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Search clinical trials for: MECP2 mutation
Total 3263 results
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University Hospital, BrestUnknownDysautonomia | Masculinity | MECP2-Related Severe Neonatal EncephalopathyFrance
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Psoriasis Treatment Center of Central New JerseyLEO PharmaUnknown
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RecruitingRett Syndrome | Rett Syndrome, Atypical | RTTUnited States
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Rett Syndrome Research TrustDuke UniversityCompletedRett SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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Neurogene Inc.RecruitingRett SyndromeUnited States
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Rett Syndrome Research TrustVanderbilt University Medical CenterCompleted
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)CompletedRett SyndromeUnited States
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationCompleted
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Edison Pharmaceuticals IncWithdrawn
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome | MECP2 Duplication Disorder | Rett-related DisorderUnited States
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University Hospital, Basel, SwitzerlandNovartisCompletedRett's SyndromeSwitzerland
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCDKL5 | Rett Syndrome | MECP2 Duplication | FOXG1 DisordersUnited States
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedRett Syndrome | CDKL5 Disorder | MECP2 Duplication dIsorder | FOXG1 SyndromeUnited States
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
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Quanta TherapeuticsNot yet recruitingAdvanced Solid Tumor
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Novartis PharmaceuticalsNot yet recruitingLeukemia, Myelogenous, Chronic, BCR-ABL Positive
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Centre Leon BerardNot yet recruitingOral Squamous Cell CarcinomasFrance
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Jacobio Pharmaceuticals Co., Ltd.Not yet recruitingAdvanced Non-squamous Non-small-cell Lung Cancer | Metastatic Non-squamous Non Small Cell Lung Cancer
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AstraZenecaNot yet recruitingMetastatic Breast CancerBrazil
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AstraZenecaDaiichi SankyoNot yet recruiting
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M.D. Anderson Cancer CenterNot yet recruitingMetastatic Colorectal Cancer | KRAS G12C MutationsUnited States
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Cancer Institute and Hospital, Chinese Academy...RecruitingEndometrial Carcinoma | Recurrent or Metastatic | TP53 MutationChina
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Assistance Publique - Hôpitaux de ParisCentre Leon Berard; Institut National de la Santé Et de la Recherche Médicale... and other collaboratorsNot yet recruitingEnvironmental Exposure | SDH Gene Mutation | SDH-Related Familial Paraganglioma | SDHx-Related SyndromesFrance
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Azienda Ospedaliero-Universitaria di ModenaRecruiting
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Cancer Institute and Hospital, Chinese Academy...Not yet recruitingEarly-stage Triple-negative Breast Cancer With BRCA1/2 MutationsChina
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858 Therapeutics, Inc.RecruitingBreast Cancer | Gastric Cancer | Colorectal Cancer | Ovarian Cancer | Prostate Cancer | Endometrial Cancer | Epithelial Ovarian Cancer | BRCA1 Mutation | BRCA2 Mutation | Advanced or Metastatic Solid Tumors | ER+ Breast Cancer | Castrate Resistant Prostate Cancer | BRCA MutationUnited States
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Radboud University Medical CenterNot yet recruitingPeritoneal Carcinoma | Ovarian Carcinoma | Serous Tubal Intraepithelial Carcinoma | BRCA Mutation
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Pauls Stradins Clinical University HospitalRecruiting
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Qian QinJanssen, LP; UT Southwestern Comprehensive Cancer CenterNot yet recruitingBRCA1 Gene Mutation | BRCA2 Gene Mutation | BRIP1 Gene Mutation | PALB2 Gene Mutation | CHEK2 Gene Mutation | FANCA Gene Mutation | RAD51B Gene Mutation | RAD54L Gene Mutation | Metastatic Hormone-sensitive Prostate Cancer (mHSPC) | Deleterious HRR Gene Mutation
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Tyligand Bioscience (Shanghai) LimitedRecruitingMalignant NeoplasmUnited States
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Jacobio Pharmaceuticals Co., Ltd.Not yet recruiting
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Jiangsu HengRui Medicine Co., Ltd.Not yet recruitingAdvanced KRAS G12D Mutant Solid TumorsChina
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Washington University School of MedicineAlzheimer's Association; Eisai Inc.Not yet recruitingDementia | Alzheimer's Disease | Alzheimer's Disease, FamilialUnited States, Australia, United Kingdom
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Zhejiang Cancer HospitalRecruitingHER2 Gene Mutation | Bile Duct Adenocarcinoma Non-ResectableChina
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MedSIRStemline Therapeutics, Inc.Not yet recruitingAdvanced Breast Cancer | ER-positive Breast Cancer | HER2-negative Breast Cancer | ESR1 Gene Mutation
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Acerand Therapeutics (Shanghai) LimitedRecruitingBreast Cancer | Ovarian Cancer | Prostate Cancer | BRCA1 Mutation | BRCA2 Mutation | Solid Tumor, AdultChina
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Centro di Riferimento Oncologico - AvianoRecruitingNon Small Cell Lung Cancer Metastatic | ALK Gene MutationItaly
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Shanghai JMT-Bio Inc.Not yet recruiting
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BayerRecruitingHealthy Volunteers | Advanced Non-small Cell Lung Cancer | EGFR Mutation | HER2 MutationUnited States
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AstraZenecaNot yet recruitingNeoplasms | Respiratory Tract Diseases | Lung Diseases | Neoplasms by Site | Carcinoma, Non-Small-Cell Lung | Lung Neoplasms | Respiratory Tract Neoplasms | Thoracic Neoplasms | Carcinoma, Bronchogenic | Bronchial NeoplasmsChina
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University College, LondonWashington University School of Medicine; University of Washington; Alzheimer... and other collaboratorsNot yet recruitingAlzheimer Disease | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 1 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 2 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Amyloid Precursor Protein (Disorder)
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SensorionNot yet recruitingOtorhinolaryngologic Diseases | Ear Diseases | Hearing Disorders | Deafness | Hearing Loss, Sensorineural | Congenital Deafness | DFNB9 | OTOF Gene MutationFrance
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Eilean TherapeuticsNot yet recruiting