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선천성 아미노산 대사 장애에 대한 임상 시험
총 43749 건
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Center Trials & TreatmentOleg Martynenko종료됨코로나바이러스감염증-19 : 코로나19 | 사스 코로나바이러스 2 | 후린 | RGMc 처리 | PACE(Paired Basic Amino Acid Cleaving Enzyme)인도, 미국, 우크라이나
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ModernaTX, Inc.모병
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.종료됨
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National Human Genome Research Institute (NHGRI)모병
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome Medical종료됨
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HemoShear Therapeutics종료됨
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King Abdullah International Medical Research Center완전한
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University of California... 그리고 다른 협력자들종료됨
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National Human Genome Research Institute (NHGRI)모병
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Recordati Rare Diseases모병프로피온산혈증 | 메틸말론산혈증프랑스, 스페인, 이탈리아, 영국, 노르웨이, 독일, 스웨덴
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.모집하지 않고 적극적으로
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PTC TherapeuticsGenzyme, a Sanofi Company종료됨
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University of California...모병
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CoA Therapeutics, Inc., a BridgeBio company종료됨건강한 자원봉사자 | 프로피온산혈증 | 메틸말론산혈증 | 유기산혈증미국
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National Taiwan University Hospital알려지지 않은
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Target PharmaSolutions, Inc.Recordati Rare Diseases초대로 등록
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.모병
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Liverpool University Hospitals NHS Foundation Trust모병
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Nicola LongoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institutes...완전한
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)정지된
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National Center for Research Resources (NCRR)Johns Hopkins University완전한아미노산 대사, 선천적 오류
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Nutricia Research완전한
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Horizon Therapeutics, LLC완전한우레아 순환 장애미국, 스페인, 이탈리아, 스위스
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University of LiverpoolLiverpool University Hospitals NHS Foundation Trust완전한
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer Center완전한대사, 선천적 오류 | 메티오닌 아데노실트랜스퍼라제 결핍
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Liverpool John Moores UniversityLiverpool University Hospitals NHS Foundation Trust아직 모집하지 않음알캅톤뇨증
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Istanbul University - Cerrahpasa (IUC)완전한
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University of MiamiHRSA/Maternal and Child Health Bureau완전한
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Children's National Research InstituteBoston Children's Hospital모병
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Cytonet GmbH & Co. KGCRS Clinical Research Services Mannheim GmbH완전한
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University of South FloridaNational Institutes of Health (NIH)완전한
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare Diseases Clinical Research Network 그리고 다른 협력자들완전한아미노산 대사, 선천적 오류 | 우레아 순환 장애 | 아르기니노숙신산뇨증미국