- ICH GCP
- US Clinical Trials Registry
- Search trials
Kliniske forsøg med Mucopolysaccharidoser
I alt 224 resultater
-
Immusoft of CA, Inc.RekrutteringMucopolysaccharidosis IH/S | Mucopolysaccharidosis ISForenede Stater
-
JCR Pharmaceuticals Co., Ltd.RekrutteringMucopolysaccharidosis III-ATyskland
-
Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation og andre samarbejdspartnereAfsluttetMucopolysaccharidosis Type IIIA | Mucopolysaccharidosis Type IIIBForenede Stater
-
IRCCS San RaffaeleFondazione TelethonAktiv, ikke rekrutterende
-
Masonic Cancer Center, University of MinnesotaRekrutteringMucopolysaccharidosis type I | Hæmatopoietisk celletransplantationForenede Stater
-
Sanguine BiosciencesDenali Therapeutics Inc.RekrutteringMucopolysaccharidosis III-AForenede Stater
-
Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTilmelding efter invitationMucopolysaccharidosis III-AForenede Stater, Australien, Spanien
-
Abeona Therapeutics, IncAfsluttetMucopolysaccharidosis III-BForenede Stater, Tyskland, Frankrig
-
Fondazione TelethonAktiv, ikke rekrutterendeMucopolysaccharidosis Type VIItalien, Kalkun
-
Abeona Therapeutics, IncAfsluttetMucopolysaccharidosis Type 3 BForenede Stater, Tyskland, Frankrig, Spanien
-
Allievex CorporationAfsluttetMucopolysaccharidosis Type IIIB | Mucopolysaccharidosis Type 3 B | MPS III B | MPS 3 BForenede Stater, Spanien, Kalkun, Taiwan, Australien, Colombia, Tyskland, Det Forenede Kongerige
-
Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...AfsluttetMucopolysaccharidosis VI | Mucopolysaccharidosis IV AForenede Stater
-
University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIForenede Stater, Canada
-
University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... og andre samarbejdspartnereAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIADet Forenede Kongerige
-
Allievex CorporationAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIBForenede Stater, Tyskland, Spanien, Argentina, Australien, Brasilien, Colombia, Taiwan, Kalkun
-
University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidosis type IForenede Stater
-
Genzyme, a Sanofi CompanyRekrutteringMucopolysaccharidosis I (MPS I)Kroatien, Forenede Stater, Argentina, Australien, Belgien, Brasilien, Canada, Danmark, Frankrig, Hong Kong, Indien, Indonesien, Korea, Republikken, Kuwait, Libanon, Malaysia, Holland, Pakistan, Filippinerne, Polen, Saudi Arabien, S... og mere
-
LYSOGENEAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIATyskland, Forenede Stater, Det Forenede Kongerige, Frankrig, Holland
-
ShireAfsluttetSanfilippo syndrom | Mucopolysaccharidosis (MPS)Forenede Stater, Det Forenede Kongerige, Spanien, Tyskland, Frankrig, Italien, Holland
-
Alexion PharmaceuticalsAfsluttetMucopolysaccharidosis IIIBForenede Stater, Det Forenede Kongerige, Spanien
-
CENTOGENE GmbH RostockTrukket tilbageMetabolisme, medfødte fejl | Mucopolysaccharidosis type I | GargoylismeTyskland, Indien, Sri Lanka, Egypten
-
ShireAfsluttetMucopolysaccharidosis (MPS)Det Forenede Kongerige, Holland
-
LYSOGENEAfsluttetMucopolysaccharidosis Type III A | Sanfilippo sygdom type AFrankrig
-
LYSOGENEAfsluttetMucopolysaccharidosis Type III A | Sanfilippo sygdom type AFrankrig
-
Denali Therapeutics Inc.RekrutteringMucopolysaccharidosis Type IIIAForenede Stater
-
Allievex CorporationAfsluttetMucopolysaccharidosis Type IIIB | MPS III BForenede Stater, Taiwan, Spanien, Colombia, Tyskland, Det Forenede Kongerige, Kalkun
-
Allievex CorporationAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIB | MPS III BTyskland, Forenede Stater, Kalkun, Det Forenede Kongerige, Colombia, Spanien, Taiwan
-
JCR Pharmaceuticals Co., Ltd.Aktiv, ikke rekrutterendeMucopolysaccharidosis IForenede Stater, Brasilien, Japan
-
Alexion PharmaceuticalsAfsluttetMucopolysaccharidosis III, Type B (MPS IIIB) | Sanfilippo BDet Forenede Kongerige
-
BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrom)Forenede Stater, Frankrig, Australien, Tyskland, Irland, Østrig, Belgien, Italien, Litauen, Holland, Portugal, Sverige, Det Forenede Kongerige
-
Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIForenede Stater
-
GOIZETBioMarin PharmaceuticalRekruttering
-
University Hospital HeidelbergAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mestringsadfærd | Mucopolysaccharidosis Type III | AdfærdsforstyrrelserTyskland
-
Alexion PharmaceuticalsAfsluttetMPS IIIB (Sanfilippo Syndrome)Spanien, Holland, Det Forenede Kongerige, Forenede Stater, Brasilien
-
Lundquist Institute for Biomedical Innovation at...Swedish Orphan Biovitrum; Cure Sanfilippo FoundationAfsluttet
-
Genzyme, a Sanofi CompanyAfsluttet
-
JCR Pharmaceuticals Co., Ltd.AfsluttetMucopolysaccharidosis IForenede Stater, Brasilien, Japan
-
LYSOGENEAfsluttetMucopolysaccharidosis IIIATyskland, Brasilien, Det Forenede Kongerige, Frankrig, Holland
-
Inventiva PharmaAfsluttetMucopolysaccharidosis VIDet Forenede Kongerige, Frankrig, Tyskland, Portugal
-
BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
-
BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
-
BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
-
BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
-
REGENXBIO Inc.Aktiv, ikke rekrutterendeHurler syndrom | Hurler-Scheie syndrom | Mucopolysaccharidosis Type I (MPS I)Forenede Stater, Brasilien, Israel
-
Masonic Cancer Center, University of MinnesotaTrukket tilbageMucopolysaccharidosis Type IH | Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome) | MPS IH, Hurler syndrom
-
Masonic Cancer Center, University of MinnesotaAfsluttetHurler syndrom | Mucopolysaccharidosis Type IH | MPS IForenede Stater
-
Emory UniversityBioMarin PharmaceuticalAfsluttetMucopolysaccharidosis Type IVAForenede Stater
-
BioMarin PharmaceuticalGodkendt til markedsføringMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Puerto Rico
-
Masonic Cancer Center, University of MinnesotaAfsluttet
-
ArmaGen, IncAfsluttetMucopolysaccharidosis IBrasilien