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Search clinical trials for: primary hyperoxaluria
Total 16247 results
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Hospices Civils de LyonRecruitingPatients With PH1 Treated With Lumasiran in FranceFrance
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Cystinose StiftungScreening Laboratory Hannover; Pediatry Kastanienhof Koeln; Medical Genetics... and other collaboratorsRecruitingCystinosis | Primary HyperoxaluriaGermany
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Centre Hospitalier Régional de la CitadelleSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Universitaire... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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University Hospital, Strasbourg, FranceRecruiting
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyRecruitingPrimary Hyperoxaluria Type 3 | Primary Hyperoxaluria Type 2 | Primary Hyperoxaluria Type 1 | Primary HyperoxaluriaUnited States, Canada, Lebanon, Turkey, United Kingdom, Germany, Italy, Japan, Poland, Spain, United Arab Emirates
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Alnylam PharmaceuticalsRecruitingPrimary Hyperoxaluria Type 1France, Spain, United States, Israel, Belgium, Switzerland, Germany, United Kingdom, Italy, Canada
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyRecruitingEnd Stage Renal Disease | Primary Hyperoxaluria Type 2 | Primary Hyperoxaluria Type 1Germany, Spain, United States, United Kingdom, Italy, United Arab Emirates, Lebanon, Morocco, France, Romania
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Recruiting
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Mayo ClinicRecruitingCystinuria | Hyperoxaluria | Dent Disease | Lowe Syndrome | Adenine Phosphoribosyltransferase DeficiencyUnited States, Canada, Iceland, Israel
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Mayo ClinicRecruitingCystinuria | Primary Hyperoxaluria | Dent Disease | APRT DeficiencyUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingCystinuria | Primary Hyperoxaluria | Dent Disease | APRT DeficiencyUnited States, Iceland
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Alnylam PharmaceuticalsActive, not recruitingPrimary Hyperoxaluria Type 1 | Primary HyperoxaluriaUnited States, Italy, France, Lebanon, Belgium, Netherlands, Israel, United Arab Emirates, Australia, Jordan, Turkey
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Alnylam PharmaceuticalsActive, not recruitingPrimary Hyperoxaluria Type 1 (PH1) | Primary HyperoxaluriaUnited States, France, United Kingdom, Israel, Germany
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Therapeutics, Inc.CompletedTinea Pedis | Tinea CrurisUnited States
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingPrimary Hyperoxaluria Type 3United States, Germany, United Kingdom, Canada, Poland
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria Type 1 (PH1)United States, France, United Kingdom, Switzerland, Netherlands, Israel, Germany, United Arab Emirates
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Alnylam PharmaceuticalsApproved for marketingPrimary HyperoxaluriaBelgium
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyEnrolling by invitationKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2) | Primary Hyperoxaluria Type 3 (PH3)United States, France, Germany, Japan, Lebanon, Spain, United Kingdom, Australia, Canada, Italy, Netherlands, Norway, Turkey
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyAvailablePrimary Hyperoxaluria Type 1 (PH1)
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Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria | PH1 | RNAi Therapeutic | siRNA | AGTFrance, United Kingdom, Netherlands, Israel, Germany
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NYU Langone HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedCystinuria | Primary Hyperoxaluria | Dent Disease | Adenine Phosphoribosyl Transferase DeficiencyUnited States, Iceland
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Dicerna Pharmaceuticals, Inc.CompletedKidney Diseases | Urologic Diseases | Genetic Disease | Primary Hyperoxaluria Type 1 (PH1) | Primary Hyperoxaluria Type 2 (PH2)Poland, United Kingdom, New Zealand, United States, Australia, Canada, France, Germany, Israel, Italy, Japan, Lebanon, Netherlands, Romania, Spain
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OxTheraFP7-SME-2013 Research for the benefit of SMEs programCompletedPrimary HyperoxaluriaGermany
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OxTheraCompletedPrimary HyperoxaluriaFrance, United Kingdom, Spain, Belgium, United States, Germany, Tunisia
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OxTheraTerminatedHyperoxaluria, PrimaryUnited Kingdom, Spain, Belgium, United States, Germany, Tunisia
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Dicerna Pharmaceuticals, Inc.CompletedPrimary Hyperoxaluria Type 3United States, Germany, Netherlands, United Kingdom
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BiocodexCompletedPrimary HyperoxaluriaFrance
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Allena PharmaceuticalsCompletedEnteric Hyperoxaluria | Primary Hyperoxaluria | HyperoxalemiaUnited States, United Kingdom, Germany
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Alnylam PharmaceuticalsCompletedPrimary Hyperoxaluria Type 1 (PH1)France, United Kingdom, Netherlands, Israel, Germany
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Dicerna Pharmaceuticals, Inc.CompletedPrimary HyperoxaluriaUnited States, France, Germany, Netherlands, United Kingdom
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Mayo ClinicCompleted
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Ann & Robert H Lurie Children's Hospital of ChicagoMayo Clinic; National Institute of Diabetes and Digestive and Kidney Diseases...CompletedPrimary Hyperoxaluria Type 1
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Dicerna Pharmaceuticals, Inc.TerminatedPrimary Hyperoxaluria Type 1Netherlands, Germany
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VA New York Harbor Healthcare SystemMayo Clinic; New York UniversityUnknownOxalate, Primary Hyperoxaluria, MicrobiomeUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompleted
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Hospices Civils de LyonCompletedIdiopathic Hypercalciuria | Primary Hyperoxaluria Type 1France
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Oxalosis...Completed
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OxTheraFP7-SME-2013 Research for the benefit of SMEs programCompletedPrimary HyperoxaluriaFrance, Germany, United Kingdom
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Withdrawn
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Mayo ClinicNational Institutes of Health (NIH); Oxalosis and Hyperoxaluria Foundation...WithdrawnKidney Stones | Nephrocalcinosis | Primary HyperoxaluriaUnited States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Orphan...CompletedHyperoxaluriaUnited States
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OxTheraCompletedPrimary HyperoxaluriaUnited States
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University of CologneCompletedPrimary Hyperoxaluria Type IGermany
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McGill University Health Centre/Research Institute...Not yet recruitingPulp Disease, Dental
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Cukurova UniversityHacettepe University; Gazi University; Marmara University; Bezmialem Vakif University and other collaboratorsNot yet recruiting
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University of PennsylvaniaNot yet recruitingParkinson Disease | Alzheimer Disease | ALS | Polyneuropathies | Frontotemporal Dementia | Pheochromocytoma | Thoracic Aortic Aneurysm | Paraganglioma | Genetic Predisposition | Cardiomyopathy Non-ischemic
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Center for Primary Care and Public Health (Unisante)...University of Lausanne Hospitals; Neuchâtel Psychiatry Centre (CNP)Not yet recruitingQuality of Life | Mental Health Issue | Collaboration | Psychosomatic Disorders | Doctor-Patient Relation | Depression/Anxiety | Patients Lived ExperiencesSwitzerland