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Search clinical trials for: Retinitis Pigmentosa GTPase Regulator (RPGR)
Total 1012 results
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Applied Genetic Technologies CorpNot yet recruiting
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MeiraGTx UK II LtdJanssen, LPActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Canada
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Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University; Henan Provincial People's HospitalRecruitingX-Linked Retinitis PigmentosaChina
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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University Hospital TuebingenRecruitingRetinitis PigmentosaGermany
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University of RochesterNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Retinal Dystrophies | Alcohol Use Disorder | Stargardt DiseaseUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Zhongmou TherapeuticsNot yet recruitingRetinitis PigmentosaChina
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ViGeneron GmbHRecruiting
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Mahidol UniversityNot yet recruitingRetinitis PigmentosaThailand
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University College, LondonNot yet recruiting
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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Zhongshan Ophthalmic Center, Sun Yat-sen UniversityNot yet recruitingGlaucoma | Diabetic Retinopathy | Age-related Macular Degeneration | Retinitis PigmentosaChina
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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University of Southern CaliforniaNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Ultrasound Therapy; Complications
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PT. Prodia Stem Cell IndonesiaRecruitingRetinitis PigmentosaIndonesia
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Eye & ENT Hospital of Fudan UniversityFudan UniversityRecruiting
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Power Life Sciences Inc.Not yet recruitingRetinitis Pigmentosa
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2C Tech CorpORA, Inc.Not yet recruitingRetinitis Pigmentosa
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Columbia UniversityNational Eye Institute (NEI); Universität Tübingen; Centre Hospitalier National...RecruitingRetinitis Pigmentosa | Best Vitelliform Macular DystrophyUnited States, Germany, France
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Peking University Third HospitalRecruitingSafety and Tolerability Study of Gene Editing Drug ZVS203e in Participants With Retinitis PigmentosaRetinitis PigmentosaChina
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Istituto Superiore di SanitàFondazione G.B. Bietti, IRCCS; Ospedale Pediatrico Bambin GesùRecruitingRetinitis Pigmentosa | Macular Dystrophy | Inherited Retinal DystrophyItaly
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SparingVisionRecruiting
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Indiana UniversityRecruitingPigmentary Retinopathy | Pentosan Polysulfate Sodium Maculopathy | Pigmentary Maculopathy | Toxic Maculopathy | Interstitial Cystitis, ChronicUnited States
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Jaeb Center for Health ResearchFoundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Inherited Retinal DegenerationUnited States, United Kingdom, France, Brazil, Canada, Finland, Israel, Mexico, Netherlands, Switzerland, Australia
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Johns Hopkins UniversityMayo Clinic; Medical University of Graz; Radboud University Medical Center; University... and other collaboratorsRecruitingRetinitis PigmentosaUnited States, Austria, Mexico, Netherlands, United Kingdom, Germany, Canada, Switzerland
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TC Erciyes UniversityRecruitingRetinitis PigmentosaTurkey
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Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States
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Kiora Pharmaceuticals, Inc.RecruitingRetinitis Pigmentosa | ChoroideremiaAustralia
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Barcelona Macula FoundationRecruitingRetinitis Pigmentosa | Choroideremia | Stargardt Disease 1 | Best Disease | Pattern Dystrophy of MaculaSpain
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Hospices Civils de LyonRecruitingPrimary Intestinal Hypocholesterolemia | Abetalipoproteinemia | Chylomicron Retention DiseaseFrance
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OcugenRecruitingRetinitis Pigmentosa | Leber Congenital AmaurosisUnited States
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The Foundation for Orthopaedics and Regenerative...RecruitingGlaucoma | Eye Diseases | Macular Degeneration | Diabetic Retinopathy | Retinitis Pigmentosa | Optic Atrophy | Traumatic Optic NeuropathyAntigua and Barbuda, Argentina, Mexico
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Mayo ClinicAstellas Pharma Inc; Casimir, LLCRecruitingMitochondrial Diseases | Mitochondrial Myopathies | Kearns-Sayre Syndrome | Mitochondrial DNA Mutation | Chronic Progressive External Ophthalmoplegia With MyopathyUnited States
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Ohio State UniversityNational Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingUsher Syndrome | Cochlear ImplantationUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingClassification, Functional Stratification and Biomarkers in Ciliopathy (CILLICORIRCM) (CILLICORIRCM)Ciliopathies | Bardet-Biedl Syndrome | Nephronophthisis | Senior-Loken Syndrome | Joubert Syndrome | Jeune SyndromeFrance
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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Oslo University HospitalRecruitingRetinitis Pigmentosa | Retinitis Pigmentosa 11Norway