- ICH GCP
- Registro degli studi clinici negli Stati Uniti
- Sperimentazione clinica NCT01808508
Obstructive Sleep Apnea and Neurocognitive and Cardiovascular Function in Children With Down Syndrome (TRIO)
Many individuals with Down syndrome (DS) have breathing problems during sleep. This is called obstructive sleep apnea syndrome (OSAS). OSAS is very common in individuals with Down syndrome because of the shape of their face and tongue and because of their low muscle tone. OSAS can cause a lot of health problems including behavioral and learning problems as well as heart problems.
The purpose of this research study is to look at the effects of treating OSAS in individuals with Down syndrome with a machine called Continuous Positive Airway Pressure (CPAP). The investigators want to see if treatment of OSAS improves learning, behavior and heart problems.
Panoramica dello studio
Stato
Descrizione dettagliata
All individuals participating in the study will be evaluated for obstructive sleep apnea syndrome (OSAS) with a baseline sleep study. Based on the results of the sleep study,individuals with OSAS will be randomly assigned into two groups. One group will receive continuous positive airway pressure (CPAP) and the other intervention group will receive sham CPAP(placebo) for four months. CPAP is a machine with a mask that fits over the nose, is worn during sleep and helps keep the airway open. Sham CPAP (placebo) is a machine that looks and sounds like a CPAP machine but does not give pressure so it does not treat OSAS. Individuals with normal breathing during the sleep study will not receive a machine, and will serve as controls.
Individuals will also have baseline tests including blood tests, an echocardiogram (pictures of the heart), a walking test and learning tests. After 4 months, the baseline tests will be repeated in all participants. At the end of the study, all individuals with OSAS will get treatment.
Tipo di studio
Iscrizione (Effettivo)
Fase
- Non applicabile
Contatti e Sedi
Luoghi di studio
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Pennsylvania
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Philadelphia, Pennsylvania, Stati Uniti, 19104
- The Children's Hospital of Philadelphia
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Criteri di partecipazione
Criteri di ammissibilità
Età idonea allo studio
Accetta volontari sani
Sessi ammissibili allo studio
Descrizione
Inclusion Criteria:
- Aged 8-20 years
- Down syndrome (based on the characteristic phenotype)
- Families provide informed consent and child provides assent
Exclusion Criteria:
- Subjects and families who do not speak English well enough to undergo psychometric testing.
- Subjects living in institutions where there is no primary caregiver to participate in the neurocognitive/behavioral battery.
- Major chronic lung disease such as chronic aspiration.
- Previous or current CPAP therapy.
- Participation in a weight loss program.
- Craniofacial or neuromuscular conditions other than those associated with DS.
- Untreated hypothyroidism. Participants with normal thyroid function tests will be included in the study.
Piano di studio
Come è strutturato lo studio?
Dettagli di progettazione
- Scopo principale: Trattamento
- Assegnazione: Randomizzato
- Modello interventistico: Assegnazione parallela
- Mascheramento: Quadruplicare
Armi e interventi
Gruppo di partecipanti / Arm |
Intervento / Trattamento |
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Comparatore attivo: Group 1- Continuous positive airway pressure (CPAP)
Group 1 will receive therapeutic CPAP for 4 months.
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Continuous positive airway pressure is a machine used with sleep which compresses air delivered via a nasal mask and thus helps stent the airway open.
Altri nomi:
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Comparatore placebo: Group 2-Sham Continuous positive airway pressure (CPAP)
Group 2 are individuals with OSAS who will receive sham or placebo continuous positive airway pressure (CPAP) for 4 months.
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Sham or placebo CPAP is a machine used instead of therapeutic CPAP.
This machine is similar to a therapeutic CPAP machine but has built in leaks and does not deliver pressure.
It is not effective in treating OSAS.
Altri nomi:
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Nessun intervento: Group 3- No Intervention
Group 3 are individuals with normal breathing during sleep who will not receive any intervention and will be used as a control group.
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Cosa sta misurando lo studio?
Misure di risultato primarie
Misura del risultato |
Misura Descrizione |
Lasso di tempo |
|---|---|---|
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Change in Epworth Sleepiness Scale From Baseline to End of Study
Lasso di tempo: 4 Months
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The primary aim of the study is to assess the relationship between obstructive sleep apnea syndrome (OSAS) and the neurocognitive and behavioral outcomes of individuals with Down syndrome.
Sleepiness was assessed using the pediatric version of the Epworth Sleepiness Scale (ESS).
The ESS is a self-administered questionnaire with 8 questions.
It provides a measure of a person's general level of daytime sleepiness, or average sleep propensity in daily life.
The ESS asks people to rate, on a 4-point scale (0, low to 3, high) their usual chances of dozing off or falling asleep in 8 different situations or activities that most people engage in as part of their daily lives.
The total ESS score provides an estimate of a general characteristic of each person's average level of sleepiness in daily life (0= no chance of dozing/no daytime sleepiness to 24=high chance of dozing/lots of daytime sleepiness).
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4 Months
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Misure di risultato secondarie
Misura del risultato |
Misura Descrizione |
Lasso di tempo |
|---|---|---|
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Change in Child Behavior Checklist (CBCL) Total Score From Baseline to 4 Months
Lasso di tempo: 4 Months
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The change in behavioral domain was measured by the Child Check Behavior List.
The CBCL is a widely used method of identifying problem behavior in children.
Problems are identified by a respondent who knows the child well, usually a parent or other care giver.
There are 2 versions based on the child's age (CBCL/1½-5 for use children 18 months-5 years; the CBCL/6-18 for children aged 6-18 years).
The checklists consists of a number of statements about the child's behavior and responses are recorded on a scale: 0 = Not True, 1 = Somewhat or Sometimes True, 2 = Very True or Often True.
The preschool checklist contains 100 questions and, school-age checklist contains 120 questions.
8 sub-scores (1 for each of 8 syndromes: anxious/depressed, withdrawn depressed, somatic complaints, social problems, thought problems, attention problems, rule-breaking behavior and aggressive behavior) are calculated, each ranging from 0 (normal) to 16 (clinical behavior).
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4 Months
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Change in the Left Ventricular (LV) Mass Index Score From Baseline to 4 Months
Lasso di tempo: 4 Months
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The change in left ventricular mass index score, measured on echocardiography, was used to assess the relationship between obstructive sleep apnea syndrome and cardiovascular function of individuals with Down syndrome.
Left ventricular (LV) mass was calculated from M-mode measurements of the LV end-diastolic dimension, the thickness of the interventricular septum and the thickness of the LV posterior wall, and presented as a z-score.
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4 Months
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Change in the Distance Walked on a 6 Minute Walk Test From Baseline to 4 Months
Lasso di tempo: 4 Months
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As secondary outcome of the second aim, we will use the distance walked during the 6 minute walk test.
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4 Months
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Collaboratori e investigatori
Investigatori
- Investigatore principale: Carole Marcus, MD, Children's Hospital of Philadelphia
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Inizio studio
Completamento primario (Effettivo)
Completamento dello studio (Effettivo)
Date di iscrizione allo studio
Primo inviato
Primo inviato che soddisfa i criteri di controllo qualità
Primo Inserito (Stima)
Aggiornamenti dei record di studio
Ultimo aggiornamento pubblicato (Stima)
Ultimo aggiornamento inviato che soddisfa i criteri QC
Ultimo verificato
Maggiori informazioni
Termini relativi a questo studio
Parole chiave
Termini MeSH pertinenti aggiuntivi
- Processi patologici
- Malattie del sistema nervoso
- Malattie delle vie respiratorie
- Disturbi respiratori
- Disturbi del sonno, intrinseci
- Dissonnie
- Disturbi del sonno e della veglia
- Manifestazioni neurologiche
- Manifestazioni neurocomportamentali
- Patologia
- Anomalie congenite
- Malattie genetiche, congenite
- Segni e sintomi, respiratori
- Disabilità intellettuale
- Anomalie multiple
- Disturbi cromosomici
- Sindromi da apnee notturne
- Apnea notturna, ostruttiva
- Sindrome
- Apnea
- Sindrome di Down
Altri numeri di identificazione dello studio
- 11-007964
Queste informazioni sono state recuperate direttamente dal sito web clinicaltrials.gov senza alcuna modifica. In caso di richieste di modifica, rimozione o aggiornamento dei dettagli dello studio, contattare register@clinicaltrials.gov. Non appena verrà implementata una modifica su clinicaltrials.gov, questa verrà aggiornata automaticamente anche sul nostro sito web .