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Kliniske forsøg med X-forbundet medfødt stationær natteblindhed
I alt 259 resultater
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University of New MexicoAfsluttetRetinitis Pigmentosa | Aldersrelateret makuladegeneration | Medfødt stationær natteblindhed | FarveblindhedForenede Stater
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Foundation Fighting BlindnessRekrutteringRetinitis Pigmentosa | Choroideræmi | Usher syndrom | Battens sygdom | Leber medfødt amaurose | Goldmann-Favre syndrom | Kearns-Sayre syndrom | Nethindesygdom | Bardet-Biedl syndrom | Stargardts sygdom | Kegledystrofi | Retinoschisis | Achromatopsi | Gyrate Atrofi | Øjensygdomme arvelig | Bassen-Kornzweig syndrom | Bedste sygdom | Koroidal dystrofi og andre forholdForenede Stater
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Newcastle-upon-Tyne Hospitals NHS TrustRekrutteringX-bundet myotubulær myopati | Centronukleær myopati | Myotubulær myopati | Myotubulær myopati 1 | Myotubulær (Centronuclear) myopati | Centronuclear Myopati, X-LinkedDet Forenede Kongerige
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... og andre samarbejdspartnereRekrutteringX Linked Myotubular MyopatiDet Forenede Kongerige, Canada, Forenede Stater
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Astellas Gene TherapiesAfsluttetX-bundet myotubulær myopatiForenede Stater, Frankrig, Det Forenede Kongerige, Canada, Tyskland
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University of FloridaAudentes TherapeuticsAfsluttetX-bundet myotubulær myopatiForenede Stater
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Astellas Gene TherapiesAfsluttetMænd med X-bundet myotubulær myopati (XLMTM)Forenede Stater, Det Forenede Kongerige
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrAfsluttet
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Edimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasiForenede Stater
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University Hospital ErlangenEdimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasiTyskland
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRekrutteringX-Linked Hypohidrotisk ektodermal dysplasi (XLHED)Forenede Stater, Spanien, Frankrig, Tyskland, Italien, Det Forenede Kongerige
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Edimer PharmaceuticalsAktiv, ikke rekrutterendeX-bundet hypohidrotisk ektodermal dysplasiForenede Stater, Det Forenede Kongerige, Frankrig, Tyskland, Italien
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Edimer PharmaceuticalsAfsluttetX-forbundet hypohidrotisk ektodermal dysplasiForenede Stater
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University of California, DavisUniversity of Alberta; St. Justine's HospitalRekrutteringNeuroadfærdsmæssige manifestationer | Genetiske sygdomme, X-forbundet | Intellektuel handicap | Fragilt X syndrom | Kønskromosomforstyrrelser | Fragilt X Mental Retardation Syndrome | Trinukleotid Gentag Udvidelse | Fra(X) syndrom | FXS | Mental retardering, X LinkedForenede Stater, Canada
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State University of New York - Upstate Medical...AfsluttetFamiliær encefalopati med neuroserpin-inklusionskroppe | X-bundet mental retardering | Medfødt lodret talus | Idiopatisk generaliseret epilepsi | Familiær demensForenede Stater
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Novartis PharmaceuticalsAfsluttet
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Edimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasi | Hypohidrotisk ektodermal dysplasiForenede Stater
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Edimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasi | Hypohidrotisk ektodermal dysplasiSpanien
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...AfsluttetFragilt X syndromForenede Stater
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Seaside Therapeutics, Inc.AfsluttetFragilt X syndromForenede Stater
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)AfsluttetFragilt X syndromForenede Stater
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Children's Hospital Medical Center, CincinnatiRekrutteringFragilt X syndromForenede Stater
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Esoterix Genetic Laboratories, LLCUkendtFragilt X syndromForenede Stater
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Sheba Medical CenterElMindA LtdRekrutteringFragilt X Associeret Tremor-ataxia Syndrome | FXTASIsrael
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Ovid Therapeutics Inc.AfsluttetFragilt X-syndrom (FXS)Forenede Stater
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Guido A. Davidzon, MD, SMTrukket tilbage
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Tetra Discovery PartnersAfsluttetFragilt X syndrom | Fra(X) syndrom | FXSForenede Stater
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Marinus PharmaceuticalsUniversity of California, Davis; U.S. Army Medical Research and Development...Afsluttet
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...AfsluttetFragilt X-syndrom (FXS)Forenede Stater
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Massachusetts General HospitalNational Institutes of Health (NIH)UkendtSund og rask | Fragilt X syndromForenede Stater
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Craig EricksonHealx LimitedRekrutteringFragilt X syndromForenede Stater
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Elizabeth Berry-KravisAfsluttetFragilt X syndromForenede Stater
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Novartis PharmaceuticalsAfsluttetFragilt X syndromForenede Stater, Spanien
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Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUkendt
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Hoffmann-La RocheAfsluttetFragilt X syndromForenede Stater
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Hoffmann-La RocheAfsluttetFragilt X syndromFrankrig, Spanien, Forenede Stater, Peru, Canada, Det Forenede Kongerige, Chile, Argentina, Mexico, Sverige
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Yolanda de Diego OteroAfsluttet
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Seaside Therapeutics, Inc.AfsluttetFragilt X syndromForenede Stater
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Seaside Therapeutics, Inc.AfsluttetFragilt X syndromForenede Stater
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IRCCS Fondazione Stella MarisRekrutteringFragilt X syndromItalien
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRekrutteringFragilt X syndromSerbien
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringFragilt X syndromForenede Stater
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Tetra Discovery PartnersRekrutteringFragilt X syndromForenede Stater
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Zynerba Pharmaceuticals, Inc.RekrutteringFragilt X syndromForenede Stater, Australien, Det Forenede Kongerige, Irland
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National Institute of Mental Health (NIMH)AfsluttetSunde frivillige | Fragilt X syndromForenede Stater
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Zynerba Pharmaceuticals, Inc.Tilmelding efter invitationFragilt X syndromForenede Stater, Det Forenede Kongerige, New Zealand, Australien
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis...Afsluttet
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Zynerba Pharmaceuticals, Inc.AfsluttetFragilt X syndromForenede Stater, New Zealand, Australien
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Children's Hospital Medical Center, CincinnatiRush University Medical CenterAfsluttet
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Novartis PharmaceuticalsAfsluttetFragilt X syndromForenede Stater, Schweiz, Tyskland, Australien, Canada, Danmark, Frankrig, Italien, Spanien, Det Forenede Kongerige