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Search clinical trials for: Scheie syndrome
Total 37117 results
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Dompé Farmaceutici S.p.ARecruiting
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Tufts Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingDry Eye Syndromes | Corneal DiseaseUnited States
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Johns Hopkins UniversityMayo Clinic; Medical University of Graz; Radboud University Medical Center; University... and other collaboratorsRecruitingRetinitis PigmentosaUnited States, Austria, Mexico, Netherlands, United Kingdom, Germany, Canada, Switzerland
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University of PennsylvaniaNot yet recruiting
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Genzyme, a Sanofi CompanyRecruitingMucopolysaccharidosis I (MPS I)Croatia, United States, Argentina, Australia, Belgium, Brazil, Canada, Denmark, France, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Lebanon, Malaysia, Netherlands, Pakistan, Philippines, Poland, Saudi Arabia, Singapore, Slovaki... and more
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCTerminatedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | ScheieItaly
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Dompé Farmaceutici S.p.ACompletedDry Eye SyndromeUnited States, Italy
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REGENXBIO Inc.Active, not recruitingHurler Syndrome | Hurler-Scheie Syndrome | Mucopolysaccharidosis Type I (MPS I)United States, Brazil, Israel
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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University of PennsylvaniaOyster Point Pharma, Inc.Completed
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University of PennsylvaniaAllerganCompleted
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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CENTOGENE GmbH RostockWithdrawnMetabolism, Inborn Errors | Mucopolysaccharidosis Type I | GargoylismGermany, India, Sri Lanka, Egypt
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Sangamo TherapeuticsTerminated
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University of PennsylvaniaNational Eye Institute (NEI)Completed
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University of PennsylvaniaCompleted
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ShireTerminatedMucopolysaccharidosis (MPS)United States, Canada, United Kingdom, Turkey, Italy, Mexico, Spain
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TearSolutions, Inc.CompletedDry Eye | Primary Sjögren SyndromeUnited States
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Cognitive Decline | Hurler-Scheie SyndromeUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler-Scheie Syndrome | Hurlers SyndromeUnited States, Canada, Germany
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeNetherlands, France, Germany, United Kingdom
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeUnited States, Canada, United Kingdom, Brazil, Germany, Italy, Netherlands
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler's Syndrome | Hurler-Scheie SyndromeBrazil, Canada
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AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | Scheie's SyndromeUnited States
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Scheie Syndrome | Hurler Syndrome | Hurler-Scheie SyndromeJapan
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Patricia I. Dickson, M.D.The Ryan FoundationTerminatedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Spinal Cord Compression | Hurler-Scheie SyndromeFinland, United States
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Catharina Ziekenhuis EindhovenMaastricht UniversityNot yet recruitingTo Establish and Quantify the in Vivo Contractility of the Human Thoracic AortaNetherlands
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Laboratorios Sophia S.A de C.V.Not yet recruitingOcular Surface Disease | Dry Eye Disease | Dry Eye Sensation
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University of AarhusNot yet recruitingObstructive Sleep Apnea | Tonsillar Hypertrophy
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University of Missouri-ColumbiaGilead SciencesRecruitingHIV Infections | ART | Noncompliance, PatientUnited States
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McGill University Health Centre/Research Institute...Not yet recruiting
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Laboratoires TheaNot yet recruiting
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Shen LeiNot yet recruiting
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The Hong Kong Polytechnic UniversityNot yet recruitingPost-Concussion Syndrome | Functional Magnetic Resonance Imaging | Transcranial Direct Current Stimulation | Magnetic Resonance SpectroscopyHong Kong
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Shanghai Changzheng HospitalRecruitingSystemic Sclerosis | Sjogren's Syndrome | Antiphospholipid Syndrome | ANCA Associated Vasculitis | Systemic Lupus Erythematosus (SLE) | Inflammatory MyopathyChina
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Centre Hospitalier Universitaire, AmiensRecruitingAntiphospholipid SyndromeFrance
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Medical Centre LeeuwardenRecruitingICU Acquired Weakness | Post-Intensive Care SyndromeNetherlands
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Italian Society for RheumatologyRecruitingAntiphospholipid Syndrome | Seronegative Antiphospholipid SyndromeItaly
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Assiut UniversityNot yet recruitingNeonatal Respiratory Distress
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Istinye UniversityNot yet recruiting
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Apollo Therapeutics LtdNot yet recruitingMyelodysplastic Syndrome With Excess Blasts | Acute Myeloid Leukemia, in Relapse | Acute Myeloid Leukemia Refractory | Myelodysplastic Syndrome Acute Myeloid Leukemia
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Kolding SygehusOdense University Hospital; Vejle HospitalRecruitingHyperlipidemias | Nephrotic SyndromeDenmark
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Assistance Publique - Hôpitaux de ParisNot yet recruitingParaneoplastic Sensory NeuronopathyFrance
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University Hospital, AntwerpNot yet recruitingObstructive Sleep Apnea
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Ting Chang, MDNot yet recruiting
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Seventh Medical Center of PLA General HospitalGuangdong Provincial People's Hospital; Henan Provincial People's Hospital; People... and other collaboratorsNot yet recruitingExtracorporeal Membrane Oxygenation | Pediatric Acute Respiratory Distress SyndromeChina
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan