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Search clinical trials for: Sandhoff Disease
Total 378636 results
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SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)RecruitingGangliosidoses | Galactosialidosis | Sialidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Morquio B Disease | Gm2-Gangliosidosis, Variant B1 | GM2 Activator DeficiencyGermany
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Tehran University of Medical SciencesMashhad University of Medical Sciences; Kashan University of Medical SciencesRecruitingEffects of Miglustat Therapy on Infantile Type of Sandhoff and Taysachs Diseases (EMTISTD) (EMTISTD)Supportive Care | GM2 GangliosidosisIran, Islamic Republic of
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Late Onset Tay-Sachs DiseaseUnited States
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National Human Genome Research Institute (NHGRI)RecruitingMyoclonus | Neurological Regression | Cherry Red Spot | Brain AtrophyUnited States
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IntraBio IncCompletedGM2 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Germany, Spain, United Kingdom
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Genzyme, a Sanofi CompanyActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States, Argentina, Czechia, Portugal, Russian Federation, Turkey, United Kingdom, Brazil, France, Germany, Italy, Japan, Spain
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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Azafaros A.G.Active, not recruitingGM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Brazil, France, Germany, Italy, United Kingdom
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Dr. Anupam SehgalTaysha Gene Therapies, Inc.; GlycoNetActive, not recruitingInfantile GM2 Gangliosidosis (Disorder)Canada
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsTerminatedTay-Sachs Disease | Sandhoff Disease | GM1 Gangliosidoses | GM2 GangliosidosesUnited States
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedLysosomal Storage Disease | Peroxisomal DisorderUnited States
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Joanne Kurtzberg, MDAldagenWithdrawnLysosomal Storage Diseases | Inborn Errors of MetabolismUnited States
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The Hospital for Sick ChildrenActelionCompletedGangliosidoses GM2Canada
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedTay Sachs Disease | Sandhoff Disease | Late Onset Tay Sachs DiseaseUnited States
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland...WithdrawnG(M2) Ganglioside | Tay-Sachs Disease Ganglioside | Sandhoff Disease GangliosideUnited States, Canada
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The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
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Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
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University of SurreyAmerican Society of HematologyRecruitingFrailty | Chronic Lymphocytic Leukemia | Muscle Function | Immune Function | Lipid Cell; TumorUnited Kingdom
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The First Affiliated Hospital of Zhejiang Chinese...RecruitingInflammatory Response | Tourette Syndrome in Children | Food IntoleranceChina
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Isfahan University of Medical SciencesNot yet recruitingInfertility | Thin Endometrium | Infertility FemaleIran, Islamic Republic of
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Chongqing Medical UniversityRecruitingHeart Failure With Preserved Ejection Fraction | PrognathismChina
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Omphis FoundationRecruiting
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Institut de cancérologie Strasbourg EuropeContinuum Plus Santé; Plateforme nationale qualité de vie et cancer; WeShareNot yet recruitingBreast Neoplasms | Lung Neoplasms | Prostatic Neoplasms | Colorectal NeoplasmsFrance
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Chunling JiangNot yet recruitingSecondary Hyperparathyroidism | End Stage Renal Failure
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China Medical University HospitalNational Cheng Kung University; National Science and Technology CouncilNot yet recruiting
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Infectopharm Arzneimittel GmbHWinicker Norimed GmbHNot yet recruiting
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Riphah International UniversityRecruiting
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Changzhou No.2 People's HospitalNot yet recruiting
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Instituto de Investigación Biomédica de SalamancaCarlos III Health InstituteRecruiting
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University Hospital, BordeauxNot yet recruiting
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Laboratorios Sophia S.A de C.V.Not yet recruitingDry Eye | Dry Eye Syndromes | Dry Eyes Chronic
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Ganzhou Hemay Pharmaceutical Co., LtdNot yet recruiting
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityRecruitingModerate to Severe Acne VulgarisChina
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King's College LondonGuy's and St Thomas' NHS Foundation TrustNot yet recruitingDeep Caries | Carious Exposure of Pulp
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Nordsjaellands HospitalNot yet recruitingColles' Fracture | Fracture Dislocation | Distal Radius Fractures | Lidocaine | Ropivacaine | Closed Reduction of Fracture and Application of Plaster CastDenmark
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Northwell HealthRecruitingPain, Postoperative | Postoperative Pain, AcuteUnited States
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University of Rome G. MarconiUniversity of Bologna; University of the Italian SwitzerlandNot yet recruitingStress | Insomnia | Postpartum DepressionItaly
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Shanghai Ninth People's Hospital Affiliated to...RecruitingNeurofibromatosis 1 | Plexiform NeurofibromaChina
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University of JordanRecruitingNon-specific Chronic Neck Pain | Diaphragmatic Breathing ExerciseJordan
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Peking UniversityRecruitingAdvanced Malignant Solid Tumor of Digestive SystemChina
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Zhujiang HospitalRecruitingDepression | Acute Ischaemic StrokeChina