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Kliniske studier på Ceroid Storage Disease
Totalt 374723 resultater
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University of RochesterRekrutteringBatten sykdom | Nevronal ceroid lipofuscinose | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3 | Neuronal Ceroid Lipofuscinosis CLN5 | Neuronal Ceroid Lipofuscinosis CLN1 | Neuronal Ceroid Lipofuscinosis CLN2 | Neuronal Ceroid Lipofuscinosis CLN7 | Neuronal Ceroid Lipofuscinosis... og andre forholdForente stater
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Eunice Kennedy Shriver National Institute of Child...RekrutteringBatten sykdom | Juvenil Neuronal Ceroid Lipofuscinosis (CLN3)Forente stater
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Amicus TherapeuticsAvsluttetBatten sykdom | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3Forente stater
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Weill Medical College of Cornell UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National... og andre samarbeidspartnereFullførtBatten sykdom | Sen Infantil Neuronal Ceroid LipofuscinosisForente stater
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Weill Medical College of Cornell UniversityAvsluttetBatten sykdom | Sen Infantil Neuronal Ceroid LipofuscinosisForente stater
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Amicus TherapeuticsFullførtVariant sen-infantil neuronal ceroid lipofuscinoseForente stater
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BioMarin PharmaceuticalAktiv, ikke rekrutterendeSen-infantil neuronal ceroid lipofuscinose type 2Forente stater
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)FullførtBatten sykdom | Sen-infantil neuronal ceroid lipofuscinoseForente stater
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Weill Medical College of Cornell UniversityFullførtBatten sykdom | Sen Infantil Neuronal Ceroid LipofuscinosisForente stater
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Weill Medical College of Cornell UniversityNathan's Battle FoundationFullførtBatten sykdom | Sen Infantil Neuronal Ceroid LipofuscinosisForente stater
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BioMarin PharmaceuticalFullførtBatten sykdom | CLN2 sykdom | Sen-infantil neuronal ceroid lipofuscinose type 2 | Jansky-Bielschowskys sykdomForente stater, Italia, Tyskland, Storbritannia
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REGENXBIO Inc.TilbaketrukketSen-infantil neuronal ceroid lipofuscinose type 2 (CLN2)
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BioMarin PharmaceuticalFullførtBatten sykdom | CLN2 sykdom | Sen-infantil neuronal ceroid lipofuscinose type 2 | Jansky-Bielschowskys sykdom | CLN2 lidelseForente stater, Tyskland, Italia, Storbritannia
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BioMarin PharmaceuticalFullførtBatten sykdom | CLN2 sykdom | Sen-infantil neuronal ceroid lipofuscinose type 2 | Jansky-Bielschowskys sykdom | CLN2 lidelseForente stater, Tyskland, Italia, Storbritannia
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Neurogene Inc.RekrutteringNeuronal Ceroid Lipofuscinosis CLN5Forente stater, Storbritannia
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Polaryx Therapeutics, Inc.Har ikke rekruttert ennåJuvenil Neuronal Ceroid Lipofuscinosis
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REGENXBIO Inc.Aktiv, ikke rekrutterendeNevronal ceroid lipofuscinose type 2Storbritannia
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University of RochesterBatten Disease Support and Research Assocation (BDSRA)FullførtJuvenil Neuronal Ceroid LipofuscinosisForente stater
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StemCells, Inc.FullførtNevronal ceroid lipofuscinoseForente stater
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Eunice Kennedy Shriver National Institute of Child...FullførtInfantil Neronal Ceroid LipofuscinosisForente stater
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REGENXBIO Inc.TilbaketrukketNeuronal Ceroid Lipofuscinosis Type 2 (CLN2)
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David L Rogers, MDAktiv, ikke rekrutterendeNevronal ceroid lipofuscinose type 2Forente stater
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Neurogene Inc.RekrutteringCeroid Lipofuscinosis, Neuronal 5Forente stater
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Jessica ScherrBioMarin PharmaceuticalPåmelding etter invitasjonBatten sykdom | Nevronale ceroid-lipofuscinoser | CLN2Forente stater
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StemCells, Inc.TilbaketrukketNevronal ceroid lipofuscinoseForente stater
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IRCCS Fondazione Stella MarisFullførtNevronale ceroid-lipofuscinoserItalia
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Nationwide Children's HospitalMassachusetts General HospitalFullførtNevronal ceroid lipofuscinose | Battens sykdomForente stater
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Eunice Kennedy Shriver National Institute of Child...RekrutteringNiemann-Pick sykdomstype C1 | Juvenil Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz syndrom | Kreatin Transporter mangelForente stater
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Children's Hospital of Orange CountyAktiv, ikke rekrutterendeNevronale ceroid-lipofuscinoser | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar ataksi, autosomal recessiv 7Forente stater
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Nadir Hastalıkları Araştırma DerneğiRekrutteringNeuronal Ceroid Lipofuxinosis Type2 (CLN2)Tyrkia
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Hannah ChoeNational Cancer Institute (NCI); PlexxikonFullførtAkutt graft versus vertssykdom | Steroid Refractory Graft Versus Host DiseaseForente stater
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Emily de los ReyesRekrutteringBatten sykdom | CLN6Forente stater
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Universidade do PortoHospital Sao JoaoRekrutteringCarotis stenose | Carotis aterosklerose | Retinal sykdom | Choroid sykdomPortugal
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Weill Medical College of Cornell UniversityNathan's Battle FoundationFullførtBatten sykdom | Sen-infantil neuronal ceroid lipfuscinose
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Universitätsklinikum Hamburg-EppendorfRekrutteringBatten sykdom | Nevronal ceroid lipofuscinose | CLN1 sykdom | CLN2 sykdom | CLN3 sykdom | CLN4 sykdom | CLN5 sykdom | CLN6 sykdom | CLN7 sykdom | CLN8 sykdom | CLN10 sykdom | CLN11 sykdom | CLN12 sykdom | CLN13 sykdom | CLN14 sykdomTyskland
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RekrutteringHematopoetisk og lymfoid celle-neoplasma | Steroid Refractory Graft Versus Host DiseaseForente stater
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Shaare Zedek Medical CenterUkjentCarotis stenose | Carotis endarterektomi | Choroid
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Renmin Hospital of Wuhan UniversityRekruttering
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Fondation Ophtalmologique Adolphe de RothschildFullført
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Zhongshan Ophthalmic Center, Sun Yat-sen UniversityFullført
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The Second People's Hospital of FoshanRekruttering
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The Second People's Hospital of FoshanHar ikke rekruttert ennå
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The First Affiliated Hospital with Nanjing Medical...Har ikke rekruttert ennå
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T.C. ORDU ÜNİVERSİTESİFullførtGrå stær | Choroid sykdom | Epinefrin toksisitet | Karbakol bivirkningTyrkia
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Alexion PharmaceuticalsFullførtLysosomal Acid Lipase-mangel | Cholesterol Ester Storage Disease (CESD)Forente stater, Storbritannia, Frankrike, Canada, Tsjekkisk Republikk, Italia, Polen, Sveits
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Navy Medical Center San DiegoHar ikke rekruttert ennåSteroid oftalmisk innlegg
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Shahid Beheshti University of Medical SciencesUkjentPupill Centroid ShiftIran, den islamske republikken
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Shaare Zedek Medical CenterUkjentRetina, Choroid, Sclera
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AstraZenecaFullførtCarotid Intima- MedietykkelseIndia