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Studi clinici sponsorizzati da Muscular Dystrophy Association Singapore
Totale 39 risultati
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Muscular Dystrophy AssociationSconosciuto
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Insmed IncorporatedMuscular Dystrophy AssociationCompletato
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PTC TherapeuticsMuscular Dystrophy AssociationCompletatoDistrofia muscolare di DuchenneStati Uniti
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Boston Children's HospitalMuscular Dystrophy AssociationReclutamentoMiopatia centronucleare | Miopatia miotubulare | Miopatia nemalina | Malattia del nucleo centrale | Sproporzione congenita del tipo di fibra | Malattia multiminicore | Distrofia muscolare della colonna vertebrale rigida | Miopatia congenita non definitaStati Uniti
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Massachusetts General HospitalMuscular Dystrophy AssociationCompletatoSclerosi laterale amiotroficaStati Uniti
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Virginia Commonwealth UniversityMuscular Dystrophy AssociationAttivo, non reclutanteLGMD2E | LGMD2I | LGMD2A | LGMD2B | LGMD2C | LGMD1B | LGMD1C | LGMD1D | LGMD1E | LGMD1F | LGMD1G | LGMD1H | LGMD2D | LGMD2F | LGMD2G | LGMD2J | LGMD2K | LGMD2L | LGMD2M | LGMD2N | LGMD2O | LGMD2P | LGMD2Q | LGMD2S | LGMD2T | LGMD2U | LGMD2W | LGMD2X | LGMD2YStati Uniti
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Ionis Pharmaceuticals, Inc.ALS Association; Muscular Dystrophy AssociationCompletatoSclerosi Laterale Amiotrofica FamiliareStati Uniti
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompletato
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Kevin FlaniganMuscular Dystrophy AssociationTerminato
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Barrow Neurological InstituteALS Association; Muscular Dystrophy Association; Synapse BiomedicalCompletatoSclerosi Laterale Amiotrofica (SLA)Stati Uniti
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Wayne State UniversityMuscular Dystrophy Association; Charcot-Marie-Tooth AssociationCompletatoMalattia di Charcot-Marie-Tooth, tipo IaStati Uniti
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Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletatoDistrofie muscolari, dei cingoli (CONFERMATO GENETICAMENTE)Stati Uniti
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Weill Medical College of Cornell UniversityMuscular Dystrophy AssociationCompletatoSclerosi Laterale Amiotrofica FamiliareStati Uniti, Germania, Italia, Svezia
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Nanyang Technological UniversityKK Women's and Children's Hospital; Club Rainbow Singapore; Muscular Dystrophy... e altri collaboratoriSconosciutoGenitore di bambino con malattia cronica pericolosa per la vitaSingapore
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletatoDistrofia muscolare di Duchenne | Atrofia muscolare spinale di tipo 3Stati Uniti
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Terry L. WahlsMuscular Dystrophy AssociationRitiratoSclerosi laterale amiotrofica | Modifica della dieta
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Forbes Norris MDA/ALS Research CenterMuscular Dystrophy AssociationCompletatoSclerosi laterale amiotroficaStati Uniti
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Johns Hopkins UniversityMuscular Dystrophy Association; Actio Biosciences, IncReclutamento
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Forbes Norris MDA/ALS Research CenterMuscular Dystrophy AssociationCompletatoSclerosi laterale amiotroficaStati Uniti
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National Center for Research Resources (NCRR)Muscular Dystrophy AssociationCompletatoSclerosi laterale amiotroficaStati Uniti
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Indiana University School of MedicineMuscular Dystrophy AssociationCompletatoDistrofia muscolare | Aritmia | Morte cardiaca improvvisaStati Uniti
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University of IowaNational Institute of Neurological Disorders and Stroke (NINDS); Muscular Dystrophy...CompletatoMalattia di Charcot Marie ToothStati Uniti
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US Department of Veterans AffairsMuscular Dystrophy AssociationCompletatoSclerosi laterale amiotroficaStati Uniti
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Muscular Dystrophy AssociationCompletatoDistrofia muscolare dei cingoliStati Uniti
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Muscular Dystrophy AssociationCompletato
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PathMaker Neurosystems Inc.Spaulding Rehabilitation Hospital; Muscular Dystrophy Association; Sean M. Healey...ReclutamentoSclerosi laterale amiotroficaStati Uniti
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriCompletatoAtrofia muscolare spinale di tipo 3 | Miopatia mitocondrialeStati Uniti
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University of IowaUniversity of South Florida; National Institute of Neurological Disorders and... e altri collaboratoriCompletatoMalattia di Charcot Marie Tooth | Neuropatia periferica ereditariaStati Uniti, Regno Unito
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King's College Hospital NHS TrustKing's College London; Barts & The London NHS Trust; University Hospital Southampton... e altri collaboratoriCompletato
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University of... e altri collaboratoriCompletatoDistrofia miotonica di tipo 1Stati Uniti
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... e altri collaboratoriReclutamentoSclerosi laterale amiotrofica | Sclerosi Laterale Primaria | Atrofia muscolare progressiva | SLA-demenza frontotemporaleStati Uniti
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... e altri collaboratoriReclutamentoDistrofia muscolare di DuchenneStati Uniti
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute e altri collaboratoriCompletatoDistrofia muscolare di DuchenneStati Uniti, Australia, Italia
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University of IowaChildren's Hospital of Philadelphia; University College London Hospitals; National... e altri collaboratoriReclutamentoMalattia di Charcot Marie ToothStati Uniti, Regno Unito, Australia, Italia
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University of... e altri collaboratoriAttivo, non reclutanteDeficit di timidina chinasi 2 | Sindrome da deplezione del DNA mitocondriale 2 Tipo miopaticoStati Uniti
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University College London HospitalsJohns Hopkins University; Children's Hospital of Philadelphia; University of Pennsylvania e altri collaboratoriCompletatoMalattia di Charcot-Marie-ToothRegno Unito
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University of IowaJohns Hopkins University; University of Colorado, Denver; King's College Hospital... e altri collaboratoriReclutamentoMalattia di Charcot-Marie-Tooth, tipo Ia (disturbo) | HMSNStati Uniti, Italia, Regno Unito, Australia
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriIscrizione su invitoIperossaluria primaria di tipo 3 | Diabete mellito | Emofilia A | Emofilia B | Intolleranza ereditaria al fruttosio | Fibrosi cistica | Carenza di fattore VII | Fenilchetonuria | Anemia falciforme | Sindrome di Dravet | Distrofia muscolare di Duchenne | Sindrome di Prader-Willi | Sindrome dell'X fragile | Malattia granulomatosa... e altre condizioniStati Uniti
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Michael ShyJohns Hopkins University; University of Colorado, Denver; King's College Hospital... e altri collaboratoriReclutamentoMalattia di Charcot Marie ToothStati Uniti, Australia, Italia, Regno Unito