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Kliniske forsøg med Mucopolysaccharidosis VI
I alt 232 resultater
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Fondazione TelethonAktiv, ikke rekrutterendeMucopolysaccharidosis Type VIItalien, Kalkun
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrom)Forenede Stater, Frankrig, Australien, Tyskland, Irland, Østrig, Belgien, Italien, Litauen, Holland, Portugal, Sverige, Det Forenede Kongerige
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIForenede Stater, Canada
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Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIForenede Stater
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Children's Hospitals and Clinics of MinnesotaBioMarin Pharmaceutical; Gillette Children's Specialty Healthcare; Greenwood...AfsluttetMucopolysaccharidosis VI | Mucopolysaccharidosis IV AForenede Stater
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetKrabbes sygdom | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)Forenede Stater
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Hospital de Clinicas de Porto AlegreThe Isaac FoundationAktiv, ikke rekrutterendeMucopolysaccharidoser | Mucopolysaccharidosis VI | Morquio A syndrom | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio syndrom A | Morquio syndromBrasilien
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Inventiva PharmaAfsluttetMucopolysaccharidosis VIDet Forenede Kongerige, Frankrig, Tyskland, Portugal
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VIForenede Stater
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Immusoft of CA, Inc.RekrutteringMucopolysaccharidosis IH/S | Mucopolysaccharidosis ISForenede Stater
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BioMarin PharmaceuticalAfsluttetMPS VIForenede Stater, Australien, Frankrig, Brasilien, Tyskland, Portugal, Det Forenede Kongerige
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JCR Pharmaceuticals Co., Ltd.RekrutteringMucopolysaccharidosis III-ATyskland
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Nationwide Children's HospitalSanfilippo Children's Research Foundation; The Sanfilippo Research Foundation og andre samarbejdspartnereAfsluttetMucopolysaccharidosis Type IIIA | Mucopolysaccharidosis Type IIIBForenede Stater
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Lundquist Institute for Biomedical Innovation at...Aktiv, ikke rekrutterendeMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIForenede Stater
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IRCCS San RaffaeleFondazione TelethonAktiv, ikke rekrutterende
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National MPS SocietyMediResource Inc.AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidoser | Mucopolysaccharidosis VI | Mucopolysaccharidosis IVForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VI | Maroteaux-Lamy syndromForenede Stater, Portugal, Frankrig
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Masonic Cancer Center, University of MinnesotaRekrutteringMucopolysaccharidosis type I | Hæmatopoietisk celletransplantationForenede Stater
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Sanguine BiosciencesDenali Therapeutics Inc.RekrutteringMucopolysaccharidosis III-AForenede Stater
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Lundquist Institute for Biomedical Innovation at...AfsluttetMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIForenede Stater
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTilmelding efter invitationMucopolysaccharidosis III-AForenede Stater, Australien, Spanien
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Abeona Therapeutics, IncAfsluttetMucopolysaccharidosis III-BForenede Stater, Tyskland, Frankrig
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Abeona Therapeutics, IncAfsluttetMucopolysaccharidosis Type 3 BForenede Stater, Tyskland, Frankrig, Spanien
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalAfsluttetMPS IVA | Maroteaux Lamy syndrom | MPS VI | Morquio syndrom AForenede Stater
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Allievex CorporationAfsluttetMucopolysaccharidosis Type IIIB | Mucopolysaccharidosis Type 3 B | MPS III B | MPS 3 BForenede Stater, Spanien, Kalkun, Taiwan, Australien, Colombia, Tyskland, Det Forenede Kongerige
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Institut National de la Santé Et de la Recherche...RekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multipel Sulfatase mangel sygdom | Mucopolysaccharidosis IXFrankrig
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... og andre samarbejdspartnereAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIADet Forenede Kongerige
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Allievex CorporationAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIBForenede Stater, Tyskland, Spanien, Argentina, Australien, Brasilien, Colombia, Taiwan, Kalkun
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetMucopolysaccharidosis type IForenede Stater
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Genzyme, a Sanofi CompanyRekrutteringMucopolysaccharidosis I (MPS I)Kroatien, Forenede Stater, Argentina, Australien, Belgien, Brasilien, Canada, Danmark, Frankrig, Hong Kong, Indien, Indonesien, Korea, Republikken, Kuwait, Libanon, Malaysia, Holland, Pakistan, Filippinerne, Polen, Saudi Arabien, S... og mere
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LYSOGENEAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIATyskland, Forenede Stater, Det Forenede Kongerige, Frankrig, Holland
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ShireAfsluttetSanfilippo syndrom | Mucopolysaccharidosis (MPS)Forenede Stater, Det Forenede Kongerige, Spanien, Tyskland, Frankrig, Italien, Holland
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Alexion PharmaceuticalsAfsluttetMucopolysaccharidosis IIIBForenede Stater, Det Forenede Kongerige, Spanien
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LYSOGENEAfsluttetMucopolysaccharidosis Type III A | Sanfilippo sygdom type AFrankrig
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LYSOGENEAfsluttetMucopolysaccharidosis Type III A | Sanfilippo sygdom type AFrankrig
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CENTOGENE GmbH RostockTrukket tilbageMetabolisme, medfødte fejl | Mucopolysaccharidosis type I | GargoylismeTyskland, Indien, Sri Lanka, Egypten
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ShireAfsluttetMucopolysaccharidosis (MPS)Det Forenede Kongerige, Holland
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Denali Therapeutics Inc.RekrutteringMucopolysaccharidosis Type IIIAForenede Stater
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Allievex CorporationAfsluttetMucopolysaccharidosis Type IIIB | MPS III BForenede Stater, Taiwan, Spanien, Colombia, Tyskland, Det Forenede Kongerige, Kalkun
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Allievex CorporationAktiv, ikke rekrutterendeMucopolysaccharidosis Type IIIB | MPS III BTyskland, Forenede Stater, Kalkun, Det Forenede Kongerige, Colombia, Spanien, Taiwan
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Alexion PharmaceuticalsAfsluttetMucopolysaccharidosis III, Type B (MPS IIIB) | Sanfilippo BDet Forenede Kongerige
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University Hospital HeidelbergAfsluttetMucopolysaccharidosis type I | Mucopolysaccharidosis Type II | Mestringsadfærd | Mucopolysaccharidosis Type III | AdfærdsforstyrrelserTyskland
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JCR Pharmaceuticals Co., Ltd.Aktiv, ikke rekrutterendeMucopolysaccharidosis IForenede Stater, Brasilien, Japan
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GOIZETBioMarin PharmaceuticalRekruttering
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University of California, San FranciscoRekrutteringMPS IVA | MPS VIForenede Stater
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Alexion PharmaceuticalsAfsluttetMPS IIIB (Sanfilippo Syndrome)Spanien, Holland, Det Forenede Kongerige, Forenede Stater, Brasilien
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Lundquist Institute for Biomedical Innovation at...Swedish Orphan Biovitrum; Cure Sanfilippo FoundationAfsluttet