此页面是自动翻译的,不保证翻译的准确性。请参阅 英文版 对于源文本。

BCMA/GPRC5D Dual-Target CAR-T Cell Immunotherapy for Relapsed/Refractory Multiple Myeloma

2026年11月4日 更新者:Liping Dou

A Clinical Study on the Safety of BCMA/GPRC5D Dual-Target Autologous CAR-T Cell Immunotherapy for Relapsed/Refractory Multiple Myeloma

This is a single-center, open-label, single-arm, investigator-initiated clinical study to evaluate the safety, tolerability, and preliminary efficacy of SL4903, a BCMA/GPRC5D dual-target autologous CAR-T cell injection, in patients with relapsed or refractory multiple myeloma (R/R MM) whose clonal plasma cells are positive for BCMA and/or GPRC5D. After leukapheresis, participants receive lymphodepleting conditioning (fludarabine 30 mg/m^2/day plus cyclophosphamide 500 mg/m^2/day on Days -5 to -3), followed by a single intravenous infusion of SL4903 at a dose of 1×10^6 CAR-positive cells/kg; bridging therapy (e.g., immunomodulatory drugs or anti-CD38 monoclonal antibody) is permitted between leukapheresis and conditioning at the investigator's discretion. Treatment-emergent adverse events, including cytokine release syndrome (CRS), neurotoxicity, hematologic toxicity, and organ toxicity, will be assessed within 3 months after infusion. Preliminary antitumor activity will be evaluated according to the 2016 International Myeloma Working Group (IMWG) criteria, including objective response rate (ORR), complete response rate (CRR), time to response (TTR), duration of response (DOR), progression-free survival (PFS), overall survival (OS), and measurable residual disease (MRD) negativity rate. Pharmacokinetics (Cmax, Tmax, persistence, and AUCd0-28 of CAR-T cells in peripheral blood by flow cytometry and qPCR) and pharmacodynamics (peripheral blood plasma cell proportion and cytokine levels) will also be evaluated. Participants will be followed for safety and efficacy for up to 2 years after cell therapy.

研究概览

详细说明

This is a single-center, single-arm, open-label, investigator-initiated clinical study of SL4903 autologous T-cell injection in adults with R/R MM. SL4903 is an autologous CAR-T cell product in which the CAR comprises, in order, a GPRC5D-targeting nanobody (VHH1), a BCMA-targeting nanobody (VHH2), a CD8 hinge region, a CD8 transmembrane domain, a 4-1BB costimulatory domain, and a CD3-zeta signaling domain; autologous peripheral blood mononuclear cells are collected by leukapheresis (approximately 80-120 mL), transduced ex vivo with a lentiviral vector, and expanded over a manufacturing period of approximately 7-8 days. Participants receive lymphodepleting conditioning with fludarabine (30 mg/m^2/day) and cyclophosphamide (500 mg/m^2/day) on Days -5 to -3, which may be adjusted at the investigator's discretion, followed by a single intravenous infusion of SL4903 at 1×10^6 CAR-positive cells/kg on Day 0. Planned enrollment is 20 participants; enrollment accounts for potential CAR-T manufacturing failure or rapid disease progression that may preclude infusion. Safety assessments include adverse events and serious adverse events graded per NCI CTCAE v5.0, with CRS and immune effector cell-associated neurotoxicity syndrome (ICANS) graded per the ASTCT consensus criteria; infection, hematologic toxicity, organ toxicity, hemophagocytic lymphohistiocytosis/macrophage activation syndrome (HLH/MAS), and tumor lysis syndrome (TLS) are also monitored. Disease response is assessed per the 2016 IMWG criteria at baseline, Day 28, and Months 2, 3, 6, 12, 18, and 24, including serum/urine M-protein studies, serum free light chains, bone marrow examination with flow cytometry/MRD, and imaging (preferably PET-CT) for extramedullary disease. Pharmacokinetic assessments include CAR-T cell expansion in peripheral blood by flow cytometry and qPCR (Cmax, Tmax, in vivo persistence, and AUCd0-28); pharmacodynamic assessments include peripheral blood plasma cell proportion/count and cytokine quantification (at least IL-6, IL-2, IL-10, IFN-gamma, and TNF-alpha).

研究类型

介入性

注册 (估计的)

20

阶段

  • 阶段1

联系人和位置

本节提供了进行研究的人员的详细联系信息,以及有关进行该研究的地点的信息。

学习联系方式

学习地点

    • Beijing Municipality
      • Beijing、Beijing Municipality、中国、100853
        • Chinese PLA General Hospital
        • 接触:

参与标准

研究人员寻找符合特定描述的人,称为资格标准。这些标准的一些例子是一个人的一般健康状况或先前的治疗。

资格标准

适合学习的年龄

18年 至 75年 (成人、年长者)

接受健康志愿者

不

有资格学习的性别

全部

描述

Inclusion Criteria:

  • Voluntarily agrees to participate in the study (signed informed consent form by the participant or a legally authorized representative), and is willing and able to comply with scheduled visits, study treatment, laboratory tests, and other study procedures.
  • Clinically diagnosed relapsed/refractory multiple myeloma, meeting both of the following:

Clonal plasma cells positive for BCMA and/or GPRC5D by flow cytometry or immunohistochemistry.

Prior treatment with at least 3 drug classes (proteasome inhibitors [PIs], immunomodulatory drugs [IMiDs], and an anti-CD38 monoclonal antibody), with best response less than partial response (PR) or disease progression after achieving PR or better.

  • Male or female participants aged 18 to 75 years, inclusive.
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0-2.
  • Estimated life expectancy of more than 3 months from the date of signing the informed consent form.
  • Adequate renal, hepatic, cardiac, and pulmonary function, defined as follows:

Creatinine clearance (estimated by the Cockcroft-Gault formula) ≥60 mL/min or serum creatinine ≤1.5 × the upper limit of normal (ULN); Serum alanine aminotransferase (ALT) and aspartate aminotransferase (AST)≤2.5×upper limit of normal (ULN), total bilirubin≤1.5×ULN; Cardiac ejection fraction≥50%, no pericardial effusion on echocardiography, and no significant abnormalities on electrocardiogram (ECG); No clinically significant pleural effusion, and oxygen saturation >92% on room air at baseline.

  • Participants of reproductive potential must agree to use highly effective contraception before enrollment and for at least 12 months after CAR-T cell infusion. A negative serum pregnancy test is required for women of childbearing potential at screening. Participants must immediately notify the investigator if pregnancy occurs or is suspected.

Exclusion Criteria:

  • The patient has severe cardiac dysfunction, or left ventricular ejection fraction (LVEF) <50%, or a history within the 12 months prior to enrollment of myocardial infarction, coronary angioplasty or coronary stent implantation, unstable angina, clinically significant arrhythmia, or other severe cardiovascular diseases.
  • A history of severe pulmonary disease with impaired lung function.
  • Concurrent progressive malignancy other than multiple myeloma.
  • Severe active infection that cannot be effectively controlled.
  • Severe autoimmune disease or congenital immunodeficiency.
  • Active hepatitis, defined as hepatitis B virus DNA (HBV-DNA) or hepatitis C virus RNA (HCV-RNA) levels above the lower limit of detection, or human immunodeficiency virus (HIV) infection, known acquired immunodeficiency syndrome (AIDS), or syphilis infection.
  • A history of severe allergic reactions to biological products, including antibiotics.
  • The patient has severe autoimmune disease, congenital immunodeficiency or active autoimmune disease requiring ongoing systemic immunosuppressive treatment, or is currently within the washout period after having received medications that may affect CAR-T cell immunotherapy, or is anticipated to require medications during the study period that may affect CAR-T cell immunotherapy treatment.
  • The investigator judges that the patient is unlikely to complete all visits and procedures required by the study protocol (including medium- and long-term follow-up visits), such as insufficient willingness of the patient and their family members to participate in the study, refusal to participate, inability of the patient to fully cooperate with the study arrangements, or inadequate compliance on the part of the patient and their family members.
  • Any other severe physical or psychiatric disorder or clinically significant laboratory abnormality that may increase the risk associated with study participation, interfere with the interpretation of study results, or, in the investigator's judgment, make the participant unsuitable for participation in the study.
  • Female participants of childbearing potential who are pregnant or breastfeeding.

学习计划

本节提供研究计划的详细信息,包括研究的设计方式和研究的衡量标准。

研究是如何设计的?

设计细节

  • 主要用途:治疗
  • 分配:不适用
  • 介入模型:单组作业
  • 屏蔽:无(打开标签)

武器和干预

参与者组/臂
干预/治疗
实验性的:The experimental group

SL4903 Treatment Group - after leukapheresis and lymphodepleting conditioning (fludarabine 30 mg/m^2/day plus cyclophosphamide 500 mg/m^2/day on Days -5 to -3), participants receive a single intravenous infusion of SL4903 autologous T-cell injection at a dose of 1 x 10^6 CAR-positive cells/kg. Bridging therapy (e.g., immunomodulatory drugs or anti-CD38 monoclonal antibody) may be given between leukapheresis and conditioning at the investigator's discretion.

SL4903 is an investigational autologous dual-target CAR T-cell therapy (lentiviral vector-based) directed against BCMA and GPRC5D, for patients with relapsed or refractory multiple myeloma whose clonal plasma cells are positive for BCMA and/or GPRC5D. The CAR comprises a GPRC5D-targeting nanobody (VHH1), a BCMA-targeting nanobody (VHH2), a CD8 hinge region, a CD8 transmembrane domain, a 4-1BB costimulatory domain, and a CD3-zeta signaling domain. After leukapheresis and lymphodepleting conditioning (fludarabine plus cyclophosphamide), participants receive a single intravenous infusion of SL4903 at 1×10^6 CAR-positive cells/kg.

其他名称:
  • SL4903; BCMA-GPRC5D CAR-T injection

研究衡量的是什么?

主要结果指标

结果测量
措施说明
大体时间
Adverse Events
大体时间:From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

AEs are graded per NCI CTCAE v5.0

From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months
Cytokine Release Syndrome
大体时间:From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

Cytokine release syndrome (CRS) is graded according to the ASTCT consensus criteria.

From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months
Immune Effector Cell-associated Neurotoxicity Syndrome
大体时间:From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

Immune effector cell-associated neurotoxicity syndrome (ICANS) is graded according to the ASTCT consensus criteria.

From SL4903 infusion through 3 months after infusion; long-term safety follow-up continues through 12 months

次要结果测量

结果测量
措施说明
大体时间
Objective Response Rate
大体时间:At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion

The proportion of participants achieving a partial response or better (ORR), assessed by the investigator according to the 2016 International Myeloma Working Group (IMWG) criteria.

At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion
Complete Response Rate
大体时间:At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion

The proportion of participants achieving a complete response (CR) or stringent complete response (sCR), per the 2016 IMWG criteria.

At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion
Time to Response and Duration of Response
大体时间:From SL4903 infusion through 24 months after treatment

Time to response (TTR), defined as the time from SL4903 infusion to first documented response, and duration of response (DOR), defined as the time from first documented response to disease progression or death, per the 2016 IMWG criteria.

From SL4903 infusion through 24 months after treatment
Progression-Free Survival
大体时间:From SL4903 infusion through 24 months after treatment

Progression-free survival (PFS), defined as the time from SL4903 infusion to disease progression or death from any cause, whichever occurs first, per the 2016 IMWG criteria; PFS rates at 6, 9, 12, 18, and 24 months will also be estimated.

From SL4903 infusion through 24 months after treatment
Overall Survival
大体时间:From SL4903 infusion through 24 months after treatment

Overall survival (OS), defined as the time from SL4903 infusion to death from any cause; OS rates at 6, 9, 12, 18, and 24 months will also be estimated. Participants who are alive at the last follow-up will be censored on the date of their last known survival status.

From SL4903 infusion through 24 months after treatment
Measurable Residual Disease (MRD) Negativity Rate
大体时间:At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion

The proportion of participants achieving MRD negativity in bone marrow, assessed by flow cytometry, among responding participants.

At Day 28 and Months 2, 3, 6, 12, 18, and 24 after SL4903 infusion
Peak Expansion of SL4903 CAR-T Cells in Peripheral Blood
大体时间:Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion

Peak expansion of SL4903 CAR-T cells in peripheral blood (Cmax, measured by both flow cytometry and qPCR),

Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion
Time to Peak Expansion
大体时间:Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion

Time to Peak Expansion

Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion
Area Under The Gene-copy Expansion Curve from Day 0 to Day 28
大体时间:Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion

in vivo persistence of CAR-T cells, and the area under the gene-copy expansion curve from Day 0 to Day 28 (AUCd0-28).

Through Day 28 for AUCd0-28, Cmax, and Tmax; CAR-T persistence through 24 months after infusion
Pharmacodynamic Markers (Exploratory)
大体时间:Through 24 months after SL4903 infusion

Proportion and absolute count of plasma cells in peripheral blood by flow cytometry, and peripheral blood cytokine levels (at least IL-6, IL-2, IL-10, IFN-gamma, and TNF-alpha) at prespecified time points.

Through 24 months after SL4903 infusion

合作者和调查者

在这里您可以找到参与这项研究的人员和组织。

赞助

研究记录日期

这些日期跟踪向 ClinicalTrials.gov 提交研究记录和摘要结果的进度。研究记录和报告的结果由国家医学图书馆 (NLM) 审查,以确保它们在发布到公共网站之前符合特定的质量控制标准。

研究主要日期

学习开始 (估计的)

2026年11月30日

初级完成 (估计的)

2028年11月30日

研究完成 (估计的)

2029年11月30日

研究注册日期

首次提交

2026年10月28日

首先提交符合 QC 标准的

2026年11月4日

首次发布 (实际的)

2026年11月10日

研究记录更新

最后更新发布 (实际的)

2026年11月10日

上次提交的符合 QC 标准的更新

2026年11月4日

最后验证

2026年11月1日

更多信息

与本研究相关的术语

计划个人参与者数据 (IPD)

计划共享个人参与者数据 (IPD)?

不

药物和器械信息、研究文件

研究美国 FDA 监管的药品

不

研究美国 FDA 监管的设备产品

不

此信息直接从 clinicaltrials.gov 网站检索,没有任何更改。如果您有任何更改、删除或更新研究详细信息的请求,请联系 register@clinicaltrials.gov. clinicaltrials.gov 上实施更改,我们的网站上也会自动更新.

订阅