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Clinical Trials on APRT Deficiency in Italy
Total 396 results
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Pharvaris Netherlands B.V.Active, not recruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Poland, Germany, Austria, Bulgaria, Canada, Ireland, Italy, United Kingdom
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Azienda Ospedaliero-Universitaria di ModenaCompletedErectile Dysfunction | Human Immunodeficiency Virus | Hypogonadism, MaleItaly
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Vifor (International) Inc.Worldwide Clinical Trials; Cytel Inc.CompletedHeart Failure | Iron DeficiencyPoland, Georgia, Lebanon, Croatia, Argentina, Brazil, Israel, Italy, Netherlands, Romania, Singapore, Spain, Sweden, Ukraine, United Kingdom
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University Hospital PadovaCompletedPreterm Birth | Respiratory Distress Syndrome | Surfactant Deficiency Syndrome NeonatalItaly
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Vifor PharmaSyneos Health; ClinStar, LLCCompletedFerinject® Assessment in Patients With Iron Deficiency and Chronic Heart Failure (FAIR-HF) (FAIR-HF)Chronic Heart Failure | Iron Deficiency Anemia | Iron Deficiency | AnaemiaItaly, Spain, Germany, Poland, Romania, Ukraine, Greece, Norway, Argentina, Russian Federation
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Fondazione SISA (Societa Italiana per lo Studio...Recruiting
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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University of PadovaCompletedCoronary Microvascular Disease | Factor XIII Deficiency | ST-Elevation Myocardial Infarction | Myocardial HaemorrhageItaly
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AEterna ZentarisCompletedGrowth Hormone Deficiency With Pituitary AnomaliesUnited Kingdom, United States, France, Poland, Spain, Austria, Germany, Italy, Serbia
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | PregnancySpain, Bahamas, France, Italy
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Barbara Ensoli, MD, PhDCompleted
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IrsiCaixaWithdrawnHIV InfectionSpain, Netherlands, Italy
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Loulou FoundationActive, not recruitingCyclin-Dependent Kinase-Like 5 Deficiency DisorderUnited States, Spain, Italy, France, Canada, Germany, United Arab Emirates
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AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
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Barbara Ensoli, MDCompleted
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Fondazione TelethonOspedale San RaffaeleActive, not recruitingWiskott-Aldrich SyndromeItaly, United States
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Meyer Children's Hospital IRCCSActive, not recruitingCytopeniaItaly, United States, Belgium
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San Raffaele UniversityUnita' di Gastroenterologia - Policlinico Universitario di Bari; Unita' di... and other collaboratorsRecruitingLynch Syndrome | MLH1 Gene Mutation | MSH2 Gene Mutation | MSH6 Gene Mutation | PMS2 Gene Mutation | Lynch Syndrome II | Small Bowel Adenocarcinoma | Lynch Syndrome IItaly
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Barbara Ensoli, MDCompleted
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Barbara Ensoli, MDCompleted
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Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)United States, Spain, France, Germany, Italy, United Kingdom
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked HypophosphatemiaUnited Kingdom, France, Ireland, Italy
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Agios Pharmaceuticals, Inc.CompletedPyruvate Kinase DeficiencyUnited States, Italy, Netherlands
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PfizerTerminatedBrain Injuries | Growth Hormone DeficiencySpain, Sweden, Italy, France, Netherlands, United Kingdom
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Ultragenyx Pharmaceutical IncCompletedGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)United States, Spain, Australia, France, Israel, Italy, United Kingdom
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Pharvaris Netherlands B.V.CompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsBulgaria, United States, Spain, Israel, Germany, Canada, Czechia, France, Hungary, Italy, Netherlands, Poland, United Kingdom
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European Organisation for Research and Treatment...PfizerCompletedLocally Advanced and/or Metastatic Anaplastic Large Cell Lymphoma | Locally Advanced and/or Metastatic Inflammatory Myofibroblastic Tumor | Locally Advanced and/or Metastatic Papillary Renal Cell Carcinoma Type 1 | Locally Advanced and/or Metastatic Alveolar Soft Part Sarcoma | Locally Advanced... and other conditionsFrance, Belgium, Netherlands, Germany, United Kingdom, Italy, Norway, Poland, Slovakia, Slovenia
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked Hypophosphatemia (XLH)Sweden, Spain, United Kingdom, Italy, Austria, France
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OctapharmaCompletedPrimary ImmunodeficiencyUnited Kingdom, Australia, Germany, Italy
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Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
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Novartis PharmaceuticalsCompletedCommon Variable Immunodeficiency (CVID), APDS / PASLIGermany, Russian Federation, Ireland, Italy, United Kingdom, Belarus, Netherlands, Czechia, United States
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AbbVieRecruitingHuman Immuno-deficiency Virus (HIV) DiseaseUnited States, Puerto Rico, Japan, Spain, Germany, Canada, Belgium, France, Poland, South Africa, Italy
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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CSL BehringCompletedCommon Variable Immunodeficiency | AgammaglobulinemiaCanada, Germany, Italy, Spain
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University of L'AquilaUnknownVon Willebrand Disease | Congenital Coagulation Factors Deficiency | Haemophilia CarriersItaly
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), ChildUnited Kingdom, Italy
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ShireCompletedHereditary Angioedema (HAE)Germany, Spain, United Kingdom, France, Italy, Belgium
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Canada, Czechia, Italy, Macedonia, The Former Yugoslav Republic of, Romania, Serbia
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
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Arrowhead PharmaceuticalsCompletedAlpha 1-Antitrypsin DeficiencyUnited States, Spain, Netherlands, Germany, Italy, Portugal
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Pharming Technologies B.V.RecruitingHereditary AngioedemaGermany, Bulgaria, Croatia, Czechia, France, Hungary, Italy, North Macedonia, Poland, Slovakia, Norway, Slovenia, Sweden
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GlaxoSmithKlineCompleted
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Boehringer IngelheimCompletedHIV InfectionsGermany, Italy, Spain
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Chelsea and Westminster NHS Foundation TrustViiV HealthcareRecruitingHIV Infections | Human Immunodeficiency Virus | Gender IdentityUnited Kingdom, Italy
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Bristol-Myers SquibbPENTA FoundationCompletedHIV InfectionRomania, Belgium, Germany, Italy, Spain, Switzerland, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela