A Study to Investigate Pharmacokinetics, Pharmacodynamics, and Safety of Subcutaneous Anifrolumab in Pediatric Participants 5 to < 18 Years of Age With Systemic Lupus Erythematosus
A Multicenter, Open-Label, Phase II Study to Evaluate the Pharmacokinetics, Pharmacodynamics, and Safety of Subcutaneous Anifrolumab in Pediatric Participants 5 to < 18 Years of Age With Systemic Lupus Erythematosus
調査の概要
詳細な説明
This is an open-label, multicenter study.
The study includes -
- Screening Period of up to 35 days
- Period A (12-week, open-label treatment period)
- Period B (a possible 12-week dosing regimen adjustment period, if required)
- Treatment Extension Period (up-to-40-week, optional)
- Period C (a 12-week safety follow-up period)
The study intervention (anifrolumab) will be administered subcutaneously using an accessorized pre-filled syringe (APFS) in 2 cohorts.
研究の種類
入学 (推定)
段階
- フェーズ2
連絡先と場所
研究連絡先
- 名前:AstraZeneca Clinical Study Information Center
- 電話番号:1-877-240-9479
- メール:information.center@astrazeneca.com
参加基準
適格基準
就学可能な年齢
- 子
健康ボランティアの受け入れ
説明
Inclusion Criteria:
- Diagnosis of SLE.
- Must be receiving at least one of the following SoC regimens for ≥ 4 weeks: oral glucocorticoids (≤1.0 mg/kg/day or ≤ 40 mg/day prednisone equivalent), antimalarials (hydroxychloroquine, chloroquine, or quinacrine), or a single permitted immunosuppressant (azathioprine, mycophenolate mofetil/mycophenolic acid, methotrexate, mizoribine, or tacrolimus) within specified dose limits.
- Participant must have moderate to severe active SLE disease defined as Systemic lupus erythematosus disease activity index 2000 (SLEDAI-2K) ≥ 6 total points.
- Body weight ≥ 15 kg.
- Participants must agree to follow study specific contraception requirements as per local regulations.
Exclusion Criteria:
- Known diagnosis of an IFN mediated autoinflammatory interferonopathy.
- History of, or current diagnosis of, clinically significant non-SLE related vasculitides.
- Active, severe SLE-driven renal disease with significant proteinuria.
- Active severe or unstable neuropsychiatric SLE including but not limited to aseptic meningitis; cerebral vasculitis; myelopathy; demyelination syndromes (ascending, transverse, acute inflammatory demyelinating polyradiculopathy); acute confusional state; impaired level of consciousness; psychosis; acute stroke or stroke syndrome; cranial neuropathy; status epilepticus; cerebellar ataxia; and mononeuritis multiplex.
- In participants ≥ 11 years of age, a history or evidence of suicidal ideation (severity of 4 [active: method and intent, but no plan] or 5 [active: method, intent, and plan]) within the past 6 months; or any suicidal behavior within the past 12 months or recurrent suicidal behavior in the lifetime of the participant based on an assessment with the Columbia suicide severity rating scale (C-SSRS).
- History of, or current diagnosis of, catastrophic antiphospholipid syndrome (APS).
- History of recurrent or opportunistic infection requiring hospitalization and intravenous (IV) antibiotics.
- Known history of a primary immunodeficiency, splenectomy, or any underlying condition that predisposes the participant to infection, or a positive result for human immunodeficiency virus (HIV) infection.
- Active hepatitis B and C infection.
- Any active or recent herpes zoster (HZ) infection that has not completely resolved within 12 weeks prior to study entry or that emerges between screening and Day 1.
- Any history of severe or recurrent HZ, including non-cutaneous HZ, herpes encephalitis, ophthalmic herpes, or 2 or more prior HZ episodes.
- Any cytomegalovirus (CMV) or Epstein Barr virus (EBV) infection that has not completely resolved.
- History of cancer.
- Prior receipt of anifrolumab.
- Prior treatment with directly acting cytotoxic B-cell depleting therapeutics.
- A known history of allergy or reaction to any component of the study intervention formulation or history of anaphylaxis to any human gamma globulin therapy, human proteins, or monoclonal antibodies (mAbs).
研究計画
研究はどのように設計されていますか?
デザインの詳細
- 主な目的:処理
- 割り当て:非ランダム化
- 介入モデル:順次割り当て
- マスキング:なし(オープンラベル)
武器と介入
参加者グループ / アーム |
介入・治療 |
|---|---|
|
実験的:Cohort 1 (body weight > 40 kg)
Participants with body weight > 40 kg will receive anifrolumab as an injection in APFS.
|
Anifrolumab will be administered as a SC injection using an APFS.
他の名前:
|
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実験的:Cohort 2 (body weight ≥ 15 to ≤ 40 kg)
Participants with body weight ≥ 15 to ≤ 40 kg will receive anifrolumab as an injection in APFS.
|
Anifrolumab will be administered as a SC injection using an APFS.
他の名前:
|
この研究は何を測定していますか?
主要な結果の測定
結果測定 |
メジャーの説明 |
時間枠 |
|---|---|---|
|
Maximum observed serum (peak) concentration (Cmax)
時間枠:Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (Cmax) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Area under the serum concentration-time curve (AUC)
時間枠:Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (AUC) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Time to maximum plasma concentration (tmax)
時間枠:Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (tmax) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Apparent total body clearance of drug from plasma (CL/F)
時間枠:Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (CL/F) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Trough drug concentration at steady state (Ctrough,ss)
時間枠:At Week 12
|
To characterize PK (Ctrough,ss) of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12
|
二次結果の測定
結果測定 |
メジャーの説明 |
時間枠 |
|---|---|---|
|
Suppression of type I IFN 21-gene signature
時間枠:At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in anti-double-stranded deoxyribonucleic acid (dsDNA) antibodies
時間枠:At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in complement component 3 (C3) levels
時間枠:At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in complement component 4 (C4) levels
時間枠:At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in total hemolytic complement (CH50) levels
時間枠:At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Number and percentage of participants who develop anti drug antibody (ADA) against anifrolumab
時間枠:From Day 1 to Week 52
|
To evaluate the immunogenicity of anifrolumab in pediatric participants with SLE following SC administration.
|
From Day 1 to Week 52
|
その他の成果指標
結果測定 |
メジャーの説明 |
時間枠 |
|---|---|---|
|
Number with participants with adverse events (AEs), serious adverse events (SAEs) and adverse events of special interest (AESIs)
時間枠:Up to follow-up visit (12 weeks post last dose of study intervention) (approximately 64 weeks)
|
To evaluate the safety and tolerability of anifrolumab in pediatric participants with SLE following SC administration.
|
Up to follow-up visit (12 weeks post last dose of study intervention) (approximately 64 weeks)
|
協力者と研究者
スポンサー
研究記録日
主要日程の研究
研究開始 (推定)
一次修了 (推定)
研究の完了 (推定)
試験登録日
最初に提出
QC基準を満たした最初の提出物
最初の投稿 (実際)
学習記録の更新
投稿された最後の更新 (実際)
QC基準を満たした最後の更新が送信されました
最終確認日
詳しくは
本研究に関する用語
キーワード
追加の関連 MeSH 用語
その他の研究ID番号
- D3465C00008
- 2025-524578-41-00 (Ctis)
- EMA/PE/0000246211 (その他の識別子:Pediatric investigation plan [PIP])
個々の参加者データ (IPD) の計画
個々の参加者データ (IPD) を共有する予定はありますか?
IPD プランの説明
Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal Vivli.org. All requests will be evaluated as per the AZ disclosure commitment:
https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.
IPD 共有時間枠
IPD 共有アクセス基準
IPD 共有サポート情報タイプ
- STUDY_PROTOCOL
- SAP
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米国FDA規制医薬品の研究
米国FDA規制機器製品の研究
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