이 페이지는 자동 번역되었으며 번역의 정확성을 보장하지 않습니다. 참조하십시오 영문판 원본 텍스트의 경우.

Peritransplant Deoxyspergualin in Islet Transplantation in Type 1 Diabetes

Peritransplant Deoxyspergualin in Islet Transplantation in Type 1 Diabetes (CIT-03)

Type 1 diabetes is an autoimmune disease in which the insulin-producing pancreatic beta cells are destroyed, resulting in poor blood sugar control. The purpose of this study is to assess the safety and efficacy of deoxyspergualin (DSG), an immunosuppressant drug, on post-transplant islet function in people with type 1 diabetes who have not responded to intensive insulin therapy.

연구 개요

상세 설명

Type 1 diabetes, also known as insulin-dependent diabetes, is a chronic disease in which the pancreas produces insufficient insulin to properly regulate blood sugar levels. Hypoglycemia, low blood sugar, and hyperglycemia, high blood sugar, can lead to significant complications in people with type 1 diabetes. Intensive insulin therapy has been shown to reduce the risk of chronic complications in people who achieve near normalization of glycemia. However, this therapy is labor intensive, difficult to implement, and associated with an increased frequency of severe hypoglycemia. Transplantation of islets from a healthy pancreas has been successful in restoring normal blood sugar levels and has led to initial insulin independence in people with type 1 diabetes. Rejection of these islets by the recipient's immune system, however, makes the treatment ineffective within a couple of years. Immunosuppressant drugs may be an effective way to maintain islet function post-transplant. The purpose of this study is to assess the safety and efficacy of an immunosuppressive regimen that includes DSG on post-transplant islet function in people with type 1 diabetes who have not responded to intensive insulin therapy. The study will also seek to improve the understanding of determinants of success and failure of islet transplants for type 1 diabetes.

Following screening procedures and 2 days prior to islet transplant, participants will be randomly assigned to either this Phase 2 trial or a multicenter Phase 3 trial. Participants in this study will receive up to three separate islet transplants. They will begin receiving antithymocyte globulin (ATG) and sirolimus 2 days prior to the first islet transplant. ATG will continue to be given until Day 2 post-transplant. Participants will continue taking sirolimus for the duration of the study. On the day of transplant, participants will receive DSG and etanercept, in addition to ATG and sirolimus. The DSG infusion will be administered over 3 hours and will immediately precede the islet transplant. Participants will continue receiving daily 3-hour infusions of DSG through Day 6 post-transplant. Etanercept will also be administered on Days 3, 7, and 10 post-transplant. Tacrolimus will be administered on Day 1 post-transplant and continued throughout the study.

Transplantations will involve an inpatient hospital stay and infusion of islets into a branch of the portal vein. Participants who do not achieve or maintain insulin independence by Day 75 post-transplant will be considered for a second islet transplant. Participants who remain dependent on insulin for longer than 1 month after the second transplant and who show partial graft function will be considered for a third transplant. Daclizumab or basiliximab will be used in place of ATG for the second and third transplants, if they are necessary. Participants who do not meet the criteria for a subsequent transplant and do not have a functioning graft will enter a reduced follow-up period.

There will be up to 21 study visits following each transplant. A physical exam, review of adverse events, blood collection, urine tests, and measures of immunosuppression levels will occur at most visits. An abdominal ultrasound and glomerular filtration rate testing will occur at some study visits. Participants will also self-test their glucose levels at least five times per day throughout the study. A 12-month follow-up period will take place after the participant's last transplant.

연구 유형

중재적

등록 (실제)

14

단계

  • 2 단계

연락처 및 위치

이 섹션에서는 연구를 수행하는 사람들의 연락처 정보와 이 연구가 수행되는 장소에 대한 정보를 제공합니다.

연구 장소

    • California
      • San Francisco, California, 미국, 94143
        • University of Californinia, San Francisco
    • Illinois
      • Chicago, Illinois, 미국, 60611
        • Northwestern University
    • Minnesota
      • Minneapolis, Minnesota, 미국, 55455
        • University of Minnesota

참여기준

연구원은 적격성 기준이라는 특정 설명에 맞는 사람을 찾습니다. 이러한 기준의 몇 가지 예는 개인의 일반적인 건강 상태 또는 이전 치료입니다.

자격 기준

공부할 수 있는 나이

18년 (성인, 고령자)

건강한 자원 봉사자를 받아들입니다

아니

연구 대상 성별

모두

설명

Inclusion Criteria:

  • Mentally stable and able to comply with study procedures
  • Clinical history compatible with type 1 diabetes, with onset of disease at less than 40 years of age; insulin dependence for at least 5 years at study entry; AND sum of age and insulin-dependent diabetes duration of at least 28
  • Absent stimulated C-peptide (less than 0.3 ng/ml) 60 and 90 minutes post mixed-meal tolerance test
  • Involvement of intensive diabetes management, defined as:

    1. Self monitoring of glucose values no less than a mean of three times each day, averaged over each week
    2. Administration of three or more insulin injections each day or insulin pump therapy
    3. Under the direction of an endocrinologist, diabetologist, or diabetes specialist, with at least three clinical evaluations during the past 12 months prior to study enrollment
  • At least one episode of severe hypoglycemia, defined as an event with one of the following symptoms: memory loss; confusion; uncontrollable behavior; irrational behavior; unusual difficulty in awakening; suspected seizure; seizure; loss of consciousness; or visual symptoms, in which the participant was unable to treat him/herself and which was associated with either a blood glucose level less than 54 mg/dl or prompt recovery after an oral carbohydrate, intravenous glucose, or glucagon administration in the 12 months prior to study enrollment.
  • Reduced awareness of hypoglycemia. More information about this criterion, including the specific definition of hypoglycemia unawareness, is in the protocol.

Exclusion Criteria:

  • Body mass index (BMI) greater than 30 kg/m2 or weight less than or equal to 50 kg
  • Insulin requirement of more than 1.0 IU/kg/day or less than 15 U/day
  • HbA1c greater than 10%
  • Untreated proliferative diabetic retinopathy
  • Systolic blood pressure higher than 160 mmHg or diastolic blood pressure higher than 100 mmHg
  • Measured glomerular filtration rate using iohexol of less than 80 ml/min/1.73m2. More information about this criterion is in the protocol.
  • Presence or history of macroalbuminuria (greater than 300 mg/g creatinine)
  • Presence or history of panel-reactive anti-HLA antibody levels greater than background by flow cytometry. More information about this criterion is in the protocol.
  • Pregnant, breastfeeding, or unwilling to use effective contraception throughout the study and for 4 months after study completion
  • Active infection, including hepatitis B virus, hepatitis C virus, HIV, or tuberculosis. More information about this criterion is in the protocol.
  • Negative for Epstein-Barr virus by IgG determination
  • Invasive aspergillus, histoplasmosis, or coccidioidomycosis infection in the past year
  • History of malignancy except for completely resected squamous or basal cell carcinoma of the skin
  • Known active alcohol or substance abuse
  • Baseline Hgb below the lower limits of normal, lymphopenia, neutropenia, or thrombocytopenia
  • History of Factor V deficiency
  • Any coagulopathy or medical condition requiring long-term anticoagulant therapy after transplantation or individuals with an INR greater than 1.5
  • Severe coexisting cardiac disease, characterized by any one of the following conditions:

    1. Heart attack within the last 6 months
    2. Evidence of ischemia on functional heart exam within the year prior to study entry
    3. Left ventricular ejection fraction less than 30%
  • Persistent elevation of liver function tests at the time of study entry
  • Symptomatic cholecystolithiasis
  • Acute or chronic pancreatitis
  • Symptomatic peptic ulcer disease
  • Severe unremitting diarrhea, vomiting, or other gastrointestinal disorders that could interfere with the ability to absorb oral medications
  • Hyperlipidemia despite medical therapy, defined as fasting LDL cholesterol greater than 130 mg/dl (treated or untreated) and/or fasting triglycerides greater than 200 mg/dl
  • Currently receiving treatment for a medical condition that requires chronic use of systemic steroids except for the use of less than or equal to 5 mg prednisone daily, or an equivalent dose of hydrocortisone, for physiological replacement only
  • Treatment with any anti-diabetic medication other than insulin within 4 weeks prior to study entry
  • Use of any study medications within the past 4 weeks
  • Received a live attenuated vaccine within the past 2 months
  • Any medical condition that, in the opinion of the investigator, might interfere with safe participation in the trial
  • Treatment with any immunosuppressive regimen at the time of enrollment.
  • A previous islet transplant.
  • A previous pancreas transplant, unless the graft failed within the first week due to thrombosis, followed by pancreatectomy and the transplant occurred more than 6 months prior to enrollment

공부 계획

이 섹션에서는 연구 설계 방법과 연구가 측정하는 내용을 포함하여 연구 계획에 대한 세부 정보를 제공합니다.

연구는 어떻게 설계됩니까?

디자인 세부사항

  • 주 목적: 치료
  • 할당: 해당 없음
  • 중재 모델: 단일 그룹 할당
  • 마스킹: 없음(오픈 라벨)

무기와 개입

참가자 그룹 / 팔
개입 / 치료
실험적: Allogeneic Pancreatic Islet Cells
Participants in this study can receive up to three separate islet transplants. They will begin receiving antithymocyte globulin (ATG) and sirolimus 2 days prior to the first islet transplant. ATG will continue to be given until Day 2 post-transplant. Participants will continue taking sirolimus for the duration of the study. On the day of transplant, participants will receive DSG and etanercept, in addition to ATG and sirolimus. The DSG infusion will be administered over 3 hours and will immediately precede the islet transplant. Participants will continue receiving daily 3-hour infusions of DSG through Day 6 post-transplant. Etanercept will also be administered on Days 3, 7, and 10 post-transplant. Tacrolimus will be administered on Day 1 post-transplant and continued throughout the study.
유지 면역 억제 요법
유지 면역 억제 요법
Preparation of allogeneic pancreatic islet cells injected into the portal vein of the liver
An anti-inflammatory agent that blocks proinflammatory cytokine production and inhibits T-cells and B-cells and affects antigen presenting cells.
Immunosuppressive that selectively depletes activated T-cells and depletes resting T-cells in a dose-dependent manner.
Will replace antithymocyte globulin in all islet transplantations after the first one
Blocks TNF-alpha which is toxic to islet cells

연구는 무엇을 측정합니까?

주요 결과 측정

결과 측정
기간
Proportion of Insulin-independent Subjects
기간: 75 days following the first islet transplant
75 days following the first islet transplant

2차 결과 측정

결과 측정
측정값 설명
기간
Percent Reduction in Insulin Requirements
기간: 75 days following the first and subsequent islet transplant
75 days following the first and subsequent islet transplant
Hemoglobin A1c (HbA1c)
기간: 75 days following the first and subsequent islet transplant
75 days following the first and subsequent islet transplant
Mean Amplitude of Glycemic Excursions (MAGE)
기간: 75 days following the first and subsequent islet transplant
75 days following the first and subsequent islet transplant
Glycemic Lability Index (LI)
기간: 75 days following the first and subsequent islet transplant
75 days following the first and subsequent islet transplant
Ryan Hypoglycemia Severity Score (HYPO)
기간: 75 days following the first and subsequent islet transplant
75 days following the first and subsequent islet transplant
Basal (fasting) and 90-minute Glucose and C-peptide Results
기간: 75 days following the first and subsequent islet transplant
Derived from Mixed Meal Tolerance Test (MMTT)
75 days following the first and subsequent islet transplant
Beta-score
기간: 75 days following the first and subsequent islet transplant
Assesses beta-cell function after islet transplantation
75 days following the first and subsequent islet transplant
C-peptide: Glucose Creatinine Ratio
기간: 75 days following the first and subsequent islet transplant
75 days following the first and subsequent islet transplant
Acute Insulin Response to Glucose, Insulin Sensitivity, and Disposition Index
기간: 75 days following the first and subsequent islet transplant
Derived from the insulin-modified frequently sampled intravenous glucose tolerance (FSIGT) test
75 days following the first and subsequent islet transplant
Glucose Variability and Hypoglycemia Duration
기간: 75 days following the first and subsequent islet transplant
Derived from the continuous glucose monitoring system (CGMS)
75 days following the first and subsequent islet transplant
Quality of Life (QOL) Measure
기간: 75 days following the first and subsequent islet transplant
75 days following the first and subsequent islet transplant
Incidence of Worsening Retinopathy
기간: 365 days following the first islet transplant
365 days following the first islet transplant
Proportion of Insulin-independent Subjects
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Percent Reduction in Insulin Requirements
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Hemoglobin A1c (HbA1c)
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Mean Amplitude of Glycemic Excursions (MAGE)
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Glycemic Lability Index (LI)
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Clarke Score
기간: 365 days following the first and final islet transplant
A hypoglycemia score
365 days following the first and final islet transplant
HYPO Score
기간: 365 days following the first and final islet transplant
A hypoglycemia score
365 days following the first and final islet transplant
Basal (fasting) and 90-minute Glucose and C-peptide
기간: 365 days following the first and final islet transplant
Derived from Mixed Meal Tolerance Test (MMTT)
365 days following the first and final islet transplant
Beta-score
기간: 365 days following the first and final islet transplant
Assesses beta-cell function after islet transplantation
365 days following the first and final islet transplant
C-peptide: Glucose Creatinine Ratio
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Quality of life (QOL) Measure
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Proportion of Subjects Receiving a Second Islet Cell Transplant
기간: 365 days following the first islet transplant
365 days following the first islet transplant
Proportion of Subjects Receiving a Third Islet Cell Transplant
기간: 365 days following the first and final islet transplant
365 days following the first and final islet transplant
Incidence and Severity of Adverse Events Related to the Islet Cell Transplant Procedure
기간: 75 days and 365 days following the first and final islet cell infusion
75 days and 365 days following the first and final islet cell infusion
Incidence and Severity of Adverse Events Related to the Immunosuppression Therapy
기간: 75 days and 365 days following the first and final islet transplant
75 days and 365 days following the first and final islet transplant
Incidence of a Change in the Immunosuppression Drug Regimen
기간: 75 days and 365 days following the first and final islet cell transplant
75 days and 365 days following the first and final islet cell transplant
Incidence of Immune Sensitization
기간: 75 days and 365 days following the first and final islet transplant
Defined by detecting anti-HLA antibodies not present prior to transplantation
75 days and 365 days following the first and final islet transplant
Acute Insulin Response to Glucose, Insulin Sensitivity, and Disposition Index (DI)
기간: 365 day following the first and final islet transplant
Derived from the insulin-modified frequently sampled intravenous glucose tolerance (FSIGT) test
365 day following the first and final islet transplant

공동 작업자 및 조사자

여기에서 이 연구와 관련된 사람과 조직을 찾을 수 있습니다.

수사관

  • 수석 연구원: Bernhard Hering, MD, University of Minnesota
  • 수석 연구원: Andrew Posselt, MD, PhD, University of California, San Francisco
  • 수석 연구원: Xunrong Luo, MD, PhD, Northwestern University

간행물 및 유용한 링크

연구에 대한 정보 입력을 담당하는 사람이 자발적으로 이러한 간행물을 제공합니다. 이것은 연구와 관련된 모든 것에 관한 것일 수 있습니다.

연구 기록 날짜

이 날짜는 ClinicalTrials.gov에 대한 연구 기록 및 요약 결과 제출의 진행 상황을 추적합니다. 연구 기록 및 보고된 결과는 공개 웹사이트에 게시되기 전에 특정 품질 관리 기준을 충족하는지 확인하기 위해 국립 의학 도서관(NLM)에서 검토합니다.

연구 주요 날짜

연구 시작

2006년 10월 1일

기본 완료 (실제)

2011년 9월 1일

연구 완료 (실제)

2013년 11월 1일

연구 등록 날짜

최초 제출

2007년 2월 9일

QC 기준을 충족하는 최초 제출

2007년 2월 9일

처음 게시됨 (추정)

2007년 2월 13일

연구 기록 업데이트

마지막 업데이트 게시됨 (추정)

2016년 3월 16일

QC 기준을 충족하는 마지막 업데이트 제출

2016년 2월 17일

마지막으로 확인됨

2016년 2월 1일

추가 정보

이 정보는 변경 없이 clinicaltrials.gov 웹사이트에서 직접 가져온 것입니다. 귀하의 연구 세부 정보를 변경, 제거 또는 업데이트하도록 요청하는 경우 register@clinicaltrials.gov. 문의하십시오. 변경 사항이 clinicaltrials.gov에 구현되는 즉시 저희 웹사이트에도 자동으로 업데이트됩니다. .

구독하다