- ICH GCP
- Registr klinických studií v USA
- Klinická studie NCT07577414
Safety and Efficacy of Fetoscopic Endoluminal Tracheal Occlusion (FETO) in Congenital Diaphragmatic Hernia (CDH)
3. června 2026 aktualizováno: Dr Erin Perrone
Infant Survival and Long-term Outcome Following Fetoscopic Endoluminal Tracheal Occlusion in Severe Left and Right Congenital Diaphragmatic Hernia, A Phase III Trial
The purpose of the study is to determine if babies with left or right-sided CDH that undergo the FETO procedure survive more often and have fewer long-term complications than babies that have similar left or right-sided CDH that elect not to have the FETO procedure performed during pregnancy.
Přehled studie
Postavení
Nábor
Podmínky
Typ studie
Intervenční
Zápis (Odhadovaný)
40
Fáze
- Nelze použít
Kontakty a umístění
Tato část poskytuje kontaktní údaje pro ty, kteří studii provádějí, a informace o tom, kde se tato studie provádí.
Studijní kontakt
- Jméno: Erin Perrone, MD
- Telefonní číslo: 734-936-8464
- E-mail: eperrone@med.umich.edu
Studijní záloha kontaktů
- Jméno: Irene Carter
- Telefonní číslo: 734-615-3883
- E-mail: irenestc@med.umich.edu
Studijní místa
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Michigan
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Ann Arbor, Michigan, Spojené státy, 48109
- Nábor
- University of Michigan
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Kontakt:
- Irene Carter
- Telefonní číslo: 734-615-3883
- E-mail: irenestc@med.umich.edu
-
Vrchní vyšetřovatel:
- Erin Perrone, MD
-
-
Kritéria účasti
Výzkumníci hledají lidi, kteří odpovídají určitému popisu, kterému se říká kritéria způsobilosti. Některé příklady těchto kritérií jsou celkový zdravotní stav osoby nebo předchozí léčba.
Kritéria způsobilosti
Věk způsobilý ke studiu
- Dospělý
- Starší dospělý
Přijímá zdravé dobrovolníky
Ne
Popis
FETO Intervention Arm: Inclusion Criteria:
- Provision of signed and dated informed consent form
- Stated willingness to comply with all study procedures and availability (meets psychosocial criteria below) for the duration of the study
- Pregnant women, age 18 years and older
- Singleton pregnancy
- Normal fetal karyotype, Chromosomal Microarray (CMA) with non-pathologic variants, Whole Exome Sequencing (WES) or Whole Genome Sequencing (WGS). Results by fluorescence in situ hybridization (FISH) will be acceptable if the patient is >26 weeks.
- Gestational age at enrollment prior to 29w6d
Fetal CDH with intrathoracic liver herniation with either:
- Isolated left CDH with Observed/Expected (o/e) Lung to Head Ratio (LHR) <30% at enrollment (18w0d-29w5d)
- Isolated right CDH with o/e LHR <45% at enrollment (18w0d-29w5d)
- Cervical length by transvaginal ultrasound >20 mm within 24hours of FETO procedure
Meets psychosocial criteria
- Willing to reside within 30 minutes of Von Voigtlander Women's Hospital and ability to maintain follow up appointments
- Patient has a support person (e.g. spouse, partner, friend, parent) that is available to stay with participant for the duration of the pregnancy near Von Voigtlander Women's Hospital
- Willing to comply with restrictions of daily living including inability to exercise, have intercourse, or return to work (work from home approved by Principal Investigator is okay)
Expectant Management Arm: Inclusion Criteria:
- Provision of signed and dated informed consent form
- Stated willingness to comply with all study procedures and availability (meets psychosocial criteria below) for the duration of the study
- Pregnant women, age 18 years and older
- Singleton pregnancy
- Normal fetal karyotype, CMA with non-pathologic variants, WES or WGS. Results by fluorescence in situ hybridization (FISH) will be acceptable if the patient is >26 weeks. (non-intervention arm can have karyotype or microarray prenatally or postnatally)
- Gestational age at enrollment prior to 29w6d
- Fetal CDH with intrathoracic liver herniation with either:
- Isolated left CDH with o/e LHR <30% at enrollment (18w0d-29w5d)
- Isolated right CDH with o/e LHR <45% at enrollment (18w0d-29w5d)
Meets psychosocial criteria
- Ability to maintain follow up appointments
FETO Intervention Arm: Exclusion Criteria:
- Patient <18 years of age
- Multi-fetal pregnancy
- History of natural rubber latex allergy
- Preterm labor, short cervix (<20mm within 24 hours of FETO balloon insertion procedure), or uterine anomaly strongly predisposing to preterm labor, placenta previa
- History of incompetent cervix with or without cerclage
Psychosocial ineligibility
- Inability to reside within 30 minutes of Von Voigtlander Women's Hospital or inability to maintain follow up appointments
- Social work will meet with each patient to evaluate the social situation and support system. Identifiable issues of social instability or compliance with the protocol will exclude participant as a potential candidate (per protocol).
- Bilateral CDH, isolated Left Congenital Diaphragmatic Hernia (LCDH) with o/e LHR > 30% (measured at 180 to 295 weeks), isolated Right Congenital Diaphragmatic Hernia (RCDH) with o/e LHR >45% (measured at 180 to 295 weeks) as determined by ultrasound
- No liver herniation into the thoracic cavity.
- Additional fetal anomaly or genetic/chromosomal abnormalities recognized to alter survival prognosis (i.e., congenital heart disease) or presence of an underlying genetic syndrome (i.e. Fryns) by ultrasound, MRI or echocardiogram at the fetal treatment center.
- Maternal contraindications to elective fetoscopic surgery or severe maternal medical condition in pregnancy
- Placental abnormalities (previa, abruption, accreta) known at time of enrollment and/or surgery
- Maternal-fetal Rh isoimmunization, Kell sensitization, or neonatal alloimmune thrombocytopenia affecting the current pregnancy
- Maternal Human Immunodeficiency Virus (HIV), Hepatitis B with positive surface antigen, Hepatitis C with presence of virus in maternal blood due to risk of fetal transmission during the procedure. If the patient's HIV or Hepatitis status is unknown, the patient must be tested and found to have negative results before enrollment
- No safe or technically feasible fetoscopic approach to balloon placement
- Uterine anomalies such as large fibroids or Mullerian duct abnormality
- Participation in another intervention study that influences maternal and fetal morbidity and mortality or participation in this trial in a previous pregnancy
Expectant Management Arm: Exclusion Criteria:
- Patient <18 years of age
- Multi-fetal pregnancy
- Preterm labor, short cervix (<20mm), or uterine anomaly strongly predisposing to preterm labor, placenta previa
- History of incompetent cervix with or without cerclage
Psychosocial ineligibility
- Inability to maintain follow up appointments
- Social work will meet with each patient to evaluate the social situation and support system. Identifiable issues of social instability or compliance with the protocol will exclude participant as a potential candidate.
- Bilateral CDH, isolated LCDH with o/e LHR > 30% (measured at 180 to 295 weeks), isolated RCDH with o/e LHR >45% (measured at 180 to 295 weeks), or any isolated CDH without intrathoracic liver herniation as determined by ultrasound
- Additional fetal anomaly or genetic/chromosomal abnormalities recognized to alter survival prognosis (i.e. congenital heart disease) or presence of an underlying genetic syndrome (i.e. Fryns) by ultrasound, Magnetic Resonance Imaging (MRI) or echocardiogram at the fetal treatment center Placental abnormalities (per protocol)
- Participation in another intervention study that influences maternal and fetal morbidity and mortality or participation in this trial in a previous pregnancy
Studijní plán
Tato část poskytuje podrobnosti o studijním plánu, včetně toho, jak je studie navržena a co studie měří.
Jak je studie koncipována?
Detaily designu
- Primární účel: Léčba
- Přidělení: Nerandomizované
- Intervenční model: Paralelní přiřazení
- Maskování: Žádné (otevřený štítek)
Zbraně a zásahy
Skupina účastníků / Arm |
Intervence / Léčba |
|---|---|
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Experimentální: FETO surgery Intervention Arm
Eligible participants that choose the FETO Intervention Arm, will undergo two surgeries, one to place the balloon and a second to remove the balloon before delivery.
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K tomu dojde mezi březostí 27w0d - 29w6d.
Balónek bude odstraněn přibližně ve 34. týdnu těhotenství.
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Žádný zásah: Expectant Management Arm
Participants choose to undergo the expectant management, or routine care, of carrying a baby with Congenital Diaphragmatic Hernia (CDH).
Participants will undergo a comprehensive fetal evaluation at Michigan Medicine's Fetal Diagnosis and Treatment Center (FDTC) to confirm the diagnosis and severity of the CDH.
Eligibility will be based on the results of the clinical assessment.
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Co je měření studie?
Primární výstupní opatření
Měření výsledku |
Popis opatření |
Časové okno |
|---|---|---|
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Compare neonatal survival to discharge in LCDH
Časové okno: 6-12 months (birth to discharge)
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6-12 months (birth to discharge)
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Compare neonatal survival to discharge in RCDH
Časové okno: 6-12 months (birth to discharge)
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6-12 months (birth to discharge)
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Number of successful placements the of FETO balloon Gestational age of 27 weeks 0 days gestation to 29 weeks 6 days gestation
Časové okno: 27weeks 0 days gestation to 29 weeks 6 days gestation
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27weeks 0 days gestation to 29 weeks 6 days gestation
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Number of successful retrievals/puncture of the FETO balloon Gestational age of 33 weeks 0 days to 35 weeks 0 days
Časové okno: Removal prior to delivery at approximately 34 weeks of gestation
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Removal prior to delivery at approximately 34 weeks of gestation
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Number of FETO procedure complications
Časové okno: Balloon placement to delivery (27 weeks up to delivery approximately 40 weeks)
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FETO procedure complications include: Failure of the FETO insertion procedure; FETO device dislodgement potentially requiring a second FETO insertion; Fetal intraoperative injury; Procedural hemorrhage: Bleeding from insertion site or Abruptions; Post-procedural hemorrhage; Preterm premature rupture of membranes; Preterm delivery; Chorioamnion separation; Chorioamnionitis; Polyhydramnios; Oligohydramnios; Emergent removal due to obstetrical complication; Failed percutaneous or fetoscopic removal requiring cesarean section or Ex-Utero Intrapartum Therapy(EXIT) procedure for removal; Neonatal death due to asphyxia if delivery before FETO removal; Non-reassuring fetal heart rate monitoring.
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Balloon placement to delivery (27 weeks up to delivery approximately 40 weeks)
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Sekundární výstupní opatření
Měření výsledku |
Popis opatření |
Časové okno |
|---|---|---|
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Fetal lung growth difference on MRI via o/e Total Fetal Lung Volume (TFLV) (FETO Intervention Arm)
Časové okno: Baseline (prior to balloon placement) and approximately 2 weeks after balloon retrieval
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Fetal MRI done prior to balloon placement and again done at approximately 2 weeks of balloon retrieval.
Fetal lung growth (difference between 1st and 2nd MRIs will be calculated for FETO intervention arm only).
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Baseline (prior to balloon placement) and approximately 2 weeks after balloon retrieval
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Fetal lung growth difference based on prenatal ultrasound via o/e LHR (Both Arms)
Časové okno: Baseline (prior to balloon placement) and immediately prior to balloon removal and SOC arm 29 + 1 week and 34 +1 week
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Prenatal ultrasound (US) will measure the o/e LHR at weekly visits while the balloon is in place (FETO intervention arm) or at routine visits per standard of care (SOC) (expectant arm).
Fetal lung growth will be calculated as the difference between the o/e LHR pre- balloon placement (or 29 + 1 week in control) and the o/e LHR immediately prior to balloon removal/puncture (or 34 + 1 week in control).
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Baseline (prior to balloon placement) and immediately prior to balloon removal and SOC arm 29 + 1 week and 34 +1 week
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Long-term outcome measure infant survival rate
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Presence of pulmonary hypertension
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Determination of the ratio of the tricuspid regurgitation jet (estimation of the right ventricular systolic pressure) to systemic blood pressure where the is an objective measurement used to estimate the pulmonary artery pressure.
Will be recorded as absent/none, systemic or suprasystemic.
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Presence of need for supplemental oxygen
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Periventricular leukomalacia at <2 months postnatally
Časové okno: After birth at 2 months
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After birth at 2 months
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Infant sepsis
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Intraventricular hemorrhage (grade 0-III)
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Retinopathy of prematurity (grade 3 or higher)
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Gastroesophageal reflux
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Number and cause of infant hospital readmissions
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Long-term outcome measure childhood growth failure
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Childhood growth failure: weight gain velocity or decline >2 in weight, for length Z score.
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Recurrence of CDH repair
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Bowel obstruction
Časové okno: After birth at 6, 12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6, 12, 18, and 24 months (+ 2 months) of corrected age
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Neurodevelopmental delay
Časové okno: 24 months (+ 2 months) of corrected age
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Bayley Scales of Infant and Toddler Development- III(BSID)>2 Standard deviation (SD) below mean, or other categorization at 24 months
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24 months (+ 2 months) of corrected age
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Bronchopulmonary dysplasia
Časové okno: After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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After birth at 6,12, 18, and 24 months (+ 2 months) of corrected age
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Spolupracovníci a vyšetřovatelé
Zde najdete lidi a organizace zapojené do této studie.
Sponzor
Vyšetřovatelé
- Vrchní vyšetřovatel: Erin Perrone, MD, University of Michigan
Termíny studijních záznamů
Tato data sledují průběh záznamů studie a předkládání souhrnných výsledků na ClinicalTrials.gov. Záznamy ze studií a hlášené výsledky jsou před zveřejněním na veřejné webové stránce přezkoumány Národní lékařskou knihovnou (NLM), aby se ujistily, že splňují specifické standardy kontroly kvality.
Hlavní termíny studia
Začátek studia (Odhadovaný)
1. června 2026
Primární dokončení (Odhadovaný)
1. dubna 2030
Dokončení studie (Odhadovaný)
1. dubna 2031
Termíny zápisu do studia
První předloženo
3. května 2026
První předloženo, které splnilo kritéria kontroly kvality
3. května 2026
První zveřejněno (Aktuální)
11. května 2026
Aktualizace studijních záznamů
Poslední zveřejněná aktualizace (Aktuální)
4. června 2026
Odeslaná poslední aktualizace, která splnila kritéria kontroly kvality
3. června 2026
Naposledy ověřeno
1. května 2026
Více informací
Termíny související s touto studií
Klíčová slova
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Tyto informace byly beze změn načteny přímo z webu clinicaltrials.gov. Máte-li jakékoli požadavky na změnu, odstranění nebo aktualizaci podrobností studie, kontaktujte prosím register@clinicaltrials.gov. Jakmile bude změna implementována na clinicaltrials.gov, bude automaticky aktualizována i na našem webu .
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