Search clinical trials for: Expanded Access Protocol
Total 10325 results
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Children's Hospital of PhiladelphiaRecruitingLeukemia | Bone Marrow Failure Syndromes | Immunodeficiencies | Inborn Errors of Metabolism | Immunodysregulation Polyendocrinopathy Enteropathy X-linked SyndromeUnited States
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Children's Hospital of PhiladelphiaAvailableLeukemia | Immunodeficiencies | Bone Marrow Failure SyndromeUnited States
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Juno Therapeutics, a Subsidiary of CelgeneAvailableLymphoma, Large B-Cell, Diffuse
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Joanne Kurtzberg, MDAvailableCerebral Palsy | Apraxia of Speech | Hydrocephalus | Hypoxia Ischemia, Cerebral | Drowning; AnoxiaUnited States
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AmgenAvailableSmall Cell Lung CancerUnited States, Brazil, Japan
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Memorial Sloan Kettering Cancer CenterAvailable
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Clene NanomedicineAvailableAmyotrophic Lateral SclerosisUnited States
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Clene NanomedicineNational Institute of Neurological Disorders and Stroke (NINDS)AvailableAmyotrophic Lateral Sclerosis | ALS | PALS
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Clene NanomedicineMassachusetts General HospitalAvailable
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Alnylam PharmaceuticalsApproved for marketingAcute Hepatic Porphyria
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Alnylam PharmaceuticalsApproved for marketingAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
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AmgenNo longer availableRelapsed/Refractory B-Precursor Acute Lymphoblastic LeukemiaUnited States, Italy, Germany, Austria, France, Switzerland, United Kingdom
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PfizerAvailableAtopic DermatitisTaiwan, United States, Australia, Austria, Belgium, Canada, Greece, Mexico, Netherlands, Russian Federation, Spain, Switzerland
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availablePost COVID-19 SyndromeUnited States
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Brainstorm-Cell TherapeuticsNo longer availableAmyotrophic Lateral SclerosisUnited States
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Jazz PharmaceuticalsAvailableHER2-Positive Advanced Biliary Tract CancerSpain, United States, France, Italy, United Kingdom
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PfizerPfizerAvailableSickle Cell DiseaseUnited States, Brazil
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PfizerAvailableMultiple MyelomaUnited States, Canada
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PfizerNo longer available
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Biohaven Pharmaceuticals, Inc.AvailableSpinocerebellar Ataxias | SCA
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Longboard PharmaceuticalsAvailableDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathiesUnited States
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Alnylam PharmaceuticalsNo longer availableTransthyretin-mediated Amyloidosis With Cardiomyopathy | ATTR Amyloidosis With CardiomyopathyUnited States
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Alnylam PharmaceuticalsApproved for marketingPrimary HyperoxaluriaBelgium
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Prasanna K KapavarapuAvailableGastroesophageal Reflux | Gastroparesis | Chronic Constipation With Overflow | Pseudo ObstructionUnited States
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Ellodi Pharmaceuticals, LPAvailableEosinophilic EsophagitisUnited States
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Aragon Pharmaceuticals, Inc.No longer availableProstatic NeoplasmsColombia, Brazil, Mexico
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AiCuris Anti-infective Cures AGImpatients N.V. trading as myTomorrowsAvailable
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Bristol-Myers SquibbNo longer available
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Mauricio LynnAvailable
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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Kedrion S.p.A.AvailableLigneous Conjunctivitis
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Vanda PharmaceuticalsAvailableGastroparesis | Diabetic GastroparesisUnited States
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Hope Biosciences Stem Cell Research FoundationAvailable
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Janssen-Cilag, S.A.Completed
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Celcuity, Inc.AvailableBreast Neoplasm Malignant FemaleUnited States
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Children's Hospital Medical Center, CincinnatiNo longer availableNeuroblastoma | Pheochromocytoma | ParagangliomaUnited States
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John MarisAvailableNeuroblastoma | Childhood Metastatic PheochromocytomaUnited States
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Regeneron PharmaceuticalsAvailable
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Atara BiotherapeuticsNo longer availableLymphoproliferative Disorders | Stem Cell Transplant Complications | Epstein-Barr Virus (EBV) Infections | EBV+ Associated Lymphoma | EBV+ Associated Post-transplant Lymphoproliferative Disease (EBV+ PTLD) | Epstein-Barr Viremia | Lymphoma, AIDS-related | Epstein-Barr Virus-associated Lymphoproliferative... and other conditions
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Northwell HealthCohen Children's Medical CenterAvailableNeuroblastoma | PheochromocytomaUnited States
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Stealth BioTherapeutics Inc.AvailableMitochondrial Diseases | Barth Syndrome
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DBV TechnologiesTodd D. Green MD, DBV TechnologiesAvailablePeanut AllergyUnited States
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Jubilant DraxImage Inc.AvailableNeuroblastoma | Pheochromocytoma | ParagangliomaUnited States
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APR Applied Pharma Research s.a.Cavendish Impact Foundation; Clinigen, Inc.; Nephron Pharmaceuticals, Inc.No longer availableCritical COVID-19 With Respiratory FailureUnited States
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CelgeneAvailable
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Prometic Biotherapeutics, Inc.No longer availableHypoplasminogenemiaUnited States
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Janssen Research & Development, LLCApproved for marketingRelapsed or Refractory Multiple Myeloma