Sweden, Ukraine, United Kingdom
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, United Kingdom, Belgium, Netherlands, France, Denmark, Israel, New Zealand, Australia, Ireland, Sweden, Canada, Germany, Poland, Switzerland, Italy, Austria, Hungary, Greece, Norway
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BayerMerck Sharp & Dohme LLCTerminatedEarly Signs of Efficacy Study With Riociguat in Adult Homozygous Delta F508 Cystic Fibrosis PatientsCystic FibrosisGermany, United States, France, Canada, Belgium, Netherlands, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompleted
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Daniel GaudetUltragenyx Pharmaceutical IncActive, not recruitingSafety and Effectiveness of Evinacumab for the Treatment of Homozygous Familial HypercholesterolemiaHomozygous Familial HypercholesterolemiaCanada
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Innovent Biologics (Suzhou) Co. Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Amryt PharmaActive, not recruitingHomozygous Familial Hypercholesterolaemia (HoFH)Germany, Israel, Italy, Saudi Arabia, Spain, Tunisia
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LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
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Centre Leon BerardCompletedHead and Neck Cancer | Metastatic Cancer | Advanced CancerFrance
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CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
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Novartis PharmaceuticalsCompletedA Study of Inclisiran in Participants With Homozygous Familial Hypercholesterolemia (HoFH) (ORION-5)Homozygous Familial HypercholesterolemiaHong Kong, Israel, Russian Federation, Serbia, South Africa, Taiwan, Turkey, Ukraine
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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Vertex Pharmaceuticals IncorporatedCompleted
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Assistance Publique - Hôpitaux de ParisCompletedCystic Fibrosis | Homozygous F508del MutationFrance
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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Organon and CoTerminatedLipid Metabolism, Inborn Errors | Hypercholesterolemia, Familial
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Organon and CoCompleted
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Organon and CoCompletedHeart Disease | Lipid Metabolism, Inborn Errors
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Organon and CoCompletedPrimary Hypercholesterolemia | Homozygous Familial Hypercholesterolemia
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Organon and CoCompletedPrimary Hypercholesterolemia and Homozygous Familial Hypercholesterolemia (HoFH)