- ICH GCP
- Registro de ensayos clínicos de EE. UU.
- Ensayo clínico NCT07630714
A Study to Investigate Pharmacokinetics, Pharmacodynamics, and Safety of Subcutaneous Anifrolumab in Pediatric Participants 5 to < 18 Years of Age With Systemic Lupus Erythematosus
A Multicenter, Open-Label, Phase II Study to Evaluate the Pharmacokinetics, Pharmacodynamics, and Safety of Subcutaneous Anifrolumab in Pediatric Participants 5 to < 18 Years of Age With Systemic Lupus Erythematosus
Descripción general del estudio
Estado
Condiciones
Intervención / Tratamiento
Descripción detallada
This is an open-label, multicenter study.
The study includes -
- Screening Period of up to 35 days
- Period A (12-week, open-label treatment period)
- Period B (a possible 12-week dosing regimen adjustment period, if required)
- Treatment Extension Period (up-to-40-week, optional)
- Period C (a 12-week safety follow-up period)
The study intervention (anifrolumab) will be administered subcutaneously using an accessorized pre-filled syringe (APFS) in 2 cohorts.
Tipo de estudio
Inscripción (Estimado)
Fase
- Fase 2
Contactos y Ubicaciones
Estudio Contacto
- Nombre: AstraZeneca Clinical Study Information Center
- Número de teléfono: 1-877-240-9479
- Correo electrónico: information.center@astrazeneca.com
Criterios de participación
Criterio de elegibilidad
Edades elegibles para estudiar
- Niño
Acepta Voluntarios Saludables
Descripción
Inclusion Criteria:
- Diagnosis of SLE.
- Must be receiving at least one of the following SoC regimens for ≥ 4 weeks: oral glucocorticoids (≤1.0 mg/kg/day or ≤ 40 mg/day prednisone equivalent), antimalarials (hydroxychloroquine, chloroquine, or quinacrine), or a single permitted immunosuppressant (azathioprine, mycophenolate mofetil/mycophenolic acid, methotrexate, mizoribine, or tacrolimus) within specified dose limits.
- Participant must have moderate to severe active SLE disease defined as Systemic lupus erythematosus disease activity index 2000 (SLEDAI-2K) ≥ 6 total points.
- Body weight ≥ 15 kg.
- Participants must agree to follow study specific contraception requirements as per local regulations.
Exclusion Criteria:
- Known diagnosis of an IFN mediated autoinflammatory interferonopathy.
- History of, or current diagnosis of, clinically significant non-SLE related vasculitides.
- Active, severe SLE-driven renal disease with significant proteinuria.
- Active severe or unstable neuropsychiatric SLE including but not limited to aseptic meningitis; cerebral vasculitis; myelopathy; demyelination syndromes (ascending, transverse, acute inflammatory demyelinating polyradiculopathy); acute confusional state; impaired level of consciousness; psychosis; acute stroke or stroke syndrome; cranial neuropathy; status epilepticus; cerebellar ataxia; and mononeuritis multiplex.
- In participants ≥ 11 years of age, a history or evidence of suicidal ideation (severity of 4 [active: method and intent, but no plan] or 5 [active: method, intent, and plan]) within the past 6 months; or any suicidal behavior within the past 12 months or recurrent suicidal behavior in the lifetime of the participant based on an assessment with the Columbia suicide severity rating scale (C-SSRS).
- History of, or current diagnosis of, catastrophic antiphospholipid syndrome (APS).
- History of recurrent or opportunistic infection requiring hospitalization and intravenous (IV) antibiotics.
- Known history of a primary immunodeficiency, splenectomy, or any underlying condition that predisposes the participant to infection, or a positive result for human immunodeficiency virus (HIV) infection.
- Active hepatitis B and C infection.
- Any active or recent herpes zoster (HZ) infection that has not completely resolved within 12 weeks prior to study entry or that emerges between screening and Day 1.
- Any history of severe or recurrent HZ, including non-cutaneous HZ, herpes encephalitis, ophthalmic herpes, or 2 or more prior HZ episodes.
- Any cytomegalovirus (CMV) or Epstein Barr virus (EBV) infection that has not completely resolved.
- History of cancer.
- Prior receipt of anifrolumab.
- Prior treatment with directly acting cytotoxic B-cell depleting therapeutics.
- A known history of allergy or reaction to any component of the study intervention formulation or history of anaphylaxis to any human gamma globulin therapy, human proteins, or monoclonal antibodies (mAbs).
Plan de estudios
¿Cómo está diseñado el estudio?
Detalles de diseño
- Propósito principal: Tratamiento
- Asignación: No aleatorizado
- Modelo Intervencionista: Asignación Secuencial
- Enmascaramiento: Ninguno (etiqueta abierta)
Armas e Intervenciones
Grupo de participantes/brazo |
Intervención / Tratamiento |
|---|---|
|
Experimental: Cohort 1 (body weight > 40 kg)
Participants with body weight > 40 kg will receive anifrolumab as an injection in APFS.
|
Anifrolumab will be administered as a SC injection using an APFS.
Otros nombres:
|
|
Experimental: Cohort 2 (body weight ≥ 15 to ≤ 40 kg)
Participants with body weight ≥ 15 to ≤ 40 kg will receive anifrolumab as an injection in APFS.
|
Anifrolumab will be administered as a SC injection using an APFS.
Otros nombres:
|
¿Qué mide el estudio?
Medidas de resultado primarias
Medida de resultado |
Medida Descripción |
Periodo de tiempo |
|---|---|---|
|
Maximum observed serum (peak) concentration (Cmax)
Periodo de tiempo: Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (Cmax) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Area under the serum concentration-time curve (AUC)
Periodo de tiempo: Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (AUC) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Time to maximum plasma concentration (tmax)
Periodo de tiempo: Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (tmax) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Apparent total body clearance of drug from plasma (CL/F)
Periodo de tiempo: Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
To characterize PK (CL/F) of anifrolumab in pediatric participants with SLE following SC administration.
|
Cohort 1: From Day 1 to Day 8; Cohort 2: From Day 1 to Day 11
|
|
Trough drug concentration at steady state (Ctrough,ss)
Periodo de tiempo: At Week 12
|
To characterize PK (Ctrough,ss) of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12
|
Medidas de resultado secundarias
Medida de resultado |
Medida Descripción |
Periodo de tiempo |
|---|---|---|
|
Suppression of type I IFN 21-gene signature
Periodo de tiempo: At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in anti-double-stranded deoxyribonucleic acid (dsDNA) antibodies
Periodo de tiempo: At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in complement component 3 (C3) levels
Periodo de tiempo: At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in complement component 4 (C4) levels
Periodo de tiempo: At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Change from baseline in total hemolytic complement (CH50) levels
Periodo de tiempo: At Week 12 and 52
|
To characterize PD of anifrolumab in pediatric participants with SLE following SC administration.
|
At Week 12 and 52
|
|
Number and percentage of participants who develop anti drug antibody (ADA) against anifrolumab
Periodo de tiempo: From Day 1 to Week 52
|
To evaluate the immunogenicity of anifrolumab in pediatric participants with SLE following SC administration.
|
From Day 1 to Week 52
|
Otras medidas de resultado
Medida de resultado |
Medida Descripción |
Periodo de tiempo |
|---|---|---|
|
Number with participants with adverse events (AEs), serious adverse events (SAEs) and adverse events of special interest (AESIs)
Periodo de tiempo: Up to follow-up visit (12 weeks post last dose of study intervention) (approximately 64 weeks)
|
To evaluate the safety and tolerability of anifrolumab in pediatric participants with SLE following SC administration.
|
Up to follow-up visit (12 weeks post last dose of study intervention) (approximately 64 weeks)
|
Colaboradores e Investigadores
Patrocinador
Fechas de registro del estudio
Fechas importantes del estudio
Inicio del estudio (Estimado)
Finalización primaria (Estimado)
Finalización del estudio (Estimado)
Fechas de registro del estudio
Enviado por primera vez
Primero enviado que cumplió con los criterios de control de calidad
Publicado por primera vez (Actual)
Actualizaciones de registros de estudio
Última actualización publicada (Actual)
Última actualización enviada que cumplió con los criterios de control de calidad
Última verificación
Más información
Términos relacionados con este estudio
Palabras clave
Términos MeSH relevantes adicionales
- Enfermedades del tejido conectivo
- Enfermedades autoinmunes
- Enfermedades del sistema inmunológico
- Infecciones
- Infecciones por bacterias grampositivas
- Infecciones bacterianas
- Infecciones bacterianas y micosis
- Infecciones por Actinomycetales
- Infecciones por micobacterias
- Enfermedades de la piel y del tejido conectivo
- Lupus Eritematoso Sistémico
- Infecciones por Mycobacterium, no tuberculosas
- anifrolumab
Otros números de identificación del estudio
- D3465C00008
- 2025-524578-41-00 (Ctis)
- EMA/PE/0000246211 (Otro identificador: Pediatric investigation plan [PIP])
Plan de datos de participantes individuales (IPD)
¿Planea compartir datos de participantes individuales (IPD)?
Descripción del plan IPD
Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal Vivli.org. All requests will be evaluated as per the AZ disclosure commitment:
https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared.
Marco de tiempo para compartir IPD
Criterios de acceso compartido de IPD
Tipo de información de apoyo para compartir IPD
- PROTOCOLO DE ESTUDIO
- SAVIA
Información sobre medicamentos y dispositivos, documentos del estudio
Estudia un producto farmacéutico regulado por la FDA de EE. UU.
Estudia un producto de dispositivo regulado por la FDA de EE. UU.
Esta información se obtuvo directamente del sitio web clinicaltrials.gov sin cambios. Si tiene alguna solicitud para cambiar, eliminar o actualizar los detalles de su estudio, comuníquese con register@clinicaltrials.gov. Tan pronto como se implemente un cambio en clinicaltrials.gov, también se actualizará automáticamente en nuestro sitio web. .