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Clinical Trials on AP4-related Hereditary Spastic Paraplegia in Netherlands
Total 21 results
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Radboud University Medical CenterJacques and Gloria Gossweiler FoundationCompletedHereditary Spastic Paraplegia | Strumpell DiseaseNetherlands
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Institut National de la Santé Et de la Recherche...National Research Agency, France; Institut des Maladies RaresUnknownCerebellar Ataxias | Spastic ParaplegiasNetherlands, France, Serbia, Belgium, Algeria, Denmark, Israel, Italy, Lebanon, Morocco, Norway, Portugal, Saudi Arabia, Tunisia, United Kingdom
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SwanBio Therapeutics, Inc.Active, not recruitingAMN | AMN Gene Mutation | X-ALDUnited States, Netherlands, Germany
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Swedish Orphan BiovitrumPediatric Rheumatology International Trials OrganizationCompletedCryopyrin-Associated Periodic SyndromesUnited Kingdom, Netherlands
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Erasmus Medical CenterUtrecht UniversityUnknownTuberous Sclerosis Complex | TSC Related Cognitive Disability | TSC Related Autism | TSC Related Learning ProblemsNetherlands
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Amsterdam University Medical CenterEnrolling by invitationRetinoblastoma | Neurocognitive Dysfunction | Health-Related BehaviorNetherlands
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J.M. de LaatRadboud University Medical Center; University Medical Center Groningen; Maastricht... and other collaboratorsRecruitingPrecision Radiotherapy Using MR-linac for Pancreatic Neuroendocrine Tumours in MEN1 Patients (PRIME)Multiple Endocrine Neoplasia Type 1 | Neuroendocrine Tumor of PancreasNetherlands
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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UMC UtrechtAlfasigma S.p.A.; ReumaNederland; Autoimmune Research and Collaboration HubNot yet recruitingIgG4-related Disease | Idiopathic Inflammatory Myopathies | Behcet's DiseaseNetherlands
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Radboud University Medical CenterPrincess Beatrix Muscle FoundationCompletedParsonage Turner Syndrome | Neuralgic Amyotrophy | Neuralgic Amyotrophy, Hereditary | Brachial NeuritisNetherlands
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Genzyme, a Sanofi CompanyCompletedThyroid CancerItaly, Spain, Romania, Netherlands, Canada, United States, Switzerland, Australia
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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dr. Laura C. G. de Graaff-HerderRecruitingDisorders of Sex Development | Congenital Adrenal Hyperplasia | Tuberous Sclerosis | Kallmann Syndrome | Prader-Willi Syndrome | Neurofibromatosis | Rett Syndrome | 22q11 Deletion Syndrome | Turner Syndrome | Noonan Syndrome | Allan-Herndon-Dudley Syndrome | Saethre-Chotzen Syndrome | Congenital Hypopituitarism | Cornelia... and other conditionsNetherlands
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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Viridian Therapeutics, Inc.Active, not recruitingThyroid Eye DiseaseUnited States, Spain, United Kingdom, Canada, Germany, Italy, Netherlands, Australia, France, Turkey
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Gyroscope Therapeutics LimitedNovartis PharmaceuticalsActive, not recruitingMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited States, Spain, United Kingdom, France, Germany, Australia, Netherlands, Poland
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy