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Search clinical trials for: Lysosomal Disease Network
Total 380253 results
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Cystinose StiftungCystinosis Research Network; Leben eben! Cystinose-Selbsthilfe e.V.Recruiting
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SanofiRecruitingFabry DiseaseChina, Finland, Germany, Norway, United Kingdom, United States, Denmark, Austria, Greece, Romania, Argentina, Brazil, Canada, Japan, Mexico, Poland, Italy, France, Turkey, Australia, Switzerland
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University Health Network, TorontoUniversity of Colorado, Denver; Mayo Clinic; Icahn School of Medicine at Mount... and other collaboratorsRecruiting
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Wuerzburg University HospitalAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA); St George... and other collaboratorsRecruitingFabry Disease | Rare Diseases | Hypertrophic Cardiomyopathy | Fabry Disease, Cardiac VariantGermany
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State University of New York at BuffaloEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruiting
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGaucher Disease Type 1United States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Washington... and other collaboratorsRecruiting
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Late Onset Tay-Sachs DiseaseUnited States
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University Health Network, TorontoOzmosis Research Inc.Completed
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AVROBIOTerminatedGaucher DiseaseUnited States, Canada
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological Disorders... and other collaboratorsTerminatedMucopolysaccharidosis I | Cognitive DeclineUnited States
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Mandos LLCTerminatedNiemann-Pick Disease, Type CUnited States, Australia, United Kingdom, Turkey, Switzerland, Germany, New Zealand, Singapore, France
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Mandos LLCCompletedNiemann-Pick Disease, Type CUnited States, Australia, United Kingdom, Germany, France, New Zealand, Singapore, Spain, Turkey
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsTerminatedTay-Sachs Disease | Sandhoff Disease | GM1 Gangliosidoses | GM2 GangliosidosesUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosesUnited States
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Massachusetts General HospitalGenzyme, a Sanofi Company; Scott and White Hospital & ClinicTerminatedKidney Diseases | Genetic Diseases, X-Linked | End Stage Renal Disease | ESRD | Fabry Disease | Rare DiseasesUnited States
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Lundquist Institute for Biomedical Innovation at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosesUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type IUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedParkinson's Disease | Gaucher's DiseaseUnited States
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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Baylor Research InstituteNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Cognitive Decline | Hurler-Scheie SyndromeUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedNiemann-Pick Disease, Type CUnited States
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Children's Hospital Medical Center, CincinnatiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedWolman Disease | Cholesterol Ester Storage Disease | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2United States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedTay Sachs Disease | Sandhoff Disease | Late Onset Tay Sachs DiseaseUnited States
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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University of Colorado, DenverAmerican Diabetes Association; High Plains Research NetworkRecruiting
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Instituto de Investigación Biomédica de SalamancaSpanish Clinical Research Network - SCReN; Fundación Canaria de Investigación... and other collaboratorsRecruitingB-cell Lymphoma Recurrent | Refractory B-Cell LymphomaSpain
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University Health Network, TorontoNot yet recruiting
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Alvernia UniversityLehigh Valley Health NetworkNot yet recruiting
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McGill University Health Centre/Research Institute...The Hospital for Sick Children; Canadian Institutes of Health Research (CIHR); Unity Health Toronto and other collaboratorsNot yet recruiting
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Stanford UniversityNational Institute of Mental Health (NIMH)Not yet recruitingDepression | InsomniaUnited States
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University Health Network, TorontoNot yet recruitingSpontaneous Intracranial Hypotension
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University of California, DavisPediatric Emergency Care Applied Research NetworkNot yet recruitingBrain Injuries | Intracranial Hemorrhages | Diffuse Axonal Injury | Head Injury | Skull Fractures | Head Injury Trauma | Brain Injury Traumatic Mild | Brain Injuries, Acute | Head Injury With Intracranial Hemorrhage | Brain Injury Traumatic Focal With Loss of ConsciousnessUnited States
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University Health Network, TorontoCanadian Institutes of Health Research (CIHR); Ozmosis Research Inc.; Canadian...Not yet recruiting
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University of StellenboschUniversity College London Hospitals; University of Copenhagen; Imperial College... and other collaboratorsNot yet recruiting
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Axoltis PharmaACT4ALS networkNot yet recruiting
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Albert Einstein Healthcare NetworkThomas Jefferson University; National Institute on Deafness and Other Communication...Not yet recruiting
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University Health Network, TorontoNot yet recruiting
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Cardiff and Vale University Health BoardWelsh Value in Health Centre (WViHC); Centre for Healthcare Evaluation, Device...Not yet recruitingVascular Diseases | Surgery | Patient Engagement | Patient Satisfaction | Patient EmpowermentUnited Kingdom
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University Health Network, TorontoThe Hospital for Sick Children; Alberta Children's Hospital; British Columbia... and other collaboratorsNot yet recruiting
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Odense University HospitalAarhus University Hospital; University of Aarhus; University of Southern Denmark and other collaboratorsRecruitingChronic Pain | InsomniaDenmark
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University Health Network, TorontoNot yet recruitingStroke | Fatigue | Exercise | Modafinil
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Owlstone LtdRecruiting
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SanofiRecruitingHealthy Volunteers | Autoimmune DisorderUnited States
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Wake Forest University Health SciencesNational Cancer Institute (NCI)Not yet recruitingBreast Cancer | Colon CancerUnited States