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- Registro de ensayos clínicos de EE. UU.
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Buscar ensayos clínicos para: genetic diseases and dysmorphic syndromes
Total 470971 resultados
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Eunice Kennedy Shriver National Institute of Child...ReclutamientoDesorden del espectro autista | Síndrome X frágil | Retraso en el desarrollo | Trastorno genético | Sindrome de AspergerEstados Unidos
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Eunice Kennedy Shriver National Institute of Child...TerminadoEnfermedad metabólica | Trastorno genéticoEstados Unidos
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National Institute of Diabetes and Digestive and...University of FloridaTerminado
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UCSF Benioff Children's Hospital OaklandTerminadoAnemia falciforme | Necrosis avascular óseaEstados Unidos
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Susan P. PerrineIcahn School of Medicine at Mount Sinai; University of Illinois at Chicago; Boston... y otros colaboradoresTerminadoAnemia falciforme | Úlceras de la pielEstados Unidos
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FDA Office of Orphan Products DevelopmentUniversity of North CarolinaTerminado
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Children's Hospital Medical Center, CincinnatiTerminadoFibrosis quísticaEstados Unidos, Italia
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FDA Office of Orphan Products DevelopmentMedical University of South CarolinaTerminado
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityTerminado
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University of North CarolinaTerminado
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FDA Office of Orphan Products DevelopmentCochlearTerminado
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FDA Office of Orphan Products DevelopmentTerminadoFibrosis quística | Infección bacteriana
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University of North CarolinaTerminadoAnemia falciformeEstados Unidos
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Ohio State UniversityTerminadoDistrofia Muscular Facioescapulohumeral
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University of IowaTerminado
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Boston Children's HospitalTerminadoAnemia falciformeEstados Unidos
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FDA Office of Orphan Products DevelopmentSciClone PharmaceuticalsTerminado
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University of North CarolinaTerminadoOsteoporosis | Fibrosis quísticaEstados Unidos
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University of PennsylvaniaTerminadoEnfermedad por deficiencia de ornitina transcarbamilasa
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Mast Therapeutics, Inc.CytRxTerminado
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University of Alabama at BirminghamNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Terminado
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University of Alabama at BirminghamTerminado
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Fairview University Medical CenterTerminadoSíndromes de deficiencia inmunológica | Inmunodeficiencia Común Variable | Inmunodeficiencia Combinada Severa | Enfermedad Granulomatosa Crónica | Linfohistiocitosis hemofagocítica | Síndrome de Wiskott-Aldrich | Enfermedad de injerto contra huésped | Agammaglobulinemia ligada al X | Síndrome de Chediak-Higashi y otras condicionesEstados Unidos
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University of UtahTerminadoFibrosis quísticaEstados Unidos
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Fred Hutchinson Cancer CenterTerminadoAnemia falciformeEstados Unidos
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National Institute of Neurological Disorders and...Jefferson Medical College of Thomas Jefferson UniversityTerminadoSíndrome de TurnerEstados Unidos
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University of UtahTerminadoFibrosis quísticaEstados Unidos
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Herbert Irving Comprehensive Cancer CenterTerminado
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Boston UniversityTerminadoBeta-talasemiaEstados Unidos, Reino Unido
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National Center for Research Resources (NCRR)Indiana University School of MedicineTerminado
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National Institute of Neurological Disorders and...Baylor College of MedicineTerminadoSíndrome de Prader-Willi | Síndrome de DiGeorge | Síndrome de Williams | Síndrome de Angelman | Síndrome de Smith-Magenis | Anomalías cromosómicas | Síndrome de ShprintzenEstados Unidos
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National Center for Research Resources (NCRR)Children's Hospital Medical Center, CincinnatiDesconocidoEnfermedades Gastrointestinales | Fibrosis quística | ColestasisEstados Unidos
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National Center for Research Resources (NCRR)Northwestern UniversityTerminadoEpidermolisis Bullosa Adquisita
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National Center for Research Resources (NCRR)University of California, Los AngelesTerminadoTrombocitopenia | Errores innatos del metabolismo | Leucodistrofia metacromática | Anemia de Fanconi | Talasemia Mayor | Aplasia pura de glóbulos rojosEstados Unidos
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National Center for Research Resources (NCRR)Yale UniversityTerminadoTelangiectasia hemorrágica hereditaria
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National Center for Research Resources (NCRR)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rockefeller UniversityTerminadoEpidermólisis Bullosa
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National Center for Research Resources (NCRR)Indiana University School of MedicineDesconocido
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National Center for Research Resources (NCRR)University of North CarolinaTerminadoFibrosis quística | Atypical Mycobacterium Infection
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National Center for Research Resources (NCRR)University of PittsburghTerminadoDeficiencia de alfa 1-antitripsinaEstados Unidos
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National Center for Research Resources (NCRR)University of RochesterTerminadoEspondiloartritis anquilosante
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National Center for Research Resources (NCRR)University of UtahTerminadoFibrosis quísticaEstados Unidos
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Fairview University Medical CenterDesconocidoMucopolisacaridosis I | Enfermedad de Niemann-Pick | Mucopolisacaridosis VI | Enfermedad de Wolman | Adrenoleucodistrofia | Leucodistrofia metacromática | Complicaciones pulmonares | Fucosidosis | Leucodistrofia de células globoides | Enfermedad de Gaucher | Manosidosis | Enfermedad de células IEstados Unidos
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National Center for Research Resources (NCRR)Baylor College of MedicineTerminado
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National Center for Research Resources (NCRR)Yale UniversityTerminado
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National Center for Research Resources (NCRR)Children's Hospital of PhiladelphiaTerminadoOsteoporosis | Osteopenia | Talasemia Mayor
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National Center for Research Resources (NCRR)University of PennsylvaniaTerminado
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National Center for Research Resources (NCRR)University of VermontTerminadoTelangiectasia Hemorrágica Hereditaria
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National Center for Research Resources (NCRR)Shirley Ryan AbilityLabTerminadoAnemia falciforme
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National Center for Research Resources (NCRR)Ann & Robert H Lurie Children's Hospital of ChicagoTerminadoDefectos Cardíacos Congénitos | Tetralogía de Fallot | Estenosis de válvula pulmonar | Hipoparatiroidismo | Atresia pulmonar | Defectos cardíacos conotruncales
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National Center for Research Resources (NCRR)University of MichiganTerminado