SMAD4 Tailored Neoadjuvant Therapy for the Treatment of Resectable and Borderline Resectable Pancreatic Ductal Adenocarcinoma, SMART-PANC Trial
SMART-PANC: SMAD4 Tailored Neoadjuvant Therapy for Pancreatic Cancer, A Phase ll Non-Randomized, Single Center Pilot Study
研究概览
地位
详细说明
PRIMARY OBJECTIVE:
I. To determine the R0/R1 surgical resection rate among patients with SMAD4-mutant pancreatic cancer treated with gemcitabine/nab-paclitaxel (Cohort A).
SECONDARY OBJECTIVES:
I. To estimate the trial participation rate among patients approached for enrollment, defined as the proportion of patients who consent and enroll among those approached, with a target participation rate of ≥ 70%, and to monitor this rate continuously during accrual.
II. To estimate the R0/R1 surgical resection rate among SMAD4 wild-type patients treated with physician choice chemotherapy (Cohort B).
III. To determine pathologic response rates, among the subset of patients who reach surgical resection.
IV. To determine the progression free survival (PFS). V. To determine the overall survival (OS).
EXPLORATORY OBJECTIVES:
I. To estimate the proportion of R0 resections among patients with SMAD4-mutant pancreatic cancer treated with gemcitabine/nab-paclitaxel (Cohort A) who undergo surgical resection (R0/R1).
II. To estimate the proportion of R0 resections among patients with SMAD4 wild-type patients treated with physician choice chemotherapy (Cohort B) who undergo surgical resection (R0/R1).
III. To compare R0/R1 resection rates between Cohort A (SMAD4-mutant, gemcitabine/nab-paclitaxel) and Cohort B (SMAD4 wild-type, physician choice) in a descriptive, exploratory manner; the study is not powered for formal non-inferiority or superiority testing of this comparison.
IV. To determine the preoperative/neoadjuvant ca19-9 dynamics in both cohorts. V. To determine the preoperative/neoadjuvant circulating tumor DNA (ctDNA) dynamics in both cohorts.
VI. To assess reason for failure to reach surgical resection, categorized by clinical deterioration, patient withdrawal/refusal of surgery, metastatic progression, or local disease progression precluding surgery.
OUTLINE: Patients with SMAD4 alterations are assigned to Cohort A and patients without SMAD4 mutations are assigned to Cohort B.
COHORT A: Patients receive gemcitabine and nab-paclitaxel with or without radiation therapy per SOC. Treatment continues for 8 weeks in the absence of disease progression or unacceptable toxicity. After 8 week restaging, patients may continue to receive treatment for up to 16 or 24 weeks at the discretion of the multidisciplinary tumor board. Starting 21 days after last dose of chemotherapy, patients undergo surgical resection. Additionally, patients undergo blood sample collection and computed tomography (CT) or magnetic resonance imaging (MRI) as clinically indicated throughout the study.
COHORT B: Patients receive either physicians choice of either fluorouracil, leucovorin, irinotecan, and oxaliplatin or gemcitabine and nab-paclitaxel with or without radiation therapy per SOC. Treatment continues for 8 weeks in the absence of disease progression or unacceptable toxicity. After 8 week restaging, patients may continue to receive treatment for up to 16 or 24 weeks at the discretion of the multidisciplinary tumor board. Starting 21 days after last dose of chemotherapy, patients undergo surgical resection. Additionally, patients undergo blood sample collection and CT or MRI as clinically indicated throughout the study.
After completion of study treatment, patients are followed up at 30 days from surgical resection then every 3 months for up to 2 years from study enrollment.
研究类型
注册 (估计的)
阶段
- 阶段2
联系人和位置
学习联系方式
- 姓名:Study Coordinator
- 电话号码:3126951301
- 邮箱:cancer@northwestern.edu
学习地点
-
-
Illinois
-
Chicago、Illinois、美国、60611
- Northwestern University
-
接触:
- Brett L. Ecker, MD
- 邮箱:Brett.Ecker@northwestern.edu
-
首席研究员:
- Brett L. Ecker, MD
-
-
参与标准
资格标准
适合学习的年龄
- 成人
- 年长者
接受健康志愿者
描述
Inclusion Criteria:
Patients must have histologically confirmed pancreas ductal adenocarcinoma
- Most recent cross-sectional imaging of the chest, abdomen and pelvis will be used to rule out distant metastases (this will have been completed within standard of care timelines which will typically fall within 90 days of registration)
Patients must have undergone next generation sequencing (NGS) testing on the pre-treatment tumor tissue and must have either SMAD4 mutant or SMAD4 wild-type mutation identified before consenting for this study
- Note: Before consenting to this study, standard of care NGS procedure will be performed on pre-treatment tumor biopsies that are routinely collected through endoscopic biopsy specimens (in-house Oncomine Precision NGS). The results will be documented for this study from clinic notes
Patients must have resectable/borderline-resectable disease
- Note: National Comprehensive Cancer Network (NCCN) definitions of resectability will be used
- Patients must be treatment-naïve and clinically fit and eligible for either FOLFIRINOX or gemcitabine/nab-paclitaxel chemotherapy regimens (per treating physician's determination)
- Patients must be ≥ 18 years of age
- Patients must exhibit an Eastern Cooperative Oncology Group (ECOG) performance status of 0-1
- Patients must have adequate organ and bone marrow function as determined by the treating physician to be considered to be clinically fit for the physician-determined chemotherapy regimen
Patients must agree to use adequate contraception: (e.g. hormonal or barrier method of birth control for a patient of child-bearing potential (POCBP), prior to study entry, and for the duration of study participation. Should a female patient, or a female partner of a patient become pregnant or suspect she is pregnant while participating in this study, she should inform her treating physician and study doctor immediately. Male patients with a female partner(s) of childbearing potential must agree to use highly effective contraceptive measures throughout the study starting with the screening visit through the time period indicated for standard of care drugs , after the last dose of study treatment is received. Males with pregnant partners must agree to use a condom; no additional method of contraception is required for the pregnant partner. Note: A POCBP is any patient (regardless of gender, sexual orientation, having undergone a tubal ligation, or remaining celibate by choice) with an egg-producing reproductive tract who meets the following criteria:
- Has not undergone a hysterectomy or bilateral oophorectomy
- Has had menses at any time in the preceding 12 consecutive months (and therefore has not been naturally postmenopausal for > 12 months)
- POCBP must have a negative pregnancy test prior to registration on study
- Patients must have the ability to understand and the willingness to sign a written informed consent document and comply with the study requirements
Exclusion Criteria:
Patients with the presence of any of the following genetic or molecular abnormalities:
- Mismatch repair (MMR)-deficiency/Lynch syndrome
- High-frequency microsatellite instability (MSI-H)
- Homologous recombination deficiency (HRD)
- Patients who are currently participating in another study and receiving a study drug
- Patients who have not recovered from adverse events due to prior anti-cancer therapy (i.e., have residual toxicities > grade 1) with the exception of alopecia, neuropathy and other non-significant adverse events per National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) version (v) 6.0
- Patients with a prior or concurrent malignancy whose natural history or treatment has the potential to interfere with the safety or efficacy assessment of the investigational regimen (per treating physician's determination)
- Patients who are pregnant or nursing
Patients who have an uncontrolled intercurrent illness (as determined by treating physician), including, but not limited to any of the following:
- Hypertension that is not controlled on medication
- Active infection requiring treatment
- Symptomatic congestive heart failure
- Unstable angina pectoris
- Cardiac arrhythmia
- Patient with presence of any concurrent medical or psychiatric condition/social situations which would make them inappropriate candidates for entry into this study or that would limit compliance with study requirements, or would compromise the patient's safety or study endpoints, in the treating investigator's judgment
学习计划
研究是如何设计的?
设计细节
- 主要用途:治疗
- 分配:非随机化
- 介入模型:并行分配
- 屏蔽:无(打开标签)
武器和干预
参与者组/臂 |
干预/治疗 |
|---|---|
|
实验性的:Cohort A (gemcitabine, nab-paclitaxel)
Patients receive gemcitabine and nab-paclitaxel with or without radiation therapy per SOC.
Treatment continues for 8 weeks in the absence of disease progression or unacceptable toxicity.
After 8 week restaging, patients may continue to receive treatment for up to 16 or 24 weeks at the discretion of the multidisciplinary tumor board.
Starting 21 days after last dose of chemotherapy, patients undergo surgical resection.
Additionally, patients undergo blood sample collection and CT or MRI as clinically indicated throughout the study.
|
进行核磁共振
其他名称:
接受CT
其他名称:
进行血液样本采集
其他名称:
接受放射治疗
其他名称:
接受手术切除
其他名称:
辅助研究
给予白蛋白结合型紫杉醇
其他名称:
给定吉西他滨
其他名称:
|
|
实验性的:Cohort B (gemcitabine, nab-paclitaxel or FOLFIRINOX)
Patients receive either physicians choice of either fluorouracil, leucovorin, irinotecan, and oxaliplatin or gemcitabine and nab-paclitaxel with or without radiation therapy per SOC.
Treatment continues for 8 weeks in the absence of disease progression or unacceptable toxicity.
After 8 week restaging, patients may continue to receive treatment for up to 16 or 24 weeks at the discretion of the multidisciplinary tumor board.
Starting 21 days after last dose of chemotherapy, patients undergo surgical resection.
Additionally, patients undergo blood sample collection and CT or MRI as clinically indicated throughout the study.
|
进行核磁共振
其他名称:
接受CT
其他名称:
进行血液样本采集
其他名称:
接受放射治疗
其他名称:
接受手术切除
其他名称:
辅助研究
给予白蛋白结合型紫杉醇
其他名称:
给定吉西他滨
其他名称:
给定奥沙利铂
其他名称:
给定氟尿嘧啶
其他名称:
Given irinotecan
Given leucovorin
其他名称:
|
研究衡量的是什么?
主要结果指标
结果测量 |
措施说明 |
大体时间 |
|---|---|---|
|
Proportion of patients who achieve R0/R1 surgical resection (Cohort A)
大体时间:Up to 30 days from surgical resection
|
Successful surgical resection is defined as macroscopically complete removal of the primary pancreatic tumor, classified as R0 or R1.
Will follow the Simon's minimax two-stage design decision rule.
The observed R0/R1 resection rate will be summarized descriptively and reported with an exact (Clopper-Pearson) binomial confidence interval.
|
Up to 30 days from surgical resection
|
次要结果测量
结果测量 |
措施说明 |
大体时间 |
|---|---|---|
|
Trial participation rate
大体时间:Up to 2 years
|
Will be defined as the proportion of patients who consent and enroll among all patients who are approached and eligible for trial participation.
Will be summarized using proportions with exact confidence intervals.
Feasibility monitoring will occur on an ongoing basis during accrual (e.g.
monthly or after every 20 approached eligible patients, whichever occurs first) using cumulative participation rate.
|
Up to 2 years
|
|
Proportion of patients who achieve R0/R1 surgical resection rate (Cohort B)
大体时间:Up to 30 days after surgical resection
|
Among participants who undergo R0/R1 surgical resection, the proportion achieving R0 resection will be summarized.
|
Up to 30 days after surgical resection
|
|
Proportion of patients who achieve R0/R1 surgical resection rate (Cohort A)
大体时间:Up to 30 days after surgical resection
|
Among participants who undergo R0/R1 surgical resection, the proportion achieving R0 resection will be summarized.
|
Up to 30 days after surgical resection
|
|
Pathologic response rates
大体时间:Up to 30 days after surgical resection
|
Pathology reports will be reviewed to determine the College of American Pathologists (CAP) tumor regression score, categorized from 0 (complete response) to 3 (poor or no response).
CAP tumor regression scores will be summarized descriptively as frequencies and percentages across categories.
The distribution of reasons for failure to reach surgical resection will be summarized descriptively using frequencies and percentages.
These summaries may be further stratified by baseline resectability status and SMAD4 mutation status to provide clinical context and inform future trial design.
|
Up to 30 days after surgical resection
|
|
Progression free survival (PFS)
大体时间:From enrollment to disease progression or clinical deterioration that precludes complete surgical resection, disease recurrence after surgery, or death from any cause, assessed up to 2 years
|
PFS will be analyzed using Kaplan-Meier methods.
The median PFS and corresponding 95% confidence interval will be estimated.
|
From enrollment to disease progression or clinical deterioration that precludes complete surgical resection, disease recurrence after surgery, or death from any cause, assessed up to 2 years
|
|
Overall survival (OS)
大体时间:From enrollment to the date of any cause of death or to the date of last follow-up, assessed up to 2 years
|
OS will be analyzed using Kaplan-Meier methods.
Median OS and corresponding 95% confidence intervals will be reported.
|
From enrollment to the date of any cause of death or to the date of last follow-up, assessed up to 2 years
|
合作者和调查者
调查人员
- 首席研究员:Brett L Ecker, MD、Northwestern University
研究记录日期
研究主要日期
学习开始 (估计的)
初级完成 (估计的)
研究完成 (估计的)
研究注册日期
首次提交
首先提交符合 QC 标准的
首次发布 (实际的)
研究记录更新
最后更新发布 (实际的)
上次提交的符合 QC 标准的更新
最后验证
更多信息
与本研究相关的术语
其他相关的 MeSH 术语
- 氨基酸,肽和蛋白质
- 蛋白质
- 有机化学品
- 杂环化合物,1形
- 杂环化合物
- 杂环化合物,2环
- 杂环化合物,融合环
- 调查技术
- 疗法
- 临床实验室技术
- 诊断技术和程序
- 诊断
- 碳氢化合物
- 环磷脂
- 碳氢化合物,Alicyclic
- 碳氢化合物,循环
- 萜烯
- 身体现象
- Camptothecin
- 生物碱
- 酶和辅酶
- 协调配合物
- 税类
- 环虫
- 二萜
- 脱氧胞苷
- 胞苷
- 嘧啶核苷
- 嘧啶
- 卫生保健经济学和组织
- 化学技术,分析
- 频谱分析
- 甲基四氢胶酸盐
- 四氢胶质
- 叶酸
- 翼
- 翼状
- 乌拉西尔
- 嘧啶酮
- 辅酶
- 白蛋白
- 紫杉醇
- 经济学
- 奥沙利铂
- 伊立替康
- 白蛋白结合型紫杉醇
- 吉西他滨
- 氟尿嘧啶
- 亚叶酸
- 放疗
- 辐射
- 标本处理
- 磁共振光谱
- 手术程序,手术
- 130 nm围绕白蛋白的紫杉醇
- 脱水植物
- 税
其他研究编号
- NU 26I01 (其他标识符:Northwestern University)
- P30CA060553 (美国 NIH 拨款/合同)
- NCI-2026-05293 (注册表标识符:CTRP (Clinical Trial Reporting Program))
- STU00226144
药物和器械信息、研究文件
研究美国 FDA 监管的药品
研究美国 FDA 监管的设备产品
此信息直接从 clinicaltrials.gov 网站检索,没有任何更改。如果您有任何更改、删除或更新研究详细信息的请求,请联系 register@clinicaltrials.gov. clinicaltrials.gov 上实施更改,我们的网站上也会自动更新.