Toni-Debre-Fanconi Syndrome的临床试验
总计101个结果
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Dana-Farber Cancer Institute未知
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National Center for Research Resources (NCRR)James Whitcomb Riley Hospital for Children完全的血小板减少症 | 先天性角化不良 | 范可尼贫血 | 施瓦克曼综合症
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Fairview University Medical Center完全的骨髓增生异常综合征 | 白血病,淋巴细胞性,急性 | 范可尼贫血 | 白血病,非淋巴细胞性,急性美国
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of Texas, Southwestern...终止
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute (NHLBI)完全的先前治疗过的骨髓增生异常综合征 | 范可尼贫血 | 新生骨髓增生异常综合征 | 缓解期急性髓性白血病美国, 巴西
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CENTOGENE GmbH Rostock撤销
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National Center for Research Resources (NCRR)University of California, San Diego完全的范可尼综合症 | 胱氨酸增多症
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University Hospital Freiburg完全的骨髓增生异常综合征 | 范可尼贫血 | 先天性角化不良 | 皮尔逊骨髓-胰腺综合征 | Shwachman-diamond综合征西班牙, 德国, 瑞士, 奥地利, 荷兰, 意大利, 捷克共和国, 比利时, 丹麦, 爱尔兰
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Masonic Cancer Center, University of Minnesota完全的
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Masonic Cancer Center, University of Minnesota终止
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)终止
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.完全的
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor Consortium终止
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Novartis Pharmaceuticals完全的骨髓增生异常综合征 | 范可尼综合症 | 贫血,再生障碍性 | Β-地中海贫血 | 贫血,Diamond-Blackfan美国
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Masonic Cancer Center, University of Minnesota招聘中
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Assistance Publique - Hôpitaux de ParisEuroFancolen完全的
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)完全的
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical Center, Cincinnati完全的
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)完全的
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products Development完全的
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Masonic Cancer Center, University of Minnesota完全的
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERER完全的
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, Cincinnati完全的
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy, Baylor College...终止
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Eisai Inc.可用的Lennox Gastaut综合症 | 原发性全身性强直-阵挛性或部分性发作比利时, 智利, 爱沙尼亚, 匈牙利, 拉脱维亚, 立陶宛, 波兰, 西班牙
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer Center招聘中
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de la Fundación Jiménez... 和其他合作者完全的
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TESS Research FoundationBrown University; Stanford University; University of Texas Southwestern Medical Center招聘中癫痫 | 运动障碍 | 罕见病 | 遗传性疾病 | 柠檬酸盐转运体缺陷 | SLC13A5 缺陷 | EIEE25 | Kohlschutter-Tonz 综合征(非 ROGDI) | 柠檬酸盐转运蛋白紊乱 | DEE25美国