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아미노산 대사, 선천적 오류에 대한 임상 시험
총 4741 건
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National Human Genome Research Institute (NHGRI)모병
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ModernaTX, Inc.모병
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.종료됨
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome Medical종료됨
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HemoShear Therapeutics종료됨
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King Abdullah International Medical Research Center완전한
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University of California... 그리고 다른 협력자들종료됨
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.모집하지 않고 적극적으로
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PTC TherapeuticsGenzyme, a Sanofi Company종료됨
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University of California...모병
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National Human Genome Research Institute (NHGRI)모병
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Recordati Rare Diseases모병프로피온산혈증 | 메틸말론산혈증프랑스, 스페인, 이탈리아, 영국, 노르웨이, 독일, 스웨덴
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CoA Therapeutics, Inc., a BridgeBio company종료됨건강한 자원봉사자 | 프로피온산혈증 | 메틸말론산혈증 | 유기산혈증미국
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National Taiwan University Hospital알려지지 않은
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)정지된
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Target PharmaSolutions, Inc.Recordati Rare Diseases초대로 등록
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer Center완전한대사, 선천적 오류 | 메티오닌 아데노실트랜스퍼라제 결핍
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University of LiverpoolLiverpool University Hospitals NHS Foundation Trust완전한
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Nicola LongoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institutes...완전한
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.모병
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Liverpool University Hospitals NHS Foundation Trust모병
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Liverpool John Moores UniversityLiverpool University Hospitals NHS Foundation Trust아직 모집하지 않음알캅톤뇨증
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University of MiamiHRSA/Maternal and Child Health Bureau완전한
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Origin Biosciences완전한몰리브덴 보조인자 결핍 | 고립된 아황산염 산화효소 결핍증스페인, 이스라엘, 미국, 영국, 캐나다, 네덜란드, 독일, 사우디 아라비아, 튀니지, 일본, 이탈리아, 말레이시아, 폴란드, 칠면조
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National Center for Research Resources (NCRR)Johns Hopkins University완전한아미노산 대사, 선천적 오류
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation Trust완전한
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Dr. Schär AG / SPA완전한
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Sanofi모병
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Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTD모병
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APR Applied Pharma Research s.a.모병
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University Children's Hospital, ZurichUniversity Children's Hospital Basel; UChildrenVienna; Insel Gruppe AG, University Hospital...모병
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University Hospital, Lille아직 모집하지 않음