- ICH GCP
- US Clinical Trials Registry
- Klinisk forsøg NCT01299298
A Study to Evaluate the Pharmacokinetics, Safety, and Tolerability of Single Doses of Mipomersen in Japanese Healthy Volunteers
1. august 2016 opdateret af: Kastle Therapeutics, LLC
A Prospective, Randomized, Double-Blind, Placebo-Controlled, Dose-Escalation, Phase 1 Study to Evaluate the Pharmacokinetics, Safety, and Tolerability of Single Doses of Mipomersen Administered Subcutaneously to Japanese Healthy Subjects
This Phase 1 study is being conducted to evaluate 3 increasing subcutaneous (SC) doses (50, mg, 100 mg or 200mg) of mipomersen in Japanese healthy volunteers.
Eligible subjects will receive a single study injection of either mipomersen or placebo.
Subjects will be enrolled into 1 of 3 treatment cohorts (Cohorts A, B, and C) in a dose-escalation design.
Dose-escalation will proceed only if there is an acceptable safety profile from the previous dosing level.
Studieoversigt
Status
Afsluttet
Betingelser
Intervention / Behandling
Undersøgelsestype
Interventionel
Tilmelding (Faktiske)
20
Fase
- Fase 1
Kontakter og lokationer
Dette afsnit indeholder kontaktoplysninger for dem, der udfører undersøgelsen, og oplysninger om, hvor denne undersøgelse udføres.
Studiesteder
-
-
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Stresemannallee 6, Neuss, Tyskland, 41460
- FOCUS Clinical Drug Development GmbH
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Deltagelseskriterier
Forskere leder efter personer, der passer til en bestemt beskrivelse, kaldet berettigelseskriterier. Nogle eksempler på disse kriterier er en persons generelle helbredstilstand eller tidligere behandlinger.
Berettigelseskriterier
Aldre berettiget til at studere
20 år til 45 år (Voksen)
Tager imod sunde frivillige
Ja
Køn, der er berettiget til at studere
Han
Beskrivelse
Inclusion Criteria:
- First generation Japanese (born in Japan of Japanese parents and Japanese grandparents), lived no more than 5 years outside of Japan, with no significant change in lifestyle or habits, including diet, while living outside of Japan.
- Surgically sterile, abstinent or subject or partner compliant with acceptable contraceptive during and 24 weeks after the last study drug dose
- Body weight >50 kg and body mass index between 18 and 30 kg/m2 inclusive
Exclusion Criteria:
- Clinically significant cardiovascular, pulmonary, hepatic, renal, haematologic, gastrointestinal, endocrine, immunologic, dermatologic, neurologic, infectious, or psychiatric disease
- Clinically significant abnormal findings on the physical examination, ECG, blood pressure, heart rate, medical history, or clinical laboratory results at Screening or before dosing
- Positive test for human immunodeficiency virus (HIV), hepatitis B or C.
- High sensitivity C-reactive protein (hsCRP) >5 mg/L
- History of or current malignancy (with the exception of basal or squamous cell carcinoma of the skin if adequately treated and no recurrence for > 1 year)
- Evidence of acute or ongoing chronic inflammatory condition or infection
- History of rash, impetigo, or drug allergies
- Alcohol and/or drug abuse
- Smoking more than 10 cigarettes per day
- Planned dental work up to and including Day 8 procedures
- Treatment with another investigational drug, biological agent, or device within 4 weeks of Screening or 5 half-lives of the study agent, whichever is longer
- Use of prescribed medications within 4 weeks or over-the counter medications (including dietary supplements and herbal remedies) within 14 days before the first study drug dose, or use of any concomitant medications (prescribed or over the counter) through Day 8 of the study without Investigator and Sponsor approval. Vaccinations are not allowed beginning 3 weeks prior to the first dose of study drug until completion of the safety follow-up period
- Previous exposure to oligonucleotide-based drug therapy
- Donated 50 to 499 mL of blood within 30 days prior to consent, or >499 mL within 60 days
Studieplan
Dette afsnit indeholder detaljer om studieplanen, herunder hvordan undersøgelsen er designet, og hvad undersøgelsen måler.
Hvordan er undersøgelsen tilrettelagt?
Design detaljer
- Primært formål: Behandling
- Tildeling: Randomiseret
- Interventionel model: Parallel tildeling
- Maskning: Tredobbelt
Våben og indgreb
Deltagergruppe / Arm |
Intervention / Behandling |
|---|---|
|
Eksperimentel: mipomersen
50 mg (cohort A), 100mg (cohort B) or 200mg (cohort C) SC single dose
|
50 mg (cohort A), 100mg (cohort B) or 200mg (cohort C) subcutaneous (SC) single dose of study drug
Andre navne:
|
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Placebo komparator: placebo
50 mg (cohort A), 100mg (cohort B) or 200mg (cohort C) SC single dose
|
50 mg (cohort A), 100mg (cohort B), or 200mg (cohort C) subcutaneous (SC) single dose of study drug
|
Hvad måler undersøgelsen?
Primære resultatmål
Resultatmål |
Foranstaltningsbeskrivelse |
Tidsramme |
|---|---|---|
|
Maximum plasma concentration (Cmax)
Tidsramme: Baseline up to Day 36 Post-Treatment
|
plasma PK parameters
|
Baseline up to Day 36 Post-Treatment
|
|
Time to maximal concentration (Tmax)
Tidsramme: Baseline up to Day 36 Post-Treatment
|
plasma PK parameters
|
Baseline up to Day 36 Post-Treatment
|
|
Area Under the Curve (AUC)
Tidsramme: Baseline up to Day 36 Post-Treatment
|
plasma PK parameters
|
Baseline up to Day 36 Post-Treatment
|
Sekundære resultatmål
Resultatmål |
Tidsramme |
|---|---|
|
Number of Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)
Tidsramme: Up to Day 36 Post-Treatment
|
Up to Day 36 Post-Treatment
|
Samarbejdspartnere og efterforskere
Det er her, du vil finde personer og organisationer, der er involveret i denne undersøgelse.
Sponsor
Samarbejdspartnere
Datoer for undersøgelser
Disse datoer sporer fremskridtene for indsendelser af undersøgelsesrekord og resumeresultater til ClinicalTrials.gov. Studieregistreringer og rapporterede resultater gennemgås af National Library of Medicine (NLM) for at sikre, at de opfylder specifikke kvalitetskontrolstandarder, før de offentliggøres på den offentlige hjemmeside.
Studer store datoer
Studiestart
1. januar 2011
Primær færdiggørelse (Faktiske)
1. april 2011
Studieafslutning (Faktiske)
1. april 2011
Datoer for studieregistrering
Først indsendt
9. februar 2011
Først indsendt, der opfyldte QC-kriterier
17. februar 2011
Først opslået (Skøn)
18. februar 2011
Opdateringer af undersøgelsesjournaler
Sidste opdatering sendt (Skøn)
3. august 2016
Sidste opdatering indsendt, der opfyldte kvalitetskontrolkriterier
1. august 2016
Sidst verificeret
1. august 2016
Mere information
Begreber relateret til denne undersøgelse
Yderligere relevante MeSH-vilkår
Andre undersøgelses-id-numre
- MIPO3700710
- 2010-021948-18 (EudraCT nummer)
Disse oplysninger blev hentet direkte fra webstedet clinicaltrials.gov uden ændringer. Hvis du har nogen anmodninger om at ændre, fjerne eller opdatere dine undersøgelsesoplysninger, bedes du kontakte register@clinicaltrials.gov. Så snart en ændring er implementeret på clinicaltrials.gov, vil denne også blive opdateret automatisk på vores hjemmeside .