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Search clinical trials for: phenylketonuria
Total 158 results
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Rigshospitalet, DenmarkNot yet recruitingBrain Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Brain Diseases, Metabolic | Phenylketonurias | Brain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Metabolic DiseaseDenmark
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NGGT (Suzhou) Biotechnology Co., Ltd.Not yet recruitingPhenylketonurias
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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PTC TherapeuticsNot yet recruitingPhenylketonuriaUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States
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First Affiliated Hospital Bengbu Medical CollegeRecruiting
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Lumos DiagnosticsAptatek BiosciencesRecruiting
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRecruiting
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SanofiRecruiting
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Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTDRecruiting
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University Hospital, GrenobleRecruitingMetabolic Diseases | PhenylketonuriaFrance
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APR Applied Pharma Research s.a.Recruiting
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
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Centre Hospitalier Régional de la CitadelleSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Universitaire... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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BioMarin PharmaceuticalSyneos HealthRecruitingPhenylketonuria, MaternalGermany, United States, Italy
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APR Applied Pharma Research s.a.RecruitingPhenylketonuriasUnited Kingdom
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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University Children's Hospital, ZurichUniversity Children's Hospital Basel; UChildrenVienna; Insel Gruppe AG, University...RecruitingPhenylketonuriasSwitzerland
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Vitaflo International, LtdRecruitingPhenylketonurias | PKU | Maple Syrup Urine Disease | Homocystinuria | Glutaric Acidemia I | Hereditary TyrosinemiaUnited Kingdom
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University Medical Centre LjubljanaNot yet recruitingPhenylketonurias | Nutritional and Metabolic Diseases
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Chang Gung Memorial HospitalRecruitingNon-Phenylketonuric HyperphenylalaninemiaTaiwan
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University Hospital, LilleNot yet recruiting
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Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
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Nutricia UK LtdNot yet recruitingPhenylketonurias | Hyperphenylalaninaemia
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Vitaflo International, LtdUniversity College London HospitalsRecruiting
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Emory UniversityRecruiting
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Ajinomoto Co., Inc.Great Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Active, not recruiting
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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SynlogicTerminatedPhenylketonuriaUnited States, Canada, Georgia, Turkey
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metaX Institut fuer Diatetik GmbHBirmingham Children's HospitalCompletedPhenylketonurias | Hyperphenylalaninaemia | Tetrahydrobiopterin DeficiencyUnited Kingdom
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Hacettepe UniversityCompletedCaregiver Burden | Life Stress | Psychological Well-BeingTurkey
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
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Vitaflo International, LtdOregon Health and Science UniversityCompleted
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Vitaflo International, LtdArla FoodsCompletedPhenylketonuriasUnited Kingdom, Denmark
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdActive, not recruiting
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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University of Massachusetts, AmherstWithdrawnOxidative Stress | COPD | Tetrahydrobiopterin DeficiencyUnited States
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Klaus ParhoferTerminated
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University of Southern CaliforniaNational PKU AllianceActive, not recruitingPhenylketonuriasUnited States
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Boston Children's HospitalBioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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PTC TherapeuticsCompletedBH4 Deficiency | HyperphenylalaninemiaUnited States
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Homology Medicines, IncTerminatedPhenylketonuria | Phenylketonurias | PAH DeficiencyUnited States