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Kliniske forsøg med Muskeldystrofi, Oculopharyngeal
I alt 50263 resultater
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University of New MexicoUniversity of FloridaTrukket tilbageOculopharyngeal muskeldystrofi
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Bioblast Pharma Ltd.AfsluttetOculopharyngeal muskeldystrofiForenede Stater, Israel, Canada
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Bioblast Pharma Ltd.Trukket tilbage
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Hillel Yaffe Medical CenterRekruttering
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Rigshospitalet, DenmarkUkendtOculopharyngeal muskeldystrofiDanmark
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Bioblast Pharma Ltd.Afsluttet
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Benitec Biopharma, Inc.RekrutteringOculopharyngeal muskeldystrofiForenede Stater
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University of FloridaAfsluttet
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University of CalgaryMuscular Dystrophy CanadaTilmelding efter invitationMuskeldystrofier | Oculopharyngeal muskeldystrofi | Myopati; ArveligCanada
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Assistance Publique - Hôpitaux de ParisAssociation Française contre les Myopathies (AFM), ParisAfsluttetMuskeldystrofi, OculopharyngealFrankrig
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Hillel Yaffe Medical CenterUkendt
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University Hospital, CaenUniversity Hospital, Rouen; Centre Hospitalier Universitaire, Amiens; University... og andre samarbejdspartnereAfsluttetMuskeldystrofi, Oculopharyngeal | PtosisFrankrig
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Myotonic Dystrophy FoundationRekrutteringMyotonisk dystrofi | Myotonisk dystrofi 1 | Steinerts sygdom | Medfødt myotonisk dystrofi | PROMM (proksimal myotonisk myopati) | Steinerts sygdom | Dystrophia Myotonica 1 | Myotonisk dystrofi 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonisk dystrofi, medfødt | Myotonisk myopati,... og andre forholdForenede Stater
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National Heart, Lung, and Blood Institute (NHLBI)AfsluttetKardiomyopati, hypertrofisk | Muskeldystrofi, OculopharyngealForenede Stater
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Mayo ClinicNational Eye Institute (NEI)AfsluttetNethindesygdom | Bedste Vitelliform Macula Dystrophy | Bestrofinopati | Vitelliform makuladystrofi hos voksne | Autosomal Dominant VitreoretinalchoroidopatiForenede Stater
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Columbia UniversityNational Eye Institute (NEI); Centre Hospitalier National d'Ophtalmologie... og andre samarbejdspartnereRekrutteringRetinitis Pigmentosa | Bedste Vitelliform Macula DystrophyForenede Stater, Tyskland, Frankrig
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PYC TherapeuticsRekrutteringRetinitis Pigmentosa | Øjensygdomme, arvelig | Nethindedystrofier | Nethindedystrofistang | Retinal Dystrophy Rod ProgressiveForenede Stater, Australien
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University Hospital, BrestUkendtDuchenne Dystrofi MuskulærFrankrig
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Stealth BioTherapeutics Inc.AfsluttetFuchs' Corneal Endothelial Dystrophy (FCED)Forenede Stater
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Grete Andersen, MDAfsluttetHyperkalæmisk periodisk lammelse | Myotonia Congenita | Paramyotonia Congenita | Dystrophia Myotonica Type 1 | Kalium-forværret myotoniDanmark
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Vienna Institute for Research in Ocular SurgeryRekrutteringKort Dot Fingerprint DystrophyØstrig
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University Hospital, MontpellierUkendtDuchennes muskeldistrofi (DMD)Frankrig
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Stichting Achmea Slachtoffer en SamenlevingAfsluttetRSD (Reflex Sympathetic Dystrophy) | Algodystrofi | CRPS Type IHolland
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Manhattan Eye, Ear & Throat HospitalGenentech, Inc.AfsluttetPolypoid choroidal vaskulopati | Pseudoxanthoma Elasticum | Patologisk nærsynethed | Retinal angiomatøs spredning | Frakkers sygdom | Idiopatisk retinal telangiektasi | Multifokal choroiditis | Rubeosis Iridis | Von Hippel Lindaus sygdom | BEDSTE VITELLIFORM MACULAR DYSTROFI, MULTIFOKAL (lidelse)Forenede Stater
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Avidity Biosciences, Inc.RekrutteringMuskeldystrofier | Muskeldystrofi, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrofi | MKS | Facioscapulohumeral muskeldystrofi 1 | FSHD2 | FSHD1 | MKS2 | Fascioscapulohumeral muskeldystrofi | Fascioscapulohumeral muskeldystrofi type 1 | Fascioscapulohumeral muskeldystrofi type 2 | Dystrofier, Facioscapulohumeral... og andre forholdForenede Stater, Det Forenede Kongerige, Canada
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Healeon Medical IncTrukket tilbageFibromyalgi | RSD (Reflex Sympathetic Dystrophy) | CRPS - komplekst regionalt smertesyndrom type IForenede Stater, Honduras
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The Lowy Medical Research Institute LimitedUkendtMacula Pigment | Macular TeleangiectasiaTyskland
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Wyeth is now a wholly owned subsidiary of PfizerAfsluttetBeckers muskeldystrofi | Facioscapulohumeral muskeldystrofi | Limb-Girdle muskeldystrofiForenede Stater
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McMaster UniversityCanadian Institutes of Health Research (CIHR); Population Health Research... og andre samarbejdspartnereAktiv, ikke rekrutterendeKirurgi (hjerte) | Kirurgi (Major Vascular)Canada, Det Forenede Kongerige
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's... og andre samarbejdspartnereRekrutteringDuchennes muskeldystrofi | Beckers muskeldystrofi | Myotonisk dystrofi | Facioscapulohumeral muskeldystrofiForenede Stater
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University of North Carolina, Chapel HillNational Institute of Arthritis and Musculoskeletal and Skin Diseases... og andre samarbejdspartnereAfsluttetMuskeldystrofier | Duchennes muskeldystrofi | Beckers muskeldystrofi | Limb-Girdle muskeldystrofiForenede Stater
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IRCCS Eugenio MedeaRekrutteringMuskeldystrofier | Beckers muskeldystrofi | Lembælte muskeldystrofi | Facio-Scapulo-Humeral DystrofiItalien
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Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RekrutteringLem-bælte muskeldystrofi | Neuromuskulær; Lidelse, arvelig | Duchenne/Becker muskeldystrofiForenede Stater
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RekrutteringMuskeldystrofi | Myotonisk dystrofi type 2 | Myotonisk dystrofi type 1 | Myotonisk dystrofi | Facioscapulohumeral muskeldystrofi | Steinerts sygdom | Medfødt myotonisk dystrofi | PROMM (proksimal myotonisk myopati) | Myotonisk muskeldystrofiForenede Stater
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Rigshospitalet, DenmarkAfsluttetBeckers muskeldystrofi | Limb-Girdle Muskeldystrofi Type 2IDanmark
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Laurent ServaisSYSNAVRekrutteringDuchennes muskeldystrofi | Fascioscapulohumeral muskeldystrofiBelgien
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RekrutteringMuskeldystrofier | Beckers muskeldystrofi | Muskeldystrofi hos børn | Muskeldystrofi, BeckerForenede Stater, Det Forenede Kongerige
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Massachusetts General HospitalAfsluttetDuchennes muskeldystrofi | Dystrofinopati | Beckers muskeldystrofiForenede Stater
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University Hospital of North NorwayUniversity of Tromso; Norwegian Muscle Disease Association (FFM); Norwegian... og andre samarbejdspartnereAktiv, ikke rekrutterendeMuskeldystrofier | Lembælte muskeldystrofi | Lembælte muskeldystrofi, type 2I | Limb urdle muskeldystrofi R9 FKRP-relateretNorge
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Carl Zeiss Meditec, Inc.DataMed Devices Inc.AfsluttetTør AMD Med Macular DrusenForenede Stater
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)AfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofi | Lembælte muskeldystrofiForenede Stater
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Cooperative International Neuromuscular Research...United States Department of DefenseAfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofi | Lembælte muskeldystrofiForenede Stater, Japan, Canada
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)AfsluttetDuchennes muskeldystrofi | Beckers muskeldystrofi | Lembælte muskeldystrofiForenede Stater
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Politecnico di MilanoIRCCS Eugenio Medea; Villa Beretta Rehabilitation CenterAfsluttetMuskeldystrofier | Muskeldystrofi, Duchenne | Muskeldystrofi, Becker | Muskeldystrofi, ekstremitetsbælte type 2Italien
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteAfsluttetBeckers muskeldystrofi | Limb-Girdle Muskeldystrofi, Type 2A (Calpain-3-mangel) | Limb-Girdle Muskeldystrofi, Type 2B (Miyoshi Myopati, Dysferlin-mangel) | Limb-Girdle Muskeldystrofi, Type 2I (FKRP-mangel)Forenede Stater
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Northwestern UniversityAfsluttetBeckers muskeldystrofi | Lem-bælte muskeldystrofiForenede Stater
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Centre Hospitalier Universitaire de NiceRekrutteringFacioscapulohumeral muskeldystrofi 1Frankrig, Canada
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Hoffmann-La RocheRekrutteringFacioscapulohumeral muskeldystrofi (FSHD)Forenede Stater, Danmark, Det Forenede Kongerige, Italien
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Fulcrum TherapeuticsAktiv, ikke rekrutterendeFacioscapulohumeral muskeldystrofi (FSHD)Forenede Stater, Spanien, Italien, Danmark, Canada, Tyskland, Frankrig, Holland, Det Forenede Kongerige