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Clinical Trial Evaluating the Impact of an Intensive Rehabilitation Program Combined With Tendon Vibratory Stimulation on Functional Balance in Individuals With Charcot-Marie-Tooth Disease Type 1A (EQUIVIB-CMT)

30 luglio 2026 aggiornato da: UGECAM PACA et Corse

Charcot-Marie-Tooth (CMT) disease is caused by a genetic abnormality involving the PMP22 gene, resulting in demyelination of the peripheral nerves. Demyelination leads to sensorimotor impairment and causes progressive muscle weakness and tendon contractures, initially affecting the lower limbs. Consequently, individuals with CMT experience balance impairments and gait disturbances, including ankle instability, foot drop, and postural instability, which lead to frequent falls and reduced quality of life. Currently, there is no disease-modifying treatment for CMT.

Several rehabilitation approaches have been proposed, including endurance training and muscle strengthening programs, to improve independence in activities of daily living. However, rehabilitation practices for individuals with CMT remain poorly standardized, and there is still a lack of clearly defined rehabilitation protocols, despite broad agreement among healthcare professionals regarding their potential benefits.

More recently, noninvasive focal tendon vibration has been investigated in several neurological disorders to improve sensory function, balance, and motor performance. Previous studies suggest that mechanical vibratory stimulation applied to the quadriceps tendon may induce sustained improvements in postural control and lower-limb muscle strength.

The present study aims to evaluate a rehabilitation program combined with tendon vibratory stimulation. The objective is to compare the effectiveness of a short-term (2-week), intensive multidisciplinary rehabilitation program focused on balance with different types of focal tendon vibration, in order to better address balance impairments and their associated complications in individuals with Charcot-Marie-Tooth disease.

Panoramica dello studio

Descrizione dettagliata

Charcot-Marie-Tooth (CMT) disease is the most common inherited peripheral neuropathy, with a prevalence ranging from 3.1 to 82.3 per 100,000 individuals. It is caused by genetic abnormalities affecting peripheral nerves. The most common form, accounting for approximately 60% of CMT cases, is Charcot-Marie-Tooth disease type 1A (CMT1A). CMT1A is characterized by a demyelinating neuropathy, autosomal dominant inheritance, and a mutation involving the PMP22 gene.

The first clinical signs of the disease typically appear before the age of 20 years and consist of a length-dependent sensorimotor impairment with distal predominance and diffuse areflexia. The disease primarily affects the lower limbs; upper limb involvement is variable and may develop after several years of disease progression. These impairments result in progressive distal muscle weakness associated with muscle atrophy, tendon contractures leading to pes cavus and claw toe deformities, and mild-to-moderate distal sensory impairment. These manifestations lead to major functional complaints among individuals with CMT, including balance disorders, gait disturbances related to ankle instability, foot clearance difficulties during the swing phase, and postural instability, resulting in frequent falls and impaired quality of life.

Currently, there is no disease-modifying treatment for CMT.

Assistive devices and lower-limb orthotic management may be prescribed. Surgical treatment may be considered in cases of severe and disabling musculoskeletal deformities.

Several rehabilitation approaches have been proposed, including endurance training and strengthening programs to improve independence in activities of daily living, as well as aerobic training programs aimed at improving functional capacity, aerobic capacity, muscle strength, and fatigue in individuals with CMT. The French National Diagnostic and Care Protocol (PNDS) for hereditary motor and sensory neuropathies associated with CMT highlights the lack of standardized rehabilitation practices and clearly defined protocols, despite a consensus among healthcare professionals regarding their potential benefits. Indeed, the literature includes only one randomized controlled trial, published in 2006, with a small sample size (n = 16), demonstrating improvements in balance, assessed using the Berg Balance Scale (BBS), following a two-week dynamic training program combining passive stretching, muscle strengthening, and standing balance exercises.

In addition, non-invasive focal tendon vibration has been proposed in several neurological disorders to improve sensory function, balance, and motor performance, particularly in individuals with diabetic peripheral neuropathy. Some studies suggest that mechanical vibratory stimulation applied to the quadriceps tendon may induce sustained improvements in postural control and lower-limb strength in women over 60 years of age.

In individuals with CMT, a pilot study involving 14 participants with CMT1A demonstrated improved balance performance on the Berg Balance Scale following three consecutive days of musculoskeletal vibration therapy applied to the quadriceps and triceps surae muscles.

In this context, we selected the Vibramoov device, a neurorehabilitation device that has already demonstrated clinical benefits in comparable studies involving other neurological disorders. Vibramoov delivers vibrations applied at the musculotendinous junction, thereby mechanically stimulating muscle spindles and reproducing the sensory signals associated with natural movement. This approach, already validated in other clinical settings, represents a promising strategy to improve balance and gait in individuals with CMT by integrating it into an intensive multidisciplinary rehabilitation program.

Therefore, it appears relevant to investigate a specific intensive multidisciplinary rehabilitation program combined with mechanical vibratory stimulation to improve functional balance and gait abilities in individuals with CMT.

Tipo di studio

Interventistico

Iscrizione (Stimato)

30

Fase

  • Non applicabile

Contatti e Sedi

Questa sezione fornisce i recapiti di coloro che conducono lo studio e informazioni su dove viene condotto lo studio.

Contatto studio

Backup dei contatti dello studio

  • Nome: Clotilde Pheulpin, MD

Luoghi di studio

Criteri di partecipazione

I ricercatori cercano persone che corrispondano a una certa descrizione, chiamata criteri di ammissibilità. Alcuni esempi di questi criteri sono le condizioni generali di salute di una persona o trattamenti precedenti.

Criteri di ammissibilità

Età idonea allo studio

  • Adulto
  • Adulto più anziano

Accetta volontari sani

No

Descrizione

Inclusion Criteria:

  • Individuals with genetically confirmed Charcot-Marie-Tooth disease type 1A (CMT1A), characterized by PMP22 gene duplication on chromosome 17 (17p11.2).
  • Age between 18 and 65 years.
  • Overall Neuropathy Limitations Scale (ONLS) score between 2 and 3/7 for the lower limbs.
  • Affiliation with a social security/health insurance system.
  • Written informed consent voluntarily provided after receiving information regarding the study objectives, procedures, and potential risks.

Exclusion Criteria:

  • Comorbidities causing peripheral neuropathy (e.g., diabetes, renal failure, medication-induced neuropathy).
  • Balance or gait disorders due to another cause.
  • Individuals without a permanent residence.
  • Individuals deprived of liberty by judicial or administrative decision or under legal guardianship.
  • Individuals unable to understand the study objectives and procedures or unable to provide informed consent.
  • Individuals unable to complete all study procedures.
  • Previous use of the Vibramoov device.
  • Pregnant women or women planning to become pregnant during the study period.
  • Concurrent participation in another research study.

Piano di studio

Questa sezione fornisce i dettagli del piano di studio, compreso il modo in cui lo studio è progettato e ciò che lo studio sta misurando.

Come è strutturato lo studio?

Dettagli di progettazione

  • Scopo principale: Terapia di supporto
  • Assegnazione: Randomizzato
  • Modello interventistico: Assegnazione parallela
  • Mascheramento: Quadruplicare

Armi e interventi

Gruppo di partecipanti / Arm
Intervento / Trattamento
Sperimentale: With mechanical vibratory stimulation
2-week intensive multidisciplinary rehabilitation program including physical therapy, occupational therapy, and adapted physical activity sessions, followed by balance assessments and evaluation of neuropathy status.
Comparatore fittizio: Without mechanical vibratory stimulation
2-week intensive multidisciplinary rehabilitation program including physical therapy, occupational therapy, and adapted physical activity sessions, followed by balance assessments and evaluation of neuropathy status.

Cosa sta misurando lo studio?

Misure di risultato primarie

Misura del risultato
Misura Descrizione
Lasso di tempo
Berg Balance Scale
Lasso di tempo: Baseline, Week 3 , Week 7, Week 15
The primary outcome measure of this study will be the assessment of balance using the Berg Balance Scale (BBS). The BBS is a 14-item scale in which each item is scored from 0 to 4 points and evaluates static and dynamic balance as well as fall risk. This scale has been validated in individuals with neurological disorders and has been used to assess balance impairments in individuals with Charcot-Marie-Tooth disease. The BBS has demonstrated good reliability and responsiveness to change. A change of 4 to 7 points, depending on the baseline score, has been identified as a clinically meaningful indicator of improvement in balance.
Baseline, Week 3 , Week 7, Week 15

Misure di risultato secondarie

Misura del risultato
Misura Descrizione
Lasso di tempo
CMT Neuropathy Score
Lasso di tempo: Baseline, Week 3 , Week 7, Week 15
This validated score provides a reliable measure of overall neuropathy severity.
Baseline, Week 3 , Week 7, Week 15
Posturography
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
Assessment of balance and proprioception by recording center of pressure sway on a force platform.
Baseline, Week 3, Week 7, Week 15
Timed Up and Go (TUG) test
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
This test is used to identify individuals at risk of falls and to assess functional mobility. Participants are timed while standing up from a chair without armrests, walking 3 meters, turning around, walking back to the chair, and sitting down.
Baseline, Week 3, Week 7, Week 15
Knee joint position sense assessment using electronic goniometers
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
Participants will be seated with their knees flexed at 90°. The examiner will passively move the knee to a target angle. After returning to the starting position, participants, with their eyes closed, will be asked to actively reproduce the target knee position.
Baseline, Week 3, Week 7, Week 15
Gait assessment
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
6-Minute Walk Test (6MWT): Assessment of walking endurance. Walking distance (meters) and number of rest stops will be recorded.
Baseline, Week 3, Week 7, Week 15
Walking speed
Lasso di tempo: Baseline, Week3, Week 7, Week 15
10-Meter Walk Test (10MWT): Assessment of self-selected walking speed by measuring the time (seconds) required to walk 10 meters.
Baseline, Week3, Week 7, Week 15
Borg Rate of Perceived Extorsion (RPE) scale
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
Measure of perceived exertion (Borg Rate of Perceived Extorsion (RPE) scale from 1 - "at rest" to 10 - "maximal") during during walk speed assessment.
Baseline, Week 3, Week 7, Week 15
Muscle strength assessment
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
Muscle strength will be assessed using the Medical Research Council (MRC) scale (0 - "no movement" to 5 - "normal force") for the tibialis anterior, extensor hallucis longus, extensor digitorum longus, triceps surae, peroneal, quadriceps, and hamstring muscles.
Baseline, Week 3, Week 7, Week 15
Patient-Reported Outcome: R-ODS questionnaire
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
The Rasch-built Overall Disability Scale (R-ODS) with 24 items is a questionnaire that reflects how neuropathy affects the patient's daily and social activities. Scale 0 - "impossible" to 48 - "without difficulties".
Baseline, Week 3, Week 7, Week 15
Patient-Reported Outcome: FSS Scale
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
The Fatigue Severity Scale (FSS) is a short questionnaire with 9 items that requires the patient to rate their level of fatigue for each item from 0 - "strongly diasagree" to 7 - "strongly agree".
Baseline, Week 3, Week 7, Week 15
Patient-Reported Outcome: QoL NMD v1.0
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
The Quality of Life in Neuromuscular Disease (QoL NMD v1.0) is a questionnaire with 26 items that assesses the quality of life in patients with neuromuscular disease. The final score is between 0 -"Poor" and 75 - "Excellent".
Baseline, Week 3, Week 7, Week 15
Patient-reported Outcome: NRS Scale
Lasso di tempo: Baseline, Week 3, Week 7, Week 15
The Numeric Rating Scale (NRS) assesses pain intensity using a 0 - 10 ranking scale with 0 representing "no pain" and 10 "unbearable pain"
Baseline, Week 3, Week 7, Week 15

Collaboratori e investigatori

Qui è dove troverai le persone e le organizzazioni coinvolte in questo studio.

Studiare le date dei record

Queste date tengono traccia dell'avanzamento della registrazione dello studio e dell'invio dei risultati di sintesi a ClinicalTrials.gov. I record degli studi e i risultati riportati vengono esaminati dalla National Library of Medicine (NLM) per assicurarsi che soddisfino specifici standard di controllo della qualità prima di essere pubblicati sul sito Web pubblico.

Studia le date principali

Inizio studio (Effettivo)

28 aprile 2025

Completamento primario (Stimato)

31 dicembre 2027

Completamento dello studio (Stimato)

31 dicembre 2027

Date di iscrizione allo studio

Primo inviato

21 luglio 2026

Primo inviato che soddisfa i criteri di controllo qualità

21 luglio 2026

Primo Inserito (Effettivo)

24 luglio 2026

Aggiornamenti dei record di studio

Ultimo aggiornamento pubblicato (Effettivo)

3 agosto 2026

Ultimo aggiornamento inviato che soddisfa i criteri QC

30 luglio 2026

Ultimo verificato

1 luglio 2026

Maggiori informazioni

Termini relativi a questo studio

Piano per i dati dei singoli partecipanti (IPD)

Hai intenzione di condividere i dati dei singoli partecipanti (IPD)?

INDECISO

Informazioni su farmaci e dispositivi, documenti di studio

Studia un prodotto farmaceutico regolamentato dalla FDA degli Stati Uniti

No

Studia un dispositivo regolamentato dalla FDA degli Stati Uniti

No

Queste informazioni sono state recuperate direttamente dal sito web clinicaltrials.gov senza alcuna modifica. In caso di richieste di modifica, rimozione o aggiornamento dei dettagli dello studio, contattare register@clinicaltrials.gov. Non appena verrà implementata una modifica su clinicaltrials.gov, questa verrà aggiornata automaticamente anche sul nostro sito web .

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