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- Registro de ensayos clínicos de EE. UU.
- Ensayo clínico NCT07628933
A Phase I Trial of Umbilical Cord Mesenchymal Stromal Cells for Acute Ischemic Stroke
A Phase I Clinical Trial to Evaluate the Safety, Tolerability, and Preliminary Efficacy of Human Umbilical Cord-derived Mesenchymal Stromal Cell Injection in Patients With Acute Ischemic Stroke (AIS)
Study Methods: The trial consists of two phases, both including a placebo control.
Phase Ia (single-dose, dose-escalation): Three dose groups (low, medium, high) are set. This is a multicenter, randomized, double-blind, placebo-controlled, single-dose, dose-escalation trial. Dose escalation to the next level is permitted only after safety assessment at 28 days post-dose in the previous group.
Phase Ib (multiple-dose): Based on Phase Ia results, two dose groups will be selected. The product is administered on Day 0, Day 7, and Day 14 (3 doses total). The trial remains randomized, double-blind, and placebo-controlled.
Descripción general del estudio
Estado
Condiciones
Descripción detallada
Objective of this study: To preliminarily evaluate the safety and efficacy of human umbilical cord-derived mesenchymal stromal cell injection in the treatment of AIS.
Study methods: This trial is divided into two phases, both including a placebo control.
Phase I (Ia): A multicenter, randomized, double-blind, placebo-controlled, single-dose, dose-escalation trial. Three dose groups are set: low dose (5.0×10⁷ cells), medium dose (1.0×10⁸ cells), and high dose (2.0×10⁸ cells). The low-dose group enrolls 3-6 participants (all receiving the investigational product, with the first of the first 3 participants as a sentinel). The medium- and high-dose groups each enroll 8 participants (2 sentinels receiving the investigational product, and the remaining 6 randomized in a 2:1 ratio to the investigational product or placebo group). Phase Ia plans to enroll 19-22 participants. Dose escalation to the next dose group is permitted only after all participants in the previous dose group have completed dosing and been observed for at least 28 days with a favorable safety assessment.
Phase Ib: A multicenter, randomized, double-blind, placebo-controlled, dose-escalation, multiple-dose trial. Based on the results of Phase Ia, two dose groups will be selected. The initial plan is to administer the product on Day 0, Day 7, and Day 14 (3 doses in total). Each dose group enrolls 8 participants (6 receiving the investigational product, 2 receiving placebo), for a total of 16 participants. Escalation to the next higher dose group is permitted only after all participants in the previous dose group have completed the three doses and been observed for at least 28 days with a favorable safety assessment.
Study duration: 720 days
Tipo de estudio
Inscripción (Estimado)
Fase
- Fase 1
Contactos y Ubicaciones
Estudio Contacto
- Nombre: Yongjun Wang Chief Physician, Professor
- Número de teléfono: 010-59978538
- Correo electrónico: yongjunwang111@aliyun.com
Ubicaciones de estudio
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Beijing Municipality
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Beijing, Beijing Municipality, Porcelana
- Beijing Tiantan Hospital, Capital Medical University
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Contacto:
- Shu ya Li Chief Physician
- Número de teléfono: +86 13601367028
- Correo electrónico: shuyali85@163.com
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Criterios de participación
Criterio de elegibilidad
Edades elegibles para estudiar
- Adulto
- Adulto Mayor
Acepta Voluntarios Saludables
Descripción
Inclusion Criteria:
- Age ≥18 years, both genders included.
- Clinical diagnosis of anterior circulation ischemic stroke, and able to receive the investigational product within 48 hours after the onset of stroke symptoms.
- National Institutes of Health Stroke Scale (NIHSS) score of 6-20 (inclusive), with a score of <2 on item Ia of the NIHSS.
- Pre-stroke modified Rankin Scale (mRS) score ≤1.
- The participant voluntarily agrees to participate in this study, signs the informed consent form personally or via a legal guardian, and has good compliance.
Exclusion Criteria:
- Planned or already performed thrombectomy for the current stroke.
- Treatment with neuroprotective agents after the current stroke.
- History of cerebral hemorrhage, subarachnoid hemorrhage, or hemorrhagic transformation after the current ischemic stroke, and judged by the investigator to be unsuitable for participation in the clinical trial.
- Uncontrolled systemic diseases, including but not limited to: hypertension (systolic blood pressure >160 mmHg and/or diastolic blood pressure ≥100 mmHg), diabetes mellitus (acute diabetic complications such as ketoacidosis, hyperglycemic hyperosmolar state, lactic acidosis, or hypoglycemic coma within the past 3 months, or glycated hemoglobin >8.5%, or poorly controlled blood glucose [blood glucose >16.8 mmol/L or <2.8 mmol/L]), renal disease (eGFR <30 mL/min), liver failure (Child-Pugh Class C), severe heart failure (New York Heart Association [NYHA] Class IV), severe chronic respiratory disease.
Organ function meeting any one or more of the following criteria:
- Absolute neutrophil count (ANC) <1.5×10⁹/L, platelet count (PLT) <100×10⁹/L, hemoglobin (Hb) <90 g/L;
- Aspartate aminotransferase (AST) >2.5× upper limit of normal (ULN) and/or alanine aminotransferase (ALT) >2.5×ULN, serum total bilirubin (TBIL) >1.5×ULN;
- Creatinine (Cr) >1.5×ULN;
- For patients not receiving anticoagulant or antithrombotic therapy: international normalized ratio (INR) >1.7 or activated partial thromboplastin time (APTT) >1.25×ULN; for patients receiving anticoagulant or antithrombotic therapy: INR >3.0 or APTT >1.5×ULN.
- Diagnosis of immunodeficiency disease, or long-term use of immunosuppressants or systemic corticosteroids at high doses within a short period before screening.
- Epilepsy, Alzheimer's disease, Parkinson's disease, severe depression, or other neurological or psychiatric disorders that, in the investigator's opinion, could affect the participant's ability to participate in the trial or interfere with study assessments.
- Presence of autoimmune diseases (e.g., rheumatoid arthritis, systemic lupus erythematosus, etc.).
- Inability to undergo cranial CT/MRI examination for any reason (e.g., metallic implants such as cardiac pacemakers, claustrophobia, etc.).
- Participation in another clinical trial of an investigational drug within 3 months before screening.
- Pregnancy, breastfeeding, planned pregnancy, or inability to use effective contraceptive measures.
- Any other condition that, in the investigator's judgment, makes the participant unsuitable for inclusion in this study.
Plan de estudios
¿Cómo está diseñado el estudio?
Detalles de diseño
- Propósito principal: Tratamiento
- Asignación: Aleatorizado
- Modelo Intervencionista: Asignación paralela
- Enmascaramiento: Cuadruplicar
Armas e Intervenciones
Grupo de participantes/brazo |
Intervención / Tratamiento |
|---|---|
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Experimental: Human Umbilical Cord Mesenchymal Stromal Cells Injection(low-dose group)
5.0×10^7 cells,Single intravenous infusion
|
the first phase (Phase Ia) is a single-dose administration
the second phase (Phase Ib) is a multiple-dose administration.
|
|
Experimental: Human Umbilical Cord Mesenchymal Stromal Cells Injection(medium-dose group)
1.0×10^8 cells,Single intravenous infusion
|
the first phase (Phase Ia) is a single-dose administration
the second phase (Phase Ib) is a multiple-dose administration.
|
|
Experimental: Human Umbilical Cord Mesenchymal Stromal Cells Injection(high-dose group)
2.0×10^8 cells,Single intravenous infusion
|
the first phase (Phase Ia) is a single-dose administration
the second phase (Phase Ib) is a multiple-dose administration.
|
|
Comparador de placebos: Placebo of Human Umbilical Cord Mesenchymal Stromal Cells Injection(medium-dose group)
1.0×10^8 cells,Single intravenous infusion
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Placebo refers to a cell-free product, whose packaging, storage conditions, expiration date, and method of administration remain consistent with those of the investigational drug.
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Comparador de placebos: Placebo of Human Umbilical Cord Mesenchymal Stromal Cells Injection(high-dose group)
2.0×10^8 cells,Single intravenous infusion
|
Placebo refers to a cell-free product, whose packaging, storage conditions, expiration date, and method of administration remain consistent with those of the investigational drug.
|
|
Experimental: Human Umbilical Cord Mesenchymal Stromal Cells Injection 1
Based on the results from the Phase Ia trial, dose group 1 will be considered for the Phase Ib trial.For multiple dosing, it is initially planned to administer the injection once on Day 0, Day 7, and Day 14, for a total of 3 doses.
|
the first phase (Phase Ia) is a single-dose administration
the second phase (Phase Ib) is a multiple-dose administration.
|
|
Experimental: Human Umbilical Cord Mesenchymal Stromal Cells Injection 2
Based on the results from the Phase Ia trial, dose group 2 will be considered for the Phase Ib trial.For multiple dosing, it is initially planned to administer the injection once on Day 0, Day 7, and Day 14, for a total of 3 doses.
|
the first phase (Phase Ia) is a single-dose administration
the second phase (Phase Ib) is a multiple-dose administration.
|
|
Comparador de placebos: Placebo of Human Umbilical Cord Mesenchymal Stromal Cells Injection 1
Based on the results from the Phase Ia trial, dose group 1 will be considered for the Phase Ib trial.For multiple dosing, it is initially planned to administer the injection once on Day 0, Day 7, and Day 14, for a total of 3 doses.
|
Placebo refers to a cell-free product, whose packaging, storage conditions, expiration date, and method of administration remain consistent with those of the investigational drug.
|
|
Comparador de placebos: Placebo of Human Umbilical Cord Mesenchymal Stromal Cells Injection 2
Based on the results from the Phase Ia trial, dose group 2 will be considered for the Phase Ib trial.For multiple dosing, it is initially planned to administer the injection once on Day 0, Day 7, and Day 14, for a total of 3 doses.
|
Placebo refers to a cell-free product, whose packaging, storage conditions, expiration date, and method of administration remain consistent with those of the investigational drug.
|
¿Qué mide el estudio?
Medidas de resultado primarias
Medida de resultado |
Periodo de tiempo |
|---|---|
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Incidence of DLT (Dose-Limiting Toxicity) events;
Periodo de tiempo: Day28
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Day28
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All adverse events/serious adverse events during the trial;
Periodo de tiempo: 2year
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2year
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All-cause mortality
Periodo de tiempo: Day90、Day180、Day360
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Day90、Day180、Day360
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Medidas de resultado secundarias
Medida de resultado |
Medida Descripción |
Periodo de tiempo |
|---|---|---|
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Proportion of participants with an Modified Rankin Scale (mRS) score of 0-2
Periodo de tiempo: Day 30, Day90, Day180, Day360
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The modified Rankin Scale (mRS) is a widely used clinical outcome measure that assesses the degree of disability or dependence in the daily activities of patients who have suffered a stroke or other neurological conditions. It is a simple, 7-level ordinal scale ranging from 0 to 6: 0 - No symptoms at all.
A higher score indicates more severe disability. The mRS is the most common primary endpoint in acute stroke clinical trials, with a score of 0-2 at 90 days often defined as a "good outcome. |
Day 30, Day90, Day180, Day360
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Proportion of participants with a ≥4-point improvement in National Institutes of Health Stroke Scale (NIHSS) score from baseline
Periodo de tiempo: Day 7, Day 14, Day 30, Day 90, Day 180, Day 360
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The National Institutes of Health Stroke Scale (NIHSS) is a standardized tool used to objectively quantify the severity of neurological deficits in patients with stroke.
It consists of 15 items, including assessments of consciousness, eye movements, visual fields, facial palsy, motor and sensory function, language, speech, and neglect.
Each item is scored, with a total score ranging from 0 to 42.
Higher scores indicate more severe neurological impairment.
The NIHSS is widely used in clinical practice and research to evaluate stroke severity, guide treatment decisions, and predict patient outcomes.
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Day 7, Day 14, Day 30, Day 90, Day 180, Day 360
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Change from baseline in National Institutes of Health Stroke Scale(NIHSS) score
Periodo de tiempo: Day 7, Day 14, Day 30, Day 90, Day 180, Day 360
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Day 7, Day 14, Day 30, Day 90, Day 180, Day 360
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Proportion of participants with a Barthel Index ≥95
Periodo de tiempo: Day 30, Day 90, Day180, Day360
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The Barthel Index (BI) is a standardized ordinal scale used to measure a person's performance in activities of daily living (ADL).
It assesses 10 basic functions, including feeding, bathing, grooming, dressing, bowel and bladder control, toilet use, transfers (e.g., bed to chair), mobility, and stair climbing.
Each item is scored based on the amount of physical assistance required, with total scores typically ranging from 0 to 100 (or 0-20 in some versions).
It is widely used in geriatrics, rehabilitation, and stroke research to evaluate functional independence and track changes over time.A higher Barthel Index score indicates greater functional independence (less need for assistance), while a lower score reflects greater disability and dependency.
For example, a score of 100 means the patient is fully independent in basic ADL.
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Day 30, Day 90, Day180, Day360
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Change from baseline in the Fugl-Meyer Motor Function Assessment Scale score
Periodo de tiempo: Day 30, Day90, Day180, Day 360
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The Fugl-Meyer Assessment (FMA) is a stroke-specific, performance-based impairment index widely recognized as a gold standard scale for evaluating sensorimotor recovery in patients with post-stroke hemiplegia.
A higher FMA score indicates better motor function and less impairment, reflecting more positive outcomes in stroke recovery.
For example, the motor domain score ranges from 0 (complete hemiplegia) to 100 (normal motor performance).
The total FMA score is therefore a direct measure of functional recovery: the higher the score, the greater the improvement in sensorimotor function following stroke.
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Day 30, Day90, Day180, Day 360
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Change from baseline in objective imaging findings (CT/MRI)
Periodo de tiempo: Day 90
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Day 90
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Otras medidas de resultado
Medida de resultado |
Periodo de tiempo |
|---|---|
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mmunogenicity: Human Leukocyte Antigen (HLA) antibodies.
Periodo de tiempo: Within 60 minutes before the first dose, and at 14 days, 30 days, and 90 days after the start of the first dose administration.
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Within 60 minutes before the first dose, and at 14 days, 30 days, and 90 days after the start of the first dose administration.
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Colaboradores e Investigadores
Patrocinador
Fechas de registro del estudio
Fechas importantes del estudio
Inicio del estudio (Estimado)
Finalización primaria (Estimado)
Finalización del estudio (Estimado)
Fechas de registro del estudio
Enviado por primera vez
Primero enviado que cumplió con los criterios de control de calidad
Publicado por primera vez (Actual)
Actualizaciones de registros de estudio
Última actualización publicada (Actual)
Última actualización enviada que cumplió con los criterios de control de calidad
Última verificación
Más información
Términos relacionados con este estudio
Términos MeSH relevantes adicionales
Otros números de identificación del estudio
- YW2026-016-02
Plan de datos de participantes individuales (IPD)
¿Planea compartir datos de participantes individuales (IPD)?
Información sobre medicamentos y dispositivos, documentos del estudio
Estudia un producto farmacéutico regulado por la FDA de EE. UU.
Estudia un producto de dispositivo regulado por la FDA de EE. UU.
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