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Kliniske forsøg med Lembelte Muskeldystrofi Type 2A
I alt 151 resultater
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Linda Pax LowesRekrutteringLimb-Girdle Muskeldystrofi Type 2A | Limb-Girdle Muskeldystrofi, Type 2EForenede Stater
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Virginia Commonwealth UniversityUniversity of Colorado, Denver; Washington University School of Medicine; University of Iowa og andre samarbejdspartnereRekrutteringLembælte muskeldystrofi | Calpain-3-mangel ekstremitetsbælte Muskeldystrofi Type 2A | Lembælte muskeldystrofi Type R1 | LGMD2AForenede Stater, Det Forenede Kongerige
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico og andre samarbejdspartnereTilmelding efter invitationCalpain-3-mangel ekstremitetsbælte Muskeldystrofi Type 2AItalien
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteAfsluttetBeckers muskeldystrofi | Limb-Girdle Muskeldystrofi, Type 2A (Calpain-3-mangel) | Limb-Girdle Muskeldystrofi, Type 2B (Miyoshi Myopati, Dysferlin-mangel) | Limb-Girdle Muskeldystrofi, Type 2I (FKRP-mangel)Forenede Stater
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Afsluttet
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University Hospital of North NorwayUniversity of Tromso; Norwegian Muscle Disease Association (FFM); Norwegian... og andre samarbejdspartnereAktiv, ikke rekrutterendeMuskeldystrofier | Lembælte muskeldystrofi | Lembælte muskeldystrofi, type 2I | Limb urdle muskeldystrofi R9 FKRP-relateretNorge
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Nationwide Children's HospitalMyonexus TherapeuticsRekrutteringLimb-Girdle Muskeldystrofi, Type 2EForenede Stater
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Rigshospitalet, DenmarkAfsluttetBeckers muskeldystrofi | Limb-Girdle Muskeldystrofi Type 2IDanmark
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ML Bio Solutions, Inc.RekrutteringLimb-Girdle Muskeldystrofi Type 2I (LGMD2I)Forenede Stater, Holland, Det Forenede Kongerige, Norge, Italien, Danmark, Australien
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Assistance Publique - Hôpitaux de ParisRekrutteringLembælte muskeldystrofierFrankrig
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbejdspartnereAfsluttetMuskeldystrofierForenede Stater
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GenethonAfsluttetKlinisk undersøgelse af AAV1-gamma-sarcoglycan-genterapi til muskeldystrofi i ekstremiteter, type 2CLembælte muskeldystrofi Type 2C | Gamma-sarcoglycanopatiFrankrig
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Mads Peter Godtfeldt StemmerikEdgewise Therapeutics, Inc.AfsluttetBeckers muskeldystrofi | McArdles sygdom | Limb-Girdle Muskeldystrofi Type 2Danmark
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aTyr Pharma, Inc.AfsluttetLem-Girdle muskeldystrofier | Facioscapulohumeral muskeldystrofiForenede Stater, Danmark, Frankrig
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Sarepta Therapeutics, Inc.Aktiv, ikke rekrutterende
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aTyr Pharma, Inc.AfsluttetFacioscapulohumeral muskeldystrofi | Lembælte muskeldystrofiForenede Stater, Danmark, Italien
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)AfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofi | Lembælte muskeldystrofiForenede Stater
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Wyeth is now a wholly owned subsidiary of PfizerAfsluttetBeckers muskeldystrofi | Facioscapulohumeral muskeldystrofi | Limb-Girdle muskeldystrofiForenede Stater
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University of North Carolina, Chapel HillNational Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbejdspartnereAfsluttetMuskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofi | Limb-Girdle muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...United States Department of DefenseAfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofi | Lembælte muskeldystrofiForenede Stater, Japan, Canada
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)AfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofi | Lembælte muskeldystrofiForenede Stater
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Wake Forest University Health SciencesMuscular Dystrophy AssociationAfsluttetMuskeldystrofier, lemmer-bælte (GENETISK BEKRÆFTET)Forenede Stater
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbejdspartnereAfsluttetLimb-Girdle muskeldystrofiForenede Stater
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PTC TherapeuticsAfsluttetLimb-Girdle muskeldystrofiForenede Stater, Norge, Canada, Sverige, Den Russiske Føderation, Danmark, Frankrig, Tyskland
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Rigshospitalet, DenmarkAfsluttet
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Northwestern UniversityAfsluttetBeckers muskeldystrofi | Lem-bælte muskeldystrofiForenede Stater
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Sarepta Therapeutics, Inc.Rekruttering
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Rigshospitalet, DenmarkAfsluttet
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Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RekrutteringLem-bælte muskeldystrofi | Neuromuskulær; Lidelse, arvelig | Duchenne/Becker muskeldystrofiForenede Stater
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Rigshospitalet, DenmarkRekrutteringLembælte muskeldystrofiDanmark
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Rigshospitalet, DenmarkFunding: Toyota Foundation; Funding: Hede Nielsen Foundation; Funding: Grosserer... og andre samarbejdspartnereAktiv, ikke rekrutterende
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Neurogen Brain and Spine InstituteTrukket tilbage
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Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University... og andre samarbejdspartnereRekrutteringMuskeldystrofier | Lembælte muskeldystrofiForenede Stater, Det Forenede Kongerige
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Neurogen Brain and Spine InstituteTrukket tilbage
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GenethonAktiv, ikke rekrutterendeLGMD2IDanmark, Frankrig, Det Forenede Kongerige
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Asklepios Biopharmaceutical, Inc.RekrutteringMuskeldystrofi | Lembælte muskeldystrofi | LGMD2I | LGMD | Limb-Girdle Muskeldystrofi Type 2 | LGMD2 | FKRP | FKRP-mutation | Fukutin-relateret proteinForenede Stater
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Sarepta Therapeutics, Inc.Aktiv, ikke rekrutterende
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityAfsluttetMuskeldystrofier | Lembælte muskeldystrofiForenede Stater, Danmark
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National Cancer Institute (NCI)AfsluttetMultipel endokrin neoplasi type 2A | Multipel endokrin neoplasi type 2B | Medullært skjoldbruskkirtelcarcinomForenede Stater
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Sarepta Therapeutics, Inc.Aktiv, ikke rekrutterendeLimb-Girdle Muskeldystrofi, Type 2EForenede Stater
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Sarepta Therapeutics, Inc.Nationwide Children's HospitalAfsluttet
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Sarepta Therapeutics, Inc.RekrutteringLem-bælte muskeldystrofiForenede Stater, Brasilien, Belgien, Canada, Tyskland, Italien, Spanien, Sverige, Kalkun, Det Forenede Kongerige
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National Cancer Institute (NCI)Trukket tilbageTilbagevendende akut myeloid leukæmi hos voksne | Tilbagevendende akut myeloid leukæmi i barndommen | CNS 2a | CNS 2b | CNS 2c | CNS1
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Politecnico di MilanoIRCCS Eugenio Medea; Villa Beretta Rehabilitation CenterAfsluttetMuskeldystrofier | Muskeldystrofi, Duchenne | Muskeldystrofi, Becker | Muskeldystrofi, ekstremitetsbælte type 2Italien
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRekrutteringCerebral Parese | Muskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofi | Spinal muskelatrofi | Lembælte muskeldystrofi | FSHDForenede Stater
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Children's Oncology GroupNational Cancer Institute (NCI)Aktiv, ikke rekrutterendeTilbagevendende neuroblastom | Stadie 4S neuroblastom | Stadium 2A neuroblastom | Stadie 2B neuroblastom | Stadium 3 neuroblastom | Stadium 4 neuroblastomForenede Stater, Canada, Australien, New Zealand
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Newcastle UniversityLudwig-Maximilians - University of Munich; LGMD2i Research Fund; CureLGMD2iRekrutteringLembælte muskeldystrofi | Medfødt muskeldystrofi | LGMDR9 | LGMD2I | Walker-Warburg syndrom | Muskel-øje-hjerne sygdom | FKRP-genmutationDet Forenede Kongerige
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Children's Oncology GroupNational Cancer Institute (NCI)Aktiv, ikke rekrutterendeStadie 4S neuroblastom | Ganglioneuroblastom | Stadium 2A neuroblastom | Stadie 2B neuroblastom | Stadium 3 neuroblastom | Stadium 4 neuroblastom | Stadie 1 neuroblastom | Stadie 2 neuroblastomForenede Stater, Canada, Australien, New Zealand
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Centre Hospitalier Universitaire de NiceRekrutteringType 1 Facioscapulohumeral muskeldystrofiFrankrig
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Ning Wang, MD., PhD.Rekruttering