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Clinical Trials on ADA Deficient SCID
Total 11639 results
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National Human Genome Research Institute (NHGRI)National Institutes of Health Clinical Center (CC); National Cancer Institute... and other collaboratorsCompletedADA-SCID | Adenosine Deaminase DeficiencyUnited States
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Primary Immune...Enrolling by invitationADA-SCID | Omenn Syndrome | SCID | Reticular Dysgenesis | XSCID | Leaky SCIDUnited States, Canada
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National Institute of Allergy and Infectious Diseases...National Center for Advancing Translational Sciences (NCATS); Office of Rare... and other collaboratorsEnrolling by invitationOmenn Syndrome | Reticular Dysgenesis | Severe Combined Immunodeficiency (SCID) | XSCID | Leaky SCID | ADA SCIDUnited States, Canada
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University of California, Los AngelesNational Institute of Allergy and Infectious Diseases (NIAID); National Heart... and other collaboratorsCompleted
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Leadiant Biosciences, Inc.CompletedSevere Combined Immunodeficiency | ADA-SCID | Adenosine Deaminase DeficiencyUnited States
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Shenzhen Geno-Immune Medical InstituteUnknownAdenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID)China
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National Human Genome Research Institute (NHGRI)Active, not recruitingWiskott- Aldrich Syndrome | ADA Deficient SCIDUnited States
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National Human Genome Research Institute (NHGRI)Withdrawn
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University Hospital, MontpellierRecruitingAromatic L-Amino Acid Decarboxylase DeficiencyFrance
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Maria Luz Couce PicoFundación Ramón DomínguezWithdrawnLong-chain Fatty Acid Transport DeficiencySpain
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Fondazione Policlinico Universitario Agostino Gemelli...Massimo Antonelli; Cristina Dominedò; Marco Rossi; Rossano Festa; Nicoletta Filetici and other collaboratorsCompletedAcid-Base Imbalance | SIDItaly
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Shanghai Jiao Tong University School of MedicineShanghai Vitalgen BioPharma Co., Ltd.RecruitingAromatic L-amino Acid Decarboxylase (AADC) DeficiencyChina
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University of California, Los AngelesOrchard Therapeutics; California Institute for Regenerative Medicine (CIRM)CompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
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Oklahoma State University Center for Health SciencesActive, not recruiting
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Fondazione TelethonActive, not recruitingSevere Combined Immunodeficiency Due to ADA DeficiencyItaly
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited Kingdom
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University of California, Los AngelesWithdrawnSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
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Fondazione TelethonCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyItaly
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Hadassah Medical OrganizationUnknown
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National Institute of Health and NutritionCompletedFolate Deficiency
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Indonesia UniversityUnited States Agency for International Development (USAID); Ministry of Research...Completed
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Harvard UniversityCompleted
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
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Mansoura UniversitySwedish University of Agricultural Sciences; The Swedish Research Council for...Completed
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingAromatic L-amino Acid Decarboxylase Deficiency
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Meir Medical CenterCompletedFolic Acid Deficiency | Vitamin B12 DeficiencyIsrael
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American Regent, Inc.CompletedIron Deficiency Anemia (IDA)Poland, Russian Federation
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Build Healthy India MovementMinistry of Science and Technology, IndiaCompleted
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American Regent, Inc.CompletedIron Deficiency Anemia (IDA)United States
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Michigan State UniversityCompletedIron Deficiency Anemia (IDA) | Iron Deficiency (ID) | General AnemiaGhana
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Medical University of GrazCompletedHealthy | Oxidative Stress | Vitamin B 12 Deficiency | Polyphenols | Thiamine and Niacin Deficiency States | Pyridoxine Deficiency | Folic Acid Deficiency Anemia, Dietary | Peroxidase; Defect | Homocystine; Metabolic DisorderAustria
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University of TorontoThe Hospital for Sick Children; Heinz EndowmentsCompletedIron Deficiency | Folic Acid DeficiencyCanada
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Boston Children's HospitalUNICEF; Ministry of Health, Liberia; Liberia Institute of Statistics and Geo-Information...WithdrawnNutritional Anemia | Knowledge, Attitudes, Practice | Food Habits | Iron Deficiency Anemia Treatment | Nutritional Deficiency | Adolescent Development | Folic Acid Deficiency Anemia, Dietary
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King's College Hospital NHS TrustCompletedAcidosis | Acid Base Disorder | Cardiac; DeficiencyUnited Kingdom
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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University Hospital, Strasbourg, FranceCompletedFolic Acid Deficiency | Elderly Patients | Social IsolationFrance
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Children's Hospital Los AngelesNot yet recruitingAnemia | Iron Deficiency Anemia | Anemia, Iron Deficiency | IDA - Iron Deficiency AnemiaUnited States
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University of Massachusetts, WorcesterCompletedLow-GI Dietary Education | ADA Dietary EducationUnited States
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Oslo University HospitalUniversity of Oslo; Umeå University; University of Geneva, SwitzerlandActive, not recruitingImmature Infant | Essential Fatty Acid DeficiencyNorway
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Walden UniversityCompletedPregnancy Related | Autism Spectrum Disorder | Autistic Disorder | Folate Deficiency | Folic Acid Deficiency | Diet, Healthy | Autism | Diet; Deficiency | Folic Acid OverdoseUnited States
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Eduardo FerriolliCompletedFatty Acid Deficiency | Nutrient Deficiency | Vitamin E Deficiency | Selenium Deficiency | Age-Related Immunodeficiency | Institutionalization; Disinhibited AttachmentBrazil
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NovartisCompleted
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Bina Nusantara UniversityMaastricht University; Yayasan Rumah Sakit Islam (YARSI) University; Universitas...Completed
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Barcelona Institute for Global HealthCompletedAttention Deficit Hyperactivity Disorder | Child Behavior Problem | Fatty Acid Deficiency
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University of LeicesterUnknown
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Hospices Civils de LyonRecruitingDeficiency, Vitamin CFrance
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University of California, DavisUniversity of California, San Francisco; Ethiopian Public Health Institute; Nutrition...CompletedFolate Deficiency | Iodine Deficiency | Anemia, Macrocytic | Anemia Deficiency | Salt IntakeEthiopia
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The University of Hong KongQueen Mary Hospital, Hong KongNot yet recruitingThalassemia | Folic Acid Deficiency Anemia
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American Regent, Inc.Unknown