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Kliniske forsøg med Arvelig Inclusion Body Myopati
I alt 125 resultater
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...AfsluttetGNE myopati | Hereditary Inclusion Body Myopati (HIBM)Forenede Stater
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Ultragenyx Pharmaceutical IncAfsluttetGNE myopati | Hereditary Inclusion Body Myopati (HIBM)Forenede Stater, Israel
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Ultragenyx Pharmaceutical IncAfsluttetHereditary Inclusion Body Myopati (HIBM)Forenede Stater
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NobelpharmaAfsluttetGNE myopati | Nonaka sygdom | Distal myopati med kantede vakuoler (DMRV) | Hereditary Inclusion Body Myopati (hIBM)Japan
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Ludwig-Maximilians - University of MunichAfsluttetInclusion Body Myositis, Sporadisk | Inclusion Body Myopati, Autosomal-recessiv | Inclusion Body Myopati, Autosomal-dominant | Medfødt grå stær, ansigtsdysmorfi og neuropatiTyskland
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Ultragenyx Pharmaceutical IncAfsluttetArvelig Inclusion Body Myopati | GNE myopati | Inklusionskropsmyopati 2 | Distal myopati med kantede vakuoler | Distal myopati, Nonaka Type | Quadriceps sparende myopatiCanada, Forenede Stater, Bulgarien
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Newcastle UniversityUkendtArvelig Inclusion Body Myopati | GNE myopatiDet Forenede Kongerige
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Tohoku UniversityAfsluttetArvelig Inclusion Body Myopati | Nonaka myopatiJapan
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Ultragenyx Pharmaceutical IncAfsluttetArvelig Inclusion Body Myopati | GNE myopati | Distal myopati med kantede vakuoler | Distal myopati, Nonaka TypeForenede Stater, Canada, Det Forenede Kongerige, Israel, Italien, Bulgarien, Frankrig
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Ultragenyx Pharmaceutical IncAfsluttetArvelig Inclusion Body Myopati | GNE myopatiForenede Stater, Israel
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Ultragenyx Pharmaceutical IncAfsluttetArvelig Inclusion Body Myopati | GNE myopati | Distal myopati med kantede vakuoler | Distal myopati, Nonaka Type | Quadriceps sparende myopatiForenede Stater, Canada, Det Forenede Kongerige, Israel, Italien, Bulgarien, Frankrig
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Ultragenyx Pharmaceutical IncNewcastle UniversityAfsluttetArvelig Inclusion Body Myopati | GNE myopati | Nonaka sygdom | Quadriceps Sparing Myopati (QSM) | Distal myopati med kantede vakuoler (DMRV)Forenede Stater, Bulgarien, Canada, Frankrig, Det Forenede Kongerige
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National Human Genome Research Institute (NHGRI)AfsluttetArvelig Inclusion Body MyopatiForenede Stater
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Institut National de la Santé Et de la Recherche...AfsluttetInclusion Body Myositis (IBM)Frankrig
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Phoenix Neurological Associates, LTDUkendt
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University of Southern DenmarkOdense University HospitalAfsluttetSporadisk inklusionslegememyositisDanmark
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University of Kansas Medical CenterAfsluttetInclusion Body Myositis | Sporadisk inklusionslegememyositisForenede Stater
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Novartis PharmaceuticalsAfsluttetSporadisk inklusionslegememyositisForenede Stater
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La-ser Europe LimitedUkendtSporadisk inklusionslegememyositis
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Regeneron PharmaceuticalsTrukket tilbageSporadisk inklusionslegememyositis
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Novartis PharmaceuticalsAfsluttetSporadisk inklusionskropsmyositis (sIBM)Forenede Stater
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Assistance Publique - Hôpitaux de ParisRekrutteringInclusion Body MyositisFrankrig
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Abcuro, Inc.Syneos HealthAktiv, ikke rekrutterendeInclusion Body MyositisForenede Stater, Australien, Belgien, Frankrig, Canada, Tyskland, Det Forenede Kongerige
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Centre Hospitalier Universitaire de NiceAfsluttetInclusion Body MyositisFrankrig
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Richard Barohn, MDAfsluttetInclusion Body MyositisForenede Stater, Det Forenede Kongerige
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University of Kansas Medical CenterBioSensicsRekrutteringInclusion Body MyositisForenede Stater
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Abcuro, Inc.Aktiv, ikke rekrutterendeInclusion Body MyositisAustralien
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ZevraDenmarkUniversity College, London; University of Kansas Medical CenterAfsluttetInclusion Body MyositisForenede Stater, Det Forenede Kongerige
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ZevraDenmarkUniversity College, London; University of Kansas Medical CenterAfsluttetInclusion Body MyositisForenede Stater, Det Forenede Kongerige
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University of Kansas Medical CenterAktiv, ikke rekrutterendeInclusion Body MyositisForenede Stater
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Washington University School of MedicineAmgenAfsluttetInclusion Body MyositisForenede Stater
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Institut de Myologie, FranceAssistance Publique - Hôpitaux de ParisAfsluttetInclusion Body MyositisFrankrig
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Phoenix Neurological Associates, LTDAfsluttet
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Yale UniversityAfsluttetInclusion Body Myositis | IBMForenede Stater
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Johns Hopkins UniversityAfsluttetSygdomme i nervesystemet | Muskelsygdomme | Neuromuskulære sygdomme | Myositis | Muskuloskeletal sygdom | Inclusion Body MyositisForenede Stater
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University of California, IrvineNational Institute of Arthritis and Musculoskeletal and Skin Diseases...Aktiv, ikke rekrutterendeInclusion Body Myositis | Sporadisk inklusionslegememyositisForenede Stater
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University of Kansas Medical CenterThe Perron InstituteRekruttering
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National Institute of Neurological Disorders and...AfsluttetMyositis, InklusionslegemeForenede Stater
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National Institute of Neurological Disorders and...AfsluttetMyositis | Sporadisk | InklusionsorganForenede Stater
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Novartis PharmaceuticalsAfsluttetSporadisk inklusionslegememyositisForenede Stater, Belgien, Italien, Australien, Holland, Schweiz, Frankrig, Det Forenede Kongerige, Danmark, Japan
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Novartis PharmaceuticalsAfsluttetSporadisk inklusionslegememyositisForenede Stater, Belgien, Italien, Australien, Holland, Schweiz, Frankrig, Det Forenede Kongerige, Danmark, Japan
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National Institute of Neurological Disorders and...AfsluttetDermatomyositis | Polymyositis | Inclusion Body MyositisForenede Stater
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Karolinska InstitutetAfsluttet
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National Institute of Environmental Health Sciences...Aktiv, ikke rekrutterendeMyositis | Dermatomyositis | Inclusion Body Myositis | Voksen polymyositisForenede Stater
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National Institute of Environmental Health Sciences...Rekruttering
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Nationwide Children's HospitalParent Project Muscular DystrophyAfsluttetBeckers muskeldystrofi | Sporadisk inklusionslegememyositisForenede Stater
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Clinic for Special ChildrenRekrutteringMyopati | Myopati; Arvelig | Myopatier, Nemaline | TNNT1-associeret myopati | Infantil-debut Nemaline Rod Myopati | Myopati, Rod | Amish Nemaline Myopati | Nemaline myopati 5 | NEM5 | Genetisk muskelsygdom | Recessiv arvelig lidelse (autosomal) | ANMForenede Stater
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LMU KlinikumAfsluttetSund og rask | Myotonisk dystrofi type 2 | Pompes sygdom (sen debut) | Spinal muskelatrofi type 3 | Myotonisk dystrofi type 1 (DM1) | Facioscapulohumeral muskeldystrofi 1 | Inclusion Body Myositis, SporadiskTyskland
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LMU KlinikumRekrutteringMyasthenia gravis | Myotonisk dystrofi | Inclusion Body Myositis | Facioscapulohumerale muskeldystrofier | The Falls Efficacy Scale International | Morse Fall ScaleTyskland
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LMU KlinikumRekrutteringPompes sygdom (sen debut) | FSHD | Spinal muskelatrofi type 3 | Inclusion Body MyositisTyskland