Příklad: Heart Attack

Klinické studie na Spinální svalová atrofie 1

Celkem 29 výsledků

NCT01862042

Dokončeno

Palliative Care in Spinal Muscular Atrophy (SMA) 1

Podmínky: Spinal Muscular Atrophy 1
NCT02122952

Dokončeno

Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1

Podmínky: Spinal Muscular Atrophy 1
NCT03421977

Aktivní, ne nábor

Long-Term Follow-up Study for Patients From AVXS-101-CL-101

Podmínky: Spinal Muscular Atrophy 1
NCT03395795

Nábor

Trial Evaluating the Interest of Noninvasive Ventilation in NAVA Mode in Respiratory Decompensations Children With Infantile Spinal Muscular Atrophy Type II

Podmínky: Infantile Spinal Muscular Atrophy
NCT00439218

Ukončeno

Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I

Podmínky: Spinal Muscular Atrophy Type I
NCT02061189

Aktivní, ne nábor

Pilot Study of an Innovative Physiotherapy in Patients With Infantile Spinal Muscular Atrophy (SMA)

Podmínky: Infantile Spinal Muscular Atrophy of Type 2 or 3
NCT00661453

Dokončeno

CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I

Podmínky: Spinal Muscular Atrophy Type I
NCT03837184

Aktivní, ne nábor

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

Podmínky: Spinal Muscular Atrophy Type I
NCT02855112

Neznámý stav

Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients

Podmínky: Infantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]
NCT00568698

Dokončeno

A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients

Podmínky: Muscular Atrophy, Spinal
NCT01547871

Ukončeno

Infants With Spinal Muscular Atrophy Type I

Podmínky: Spinal Muscular Atrophy
NCT02466529

Dokončeno

Natural History of Spinal Muscular Atrophy Type 1 in Taiwan

Podmínky: Natural History of Type 1 Spinal Muscular Atrophy (SMA)
NCT04042025

Registrace pomocí pozvánky

Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

Podmínky: Spinal Muscular Atrophy Type I; Spinal Muscular Atrophy Type II; Spinal Muscular Atrophy Type III; SMA
NCT02268552

Aktivní, ne nábor

An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)

Podmínky: Spinal Muscular Atrophy
NCT01780246

Dokončeno

An Open-label Safety and Tolerability Study of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy Who Previously Participated in ISIS 396443-CS1 (NCT01494701)

Podmínky: Spinal Muscular Atrophy
NCT03306277

Dokončeno

Gene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1

Podmínky: SMA - Spinal Muscular Atrophy; Gene Therapy
NCT02550691

Ukončeno

Identification of a Biomarker Associated With Cis-duplication of the SMN1 Gene

Podmínky: Spinal Muscular Atrophy
NCT02831296

Nábor

Prospective Evaluation of Infants With Spinal Muscular Atrophy:

Podmínky: Spinal Muscular Atrophy
NCT00155168

Neznámý stav

Quantitative Analysis of SMN1 and SMN2 Gene Based on DHPLC System

Podmínky: Spinal Muscular Atrophy
NCT02913482

Aktivní, ne nábor

Investigate Safety, Tolerability, PK, PD and Efficacy of Risdiplam (RO7034067) in Infants With Type1 Spinal Muscular Atrophy

Podmínky: Muscular Atrophy, Spinal
NCT02865109

Available

Expanded Access Program (EAP) for Nusinersen in Participants With Infantile-onset (Consistent With Type 1) Spinal Muscular Atrophy (SMA)

Podmínky: Infantile-onset Spinal Muscular Atrophy
NCT03461289

Dokončeno

Single-Dose Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1

Podmínky: SMA
NCT03955679

Approved for marketing

AveXis Managed Access Program Cohort for Access to AVXS-101

Podmínky: Spinal Muscular Atrophy
NCT04292574

Nábor

UK Spinal Muscular Atrophy Patient Registry

Podmínky: Spinal Muscular Atrophy; SMA
NCT00466349

Dokončeno

International SMA Patient Registry

Podmínky: Muscular Atrophy, Spinal