先天性氨基酸代谢障碍的临床试验
总计43740个结果
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ModernaTX, Inc.招聘中
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.终止
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome Medical终止
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King Abdullah International Medical Research Center完全的
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Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University of California,... 和其他合作者终止
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National Human Genome Research Institute (NHGRI)招聘中
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Recordati Rare Diseases招聘中
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University of California, San...招聘中
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PTC TherapeuticsGenzyme, a Sanofi Company终止
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CoA Therapeutics, Inc., a BridgeBio company终止
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Target PharmaSolutions, Inc.Recordati Rare Diseases邀请报名
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Recordati Rare DiseasesTarget PharmaSolutions, Inc.招聘中
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Liverpool University Hospitals NHS Foundation Trust招聘中
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Nicola LongoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National Institutes...完全的
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Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)暂停
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National Center for Research Resources (NCRR)Johns Hopkins University完全的氨基酸代谢,先天性错误
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University of LiverpoolLiverpool University Hospitals NHS Foundation Trust完全的
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer Center完全的新陈代谢,先天性错误 | 甲硫氨酸腺苷转移酶缺乏症
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Liverpool John Moores UniversityLiverpool University Hospitals NHS Foundation Trust尚未招聘
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University of MiamiHRSA/Maternal and Child Health Bureau完全的
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University of South FloridaNational Institutes of Health (NIH)完全的
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Children's National Research InstituteBoston Children's Hospital招聘中
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Cytonet GmbH & Co. KGCRS Clinical Research Services Mannheim GmbH完全的
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD); Rare... 和其他合作者完全的