例：Heart Attack

モリブデン補因子欠乏症の臨床試験

合計6件

NCT02629393

採用

Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A

条件：Molybdenum Cofactor Deficiency, Type A
NCT01640717

完了しました

A Retrospective, Observational, Noninterventional Data Collection Study for Patients With Molybdenum Cofactor Deficiency Who Have Been Previously Treated With Cyclic Pyranopterin Monophosphate (cPMP)

条件：Molybdenum Cofactor Deficiency
NCT00957749

引きこもった

Study of cPMP (Precusor Z) to Treat Molybdenum Cofactor Deficiency (MoCD) Type A

条件：Molybdenum Cofactor Deficiency Type A
NCT02047461

採用ではなくアクティブ

Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treated With rcPMP

条件：Molybdenum Cofactor Deficiency, Type A
NCT01735188

完了しました

A Natural History Study of Molybdenum Cofactor and Isolated Sulfite Oxidase Deficiencies

条件：Molybdenum Cofactor Deficiency; Isolated Sulfite Oxidase Deficiency
NCT01894165

完了しました

Phase 1 Single Dose Study of ALXN1101 in Healthy Volunteers

条件：Molybdenum Cofactor Deficiency (MoCD); Rare Autosomal Recessive Disorder; Deficiency of Activity of Molybdenum-dependent Enzymes (Sulfite Oxidase [SOX], Xanthine Dehydrogenase, and Aldehyde Oxidase)