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Kliniske forsøg med Mucopolysaccharidosis Type IV
I alt 58004 resultater
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIForenede Stater, Canada
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Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...AfsluttetMucopolysaccharidosis VI | Mucopolysaccharidosis IV AForenede Stater
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GOIZETBioMarin PharmaceuticalRekruttering
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BioMarin PharmaceuticalICON plcAfsluttetMucopolysaccharidosis IV Type A | Morquio A syndrom | MPS IVAForenede Stater, Det Forenede Kongerige, Australien, Taiwan, Belgien, Malaysia, Østrig, Canada, Portugal, Frankrig, Irland, Tjekkiet, Danmark, Italien, Holland, Polen, Puerto Rico
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Hospital de Clinicas de Porto AlegreThe Isaac FoundationAktiv, ikke rekrutterendeMucopolysaccharidoser | Mucopolysaccharidosis VI | Morquio A syndrom | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio syndrom A | Morquio syndromBrasilien
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringMucopolysaccharidosis IV Type A | Morquio A syndrom | MPS IVAForenede Stater
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Emory UniversityBioMarin PharmaceuticalAfsluttetMucopolysaccharidosis Type IVAForenede Stater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IV A | Mucopolysaccharidosis IVADet Forenede Kongerige
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IV AForenede Stater, Canada, Frankrig, Taiwan, Argentina, Colombia, Spanien, Kalkun, Japan, Saudi Arabien, Holland, Danmark, Korea, Republikken, Brasilien, Det Forenede Kongerige, Tyskland, Norge, Portugal, Italien, Qatar
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMorquio A syndrom | Mucopolysaccharidosis IV AForenede Stater
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation og andre samarbejdspartnereAfsluttetMucopolysaccharidosis Type IIIA | Mucopolysaccharidosis Type IIIBForenede Stater
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Masonic Cancer Center, University of MinnesotaRekrutteringMucopolysaccharidosis type I | Hæmatopoietisk celletransplantationForenede Stater
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BioMarin PharmaceuticalAfsluttetEn klinisk vurderingsundersøgelse af forsøgspersoner med mucopolysaccharidosis IVA (Morquio syndrom)Morquio A syndrom | MPS IV A | Mucopolysaccharidosis IVAFrankrig, Det Forenede Kongerige, Taiwan, Forenede Stater, Argentina, Holland, Canada, Brasilien, Tyskland, Italien
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BioMarin PharmaceuticalGodkendt til markedsføringMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Puerto Rico
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Allievex CorporationAfsluttetMucopolysaccharidosis Type IIIB | Mucopolysaccharidosis Type 3 B | MPS III B | MPS 3 BForenede Stater, Spanien, Kalkun, Taiwan, Australien, Colombia, Tyskland, Det Forenede Kongerige
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JCR Pharmaceuticals Co., Ltd.RekrutteringMucopolysaccharidosis III-ATyskland
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IRCCS San RaffaeleFondazione TelethonAktiv, ikke rekrutterende
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Abeona Therapeutics, IncAfsluttetMucopolysaccharidosis Type 3 BForenede Stater, Tyskland, Frankrig, Spanien
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Emory UniversityBioMarin PharmaceuticalAfsluttetGraviditet med Morquio Syndrom - Hvad er patienternes perspektiver og har ERT ændret dem? (MorqPreg)MPS - Mucopolysaccharidosis | Morquios sygdomForenede Stater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVAForenede Stater, Det Forenede Kongerige, Canada, Tyskland
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LYSOGENEAfsluttetMucopolysaccharidosis Type III A | Sanfilippo sygdom type AFrankrig
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LYSOGENEAfsluttetMucopolysaccharidosis Type III A | Sanfilippo sygdom type AFrankrig
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Sanguine BiosciencesDenali Therapeutics Inc.RekrutteringMucopolysaccharidosis III-AForenede Stater
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Fondazione TelethonAktiv, ikke rekrutterendeMucopolysaccharidosis Type VIItalien, Kalkun
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVATaiwan, Forenede Stater, Italien, Det Forenede Kongerige
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalTrukket tilbageMucopolysaccharidosis IV | Morquio A DiseaseDet Forenede Kongerige
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Immusoft of CA, Inc.RekrutteringMucopolysaccharidosis IH/S | Mucopolysaccharidosis ISForenede Stater
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Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMorquio A syndrom | MPS IVA | Mucopolysaccharidosis IVADet Forenede Kongerige, Forenede Stater, Tyskland
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University Hospital HeidelbergAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mestringsadfærd | Mucopolysaccharidosis Type III | AdfærdsforstyrrelserTyskland
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetKrabbes sygdom | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)Forenede Stater
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... og andre samarbejdspartnereAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIADet Forenede Kongerige
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Allievex CorporationAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIBForenede Stater, Tyskland, Spanien, Argentina, Australien, Brasilien, Colombia, Taiwan, Kalkun
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidosis type IForenede Stater
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National MPS SocietyMediResource Inc.AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoser | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVForenede Stater
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LYSOGENEAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIATyskland, Forenede Stater, Det Forenede Kongerige, Frankrig, Holland
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CENTOGENE GmbH RostockTrukket tilbageMetabolisme, medfødte fejl | Mucopolysaccharidosis type I | GargoylismeTyskland, Indien, Sri Lanka, Egypten
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Denali Therapeutics Inc.RekrutteringMucopolysaccharidosis Type IIIAForenede Stater
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Allievex CorporationAfsluttetMucopolysaccharidosis Type IIIB | MPS III BForenede Stater, Taiwan, Spanien, Colombia, Tyskland, Det Forenede Kongerige, Kalkun
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REGENXBIO Inc.Aktiv, ikke rekrutterendeHurler syndrom | Hurler-Scheie syndrom | Mucopolysaccharidosis Type I (MPS I)Forenede Stater, Brasilien, Israel
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Masonic Cancer Center, University of MinnesotaTrukket tilbageMucopolysaccharidosis Type IH | Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome) | MPS IH, Hurler syndrom
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University of California, San FranciscoRekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolmans sygdom | Pompes sygdom infantil | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopatisk Gauchers sygdomForenede Stater
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Nadia Ali, PhDBioMarin PharmaceuticalAfsluttetMucopolysaccharidosis IV | Morquios sygdomForenede Stater
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Allievex CorporationAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIB | MPS III BTyskland, Forenede Stater, Kalkun, Det Forenede Kongerige, Colombia, Spanien, Taiwan
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Alexion PharmaceuticalsAfsluttetMucopolysaccharidosis III, Type B (MPS IIIB) | Sanfilippo BDet Forenede Kongerige
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Alexion PharmaceuticalsAfsluttetMPS IIIB (Sanfilippo Syndrome)Spanien, Holland, Det Forenede Kongerige, Forenede Stater, Brasilien
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTilmelding efter invitationMucopolysaccharidosis III-AForenede Stater, Australien, Spanien
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Abeona Therapeutics, IncAfsluttetMucopolysaccharidosis III-BForenede Stater, Tyskland, Frankrig
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Masonic Cancer Center, University of MinnesotaAfsluttetHurler syndrom | Mucopolysaccharidosis Type IH | MPS IForenede Stater
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SanofiAfsluttetPompes sygdom | Mucopolysaccharidosis Type I (MPS I)Italien