- ICH GCP
- US Clinical Trials Registry
- Klinisk forsøg NCT07702981
Immunophenotyping Profiling in Patients With Primary Nephrotic Syndrome
Immunophenotyping Profiling in Patients With Nephrotic Syndrome: Emphasis on the Diagnostic and Prognostic Value of Immune Cells in the Different Phenotypes of Nephrotic Syndrome.
Studieoversigt
Status
Betingelser
Intervention / Behandling
Detaljeret beskrivelse
Primary nephrotic syndrome caused by membranous nephropathy (MN), focal segmental glomerulosclerosis (FSGS), or minimal change disease (MCD) is, in each case, associated with dysregulation of specific innate and adaptive immune cell populations. However, the relationship between circulating immune cell subsets and key clinical outcomes, specifically treatment response and disease relapse, remains incompletely defined, and the classical clinical and laboratory markers currently used to monitor these diseases are non-specific and have limited predictive value.
The principal parameter used clinically to monitor treatment response remains 24-hour urinary protein excretion. Complete remission is defined as a reduction in proteinuria to below 0.3 g/24h, and partial remission as a reduction of ≥50% from baseline together with total proteinuria below 3.5 g/24h. Non-response is defined as persistent proteinuria above 3.5 g/24h despite guideline-directed therapy, and relapse as recurrence of proteinuria above 3.5 g/24h in a patient who had previously achieved complete remission.
In MN specifically, serum anti-PLA2R antibody titers provide an additional marker of immunological disease activity: a decline in antibody levels can precede and predict clinical response, while re-emergence or a rise in titer in a patient previously in remission can predict relapse.
Despite the established contribution of specific immune cell populations to primary nephrotic syndrome, the literature remains comparatively sparse regarding abnormalities in regulatory T-cell subsets, monocyte subsets, B-cell subsets (including CD5+ B cells), T-helper subsets, and NK cells, and their potential role in disease pathogenesis across MN, MCD, and FSGS. Furthermore, classical clinical and immunological biomarkers of disease activity and treatment response are non-specific, correlate poorly with the degree of underlying renal injury, and in most cases cannot predict renal outcome. Anti-PLA2R1 antibody titers capture humoral activity and glomerular injury, but only partially explain this heterogeneity, are informative in only 70-80% of patients and frequently lag behind cellular events.
Whether changes in specific circulating immune cell subsets are associated with clinical outcomes in primary nephrotic syndrome, and whether they add predictive value beyond classical markers, remains an open question that this study is designed to address.
This prospective, single-center cohort study will enroll adult patients with either de novo or relapsing primary MN, primary FSGS and MCD, diagnosed by renal biopsy , who underwent rituximab (RTX) or corticosteroids treatment at the University Hospital of Ioannina between JUN 2023 and NOV 2025. Baseline was defined as the time of treatment initiation.
Baseline Assessment - Month 0
- Demographic and clinical data: sex, age, smoking status, alcohol use, obesity, family history, and comorbidities, with particular attention to hypertension, diabetes mellitus, dyslipidemia, coronary artery disease, and coexisting autoimmune disease. A full clinical examination will be performed (systems review, blood pressure, pulse, weight, height, body mass index), and current medications will be recorded.
- Routine laboratory assessment (at baseline and at regular intervals thereafter, per current standards of care for primary nephrotic syndrome): complete blood count, INR, comprehensive metabolic panel (glucose, urea, creatinine, potassium, sodium, calcium, phosphate, AST, ALT, CPK, GGT, alkaline phosphatase, total serum protein, HDL and LDL cholesterol, triglycerides, HbA1c, iron, TIBC, ferritin), inflammatory markers (CRP, ESR), urinalysis, and UPCR/UACR (creatinine, urea, protein, albumin, sodium). Estimated glomerular filtration rate will be calculated using the CKD-EPI creatinine equation.
- Disease-specific serology: in patients with confirmed membranous nephropathy, serum anti-PLA2R antibody titers will be measured per the KDIGO 2021 Clinical Practice Guideline for Glomerular Diseases.
- Annual assessments: viral serology and tumor markers (HBsAg, HBsAb, HBcAb, anti-HCV, AFP, CA 19-9, CA 15-3, CEA, CA-125, PSA); lipid panel (apo-A, apo-B, Lp(a)) and fasting insulin.
After baseline serum creatinine, eGFR (CKD-EPI), albumin, urine protein-to-creatinine ratio (UPCR), urine albumin-to-creatinine ratio (UACR), lipid parameters and inflammatory markers (ESR, CRP) were measured every month after treatment.
Anti-PLA2R antibody levels were measured at baseline and months 3,6 and 12 respectively.
Peripheral-blood immune-cell subsets were analysed by flow cytometry at baseline and at months 3, 6 and 12.
The following immune cell subsets were measured through flow cytometry:
- B-cell compartment: total CD3-CD19+; CD19+CD27+IgD+ (non-switched memory); CD19+CD27+IgD- (class-switched memory); CD19+CD27-IgD+ (naïve mature); CD19+CD5+ (regulatory B cells, Bregs).
- T-cell compartment: CD3+; CD3+CD4+; CD3+CD8+; CD4/CD8 ratio; CD4+CD25+FoxP3+ (regulatory T cells, Tregs); CD4+CD45RA+ (naïve); CD4+CD45RO+ (memory); CD45RA+RO+ (transitional).
- Monocyte compartment: total monocytes; CD14++CD16- (classical); CD14++CD16+ (intermediate); CD14+CD16++ (non-classical); CD14+HLA-DR+ (activated).
- CD16+CD56+ (NK cells).
The study aims to determine whether baseline levels and treatment-related changes in these immune cell subsets are associated with treatment response and disease relapse, and to correlate them with standard clinical and laboratory markers of renal function and disease activity.
Undersøgelsestype
Tilmelding (Faktiske)
Kontakter og lokationer
Studiesteder
-
-
Epirus
-
Ioannina, Epirus, Grækenland, 45500
- University Hospital of Ioannina
-
-
Deltagelseskriterier
Berettigelseskriterier
Aldre berettiget til at studere
- Voksen
- Ældre voksen
Tager imod sunde frivillige
Prøveudtagningsmetode
Studiebefolkning
Beskrivelse
Inclusion Criteria:
- Patients with nephrotic syndrome and a biopsy-confirmed diagnosis of membranous nephropathy, primary focal segmental glomerulosclerosis, or minimal change disease.
- Patients with membranous nephropathy and positive serum anti-PLA2R antibodies, in the absence of histological confirmation by renal biopsy.
- Patients with a previously confirmed diagnosis of primary nephrotic syndrome who present with disease relapse requiring re-induction therapy.
Exclusion Criteria:
- Patients with nephrotic syndrome in whom membranous nephropathy, primary FSGS, or MCD has not been confirmed by renal biopsy (and who do not meet Inclusion Criterion 2).
- Patients with secondary causes of nephrotic syndrome (malignancy, autoimmune disease, drug-induced, etc.).
- Patients with active malignancy.
- Patients with severe heart failure (NYHA class IV) or hepatic failure.
- Patients with active infection or inflammation.
- Patients receiving, or who received within the preceding 6 months, immunomodulatory agents for an unrelated condition.
Studieplan
Hvordan er undersøgelsen tilrettelagt?
Design detaljer
Kohorter og interventioner
Gruppe / kohorte |
Intervention / Behandling |
|---|---|
|
Primary Membranous Nephropathy
Patients with primary MN
|
Patients with primary MN treated with Rituximab
|
|
FSGS
Patients with primary focal segmental glomerulosclerosis
|
Patients with MCD treated with Corticosteroids
Patients with primary FSGS treated with Corticosteroids
|
|
MCD
Patients with minimal change disease
|
Patients with MCD treated with Corticosteroids
Patients with primary FSGS treated with Corticosteroids
|
Hvad måler undersøgelsen?
Primære resultatmål
Resultatmål |
Foranstaltningsbeskrivelse |
Tidsramme |
|---|---|---|
|
Partial Remission
Tidsramme: 12 months
|
Urine protein to creatinine ratio< 3.5 g/g and >50 % reduction from baseline
|
12 months
|
|
Complete Remission
Tidsramme: 12 months
|
Urine protein to creatinine ratio <0.3 g/g
|
12 months
|
|
Relapse
Tidsramme: 24 months
|
Urine protein to creatinine ratio>3.5 g/g
|
24 months
|
Sekundære resultatmål
Resultatmål |
Foranstaltningsbeskrivelse |
Tidsramme |
|---|---|---|
|
Composite renal outcome
Tidsramme: 24 months
|
>50% decline in eGFR (CKD-EPI) from baseline, and/or initiation of kidney replacement therapy
|
24 months
|
|
Cardiovascular events
Tidsramme: 24 months
|
Incident cardiovascular events during follow-up
|
24 months
|
|
Thromboembolic events
Tidsramme: 24 months
|
Incident venous or arterial thromboembolic events
|
24 months
|
|
Infections
Tidsramme: 24 months
|
Incident infections requiring medical evaluation or treatment
|
24 months
|
|
Hospitalization
Tidsramme: 24 months
|
All-cause hospitalization
|
24 months
|
Samarbejdspartnere og efterforskere
Sponsor
Efterforskere
- Studieleder: Evangelia Dounousi, Medical Degree, University of Ioannina
Publikationer og nyttige links
Generelle publikationer
- Beck LH Jr, Bonegio RG, Lambeau G, Beck DM, Powell DW, Cummins TD, Klein JB, Salant DJ. M-type phospholipase A2 receptor as target antigen in idiopathic membranous nephropathy. N Engl J Med. 2009 Jul 2;361(1):11-21. doi: 10.1056/NEJMoa0810457.
- Rosenzwajg M, Languille E, Debiec H, Hygino J, Dahan K, Simon T, Klatzmann D, Ronco P. B- and T-cell subpopulations in patients with severe idiopathic membranous nephropathy may predict an early response to rituximab. Kidney Int. 2017 Jul;92(1):227-237. doi: 10.1016/j.kint.2017.01.012. Epub 2017 Mar 15.
- Cantarelli C, Jarque M, Angeletti A, Manrique J, Hartzell S, O'Donnell T, Merritt E, Laserson U, Perin L, Donadei C, Anderson L, Fischman C, Chan E, Draibe J, Fulladosa X, Torras J, Riella LV, La Manna G, Fiaccadori E, Maggiore U, Bestard O, Cravedi P. A Comprehensive Phenotypic and Functional Immune Analysis Unravels Circulating Anti-Phospholipase A2 Receptor Antibody Secreting Cells in Membranous Nephropathy Patients. Kidney Int Rep. 2020 Aug 1;5(10):1764-1776. doi: 10.1016/j.ekir.2020.07.028. eCollection 2020 Oct.
- Watts AJB, Keller KH, Lerner G, Rosales I, Collins AB, Sekulic M, Waikar SS, Chandraker A, Riella LV, Alexander MP, Troost JP, Chen J, Fermin D, Yee JL, Sampson MG, Beck LH Jr, Henderson JM, Greka A, Rennke HG, Weins A. Discovery of Autoantibodies Targeting Nephrin in Minimal Change Disease Supports a Novel Autoimmune Etiology. J Am Soc Nephrol. 2022 Jan;33(1):238-252. doi: 10.1681/ASN.2021060794. Epub 2021 Nov 3.
- Yap HK, Cheung W, Murugasu B, Sim SK, Seah CC, Jordan SC. Th1 and Th2 cytokine mRNA profiles in childhood nephrotic syndrome: evidence for increased IL-13 mRNA expression in relapse. J Am Soc Nephrol. 1999 Mar;10(3):529-37. doi: 10.1681/ASN.V103529.
- Ishimoto T, Shimada M, Araya CE, Huskey J, Garin EH, Johnson RJ. Minimal change disease: a CD80 podocytopathy? Semin Nephrol. 2011 Jul;31(4):320-5. doi: 10.1016/j.semnephrol.2011.06.002.
- Hengel FE, Dehde S, Lasse M, Zahner G, Seifert L, Schnarre A, Kretz O, Demir F, Pinnschmidt HO, Grahammer F, Lucas R, Mehner LM, Zimmermann T, Billing AM, Oh J, Mitrotti A, Pontrelli P, Debiec H, Dossier C, Colucci M, Emma F, Smoyer WE, Weins A, Schaefer F, Alachkar N, Diemert A, Hogan J, Hoxha E, Wiech T, Rinschen MM, Ronco P, Vivarelli M, Gesualdo L, Tomas NM, Huber TB; International Society of Glomerular Disease. Autoantibodies Targeting Nephrin in Podocytopathies. N Engl J Med. 2024 Aug 1;391(5):422-433. doi: 10.1056/NEJMoa2314471. Epub 2024 May 25.
- Bertelli R, Bonanni A, Di Donato A, Cioni M, Ravani P, Ghiggeri GM. Regulatory T cells and minimal change nephropathy: in the midst of a complex network. Clin Exp Immunol. 2016 Feb;183(2):166-74. doi: 10.1111/cei.12675. Epub 2015 Oct 12.
- Logt AV, Justino J, Vink CH, van den Brand J, Debiec H, Lambeau G, Wetzels JF. Anti-PLA2R1 Antibodies as Prognostic Biomarker in Membranous Nephropathy. Kidney Int Rep. 2021 Apr 22;6(6):1677-1686. doi: 10.1016/j.ekir.2021.04.002. eCollection 2021 Jun.
- Hou J, Zhang M, Ding Y, Wang X, Li T, Gao P, Jiang Y. Circulating CD14+CD163+CD206+ M2 Monocytes Are Increased in Patients with Early Stage of Idiopathic Membranous Nephropathy. Mediators Inflamm. 2018 Jun 21;2018:5270657. doi: 10.1155/2018/5270657. eCollection 2018.
- Gaggar P, Madipally R, Raju SB. Rituximab, Use and B Cell Depletion in Patients with Membranous Nephropathy- A Retrospective, Observational Study. Indian J Nephrol. 2023 Sep-Oct;33(5):356-361. doi: 10.4103/ijn.ijn_62_22. Epub 2023 Apr 19.
- Duan S, Ye Y, Zhou Q, Hua H, Zeng M, Zhang C, Yuan Y, Xing C, Mao H, Zhang B. Systemic inflammation and B cell indices predict rituximab responses in membranous nephropathy. Clin Kidney J. 2025 Dec 18;19(2):sfaf396. doi: 10.1093/ckj/sfaf396. eCollection 2026 Feb.
- Colucci M, Carsetti R, Cascioli S, Casiraghi F, Perna A, Rava L, Ruggiero B, Emma F, Vivarelli M. B Cell Reconstitution after Rituximab Treatment in Idiopathic Nephrotic Syndrome. J Am Soc Nephrol. 2016 Jun;27(6):1811-22. doi: 10.1681/ASN.2015050523. Epub 2015 Nov 13.
- Cheddadi Y, El Mai M, Brglez V, Nahon Carzo S, Cremoni M, Teisseyre M, Seitz-Polski B. Early-Stage B-cells Predict Relapse After Rituximab Treatment in Patients With Membranous Nephropathy. Kidney Int Rep. 2026 Feb 19;11(5):106365. doi: 10.1016/j.ekir.2026.106365. eCollection 2026 May. No abstract available.
Datoer for undersøgelser
Studer store datoer
Studiestart (Faktiske)
Primær færdiggørelse (Faktiske)
Studieafslutning (Faktiske)
Datoer for studieregistrering
Først indsendt
Først indsendt, der opfyldte QC-kriterier
Først opslået (Faktiske)
Opdateringer af undersøgelsesjournaler
Sidste opdatering sendt (Faktiske)
Sidste opdatering indsendt, der opfyldte kvalitetskontrolkriterier
Sidst verificeret
Mere information
Begreber relateret til denne undersøgelse
Nøgleord
Yderligere relevante MeSH-vilkår
- Urogenitale sygdomme
- Mandlige urogenitale sygdomme
- Nyresygdomme
- Urologiske sygdomme
- Urogenitale sygdomme hos kvinder
- Kvinders urogenitale sygdomme og graviditetskomplikationer
- Autoimmune sygdomme
- Sygdomme i immunsystemet
- Glomerulonefritis
- Nefritis
- Nefrose
- Nefrotisk syndrom
- Glomerulonephritis, Membranøs
- Glomerulosklerose, Focal Segmental
- Nephrosis, Lipoid
- Makulær dystrofi, hornhindetype 1
- Hormoner
- Hormoner, hormonsubstitutter og hormonantagonister
- Aminosyrer, peptider og proteiner
- Proteiner
- Antistoffer, monoklonal
- Antistoffer
- Immunoglobuliner
- Immunoproteiner
- Blodproteiner
- Serum globuliner
- Globuliner
- Antistoffer, monoklonal, murint afledt
- Rituximab
- Adrenale cortexhormoner
Andre undersøgelses-id-numre
- 695
Plan for individuelle deltagerdata (IPD)
Planlægger du at dele individuelle deltagerdata (IPD)?
IPD-planbeskrivelse
IPD-delingsadgangskriterier
IPD-deling Understøttende informationstype
- STUDY_PROTOCOL
Lægemiddel- og udstyrsoplysninger, undersøgelsesdokumenter
Studerer et amerikansk FDA-reguleret lægemiddelprodukt
Studerer et amerikansk FDA-reguleret enhedsprodukt
Disse oplysninger blev hentet direkte fra webstedet clinicaltrials.gov uden ændringer. Hvis du har nogen anmodninger om at ændre, fjerne eller opdatere dine undersøgelsesoplysninger, bedes du kontakte register@clinicaltrials.gov. Så snart en ændring er implementeret på clinicaltrials.gov, vil denne også blive opdateret automatisk på vores hjemmeside .