氨基酸代谢,先天性错误的临床试验
总计4741个结果
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ModernaTX, Inc.招聘中
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.终止
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome Medical终止
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King Abdullah International Medical Research Center完全的
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University of California,... 和其他合作者终止
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PTC TherapeuticsGenzyme, a Sanofi Company终止
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University of California, San...招聘中
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National Human Genome Research Institute (NHGRI)招聘中
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Recordati Rare Diseases招聘中
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CoA Therapeutics, Inc., a BridgeBio company终止
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)暂停
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Target PharmaSolutions, Inc.Recordati Rare Diseases邀请报名
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University of LiverpoolLiverpool University Hospitals NHS Foundation Trust完全的
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer Center完全的新陈代谢,先天性错误 | 甲硫氨酸腺苷转移酶缺乏症
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.招聘中
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Liverpool University Hospitals NHS Foundation Trust招聘中
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Nicola LongoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institutes...完全的
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University of MiamiHRSA/Maternal and Child Health Bureau完全的
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Liverpool John Moores UniversityLiverpool University Hospitals NHS Foundation Trust尚未招聘
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation Trust完全的
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Origin Biosciences完全的钼辅助因子缺乏症 | 孤立性亚硫酸盐氧化酶缺乏症西班牙, 以色列, 美国, 英国, 加拿大, 荷兰, 德国, 沙特阿拉伯, 突尼斯, 日本, 意大利, 马来西亚, 波兰, 火鸡
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National Center for Research Resources (NCRR)Johns Hopkins University完全的氨基酸代谢,先天性错误
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Children's Hospital of Fudan UniversityHedu Biotechnology (Shanghai) Co., LTD招聘中
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APR Applied Pharma Research s.a.招聘中
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University Children's Hospital, ZurichUniversity Children's Hospital Basel; UChildrenVienna; Insel Gruppe AG, University Hospital Bern招聘中