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Clinical Trials on APRT Deficiency in Italy
Total 396 results
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingEndocrine System Diseases | Adult Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Greece, Ukraine, Australia, Canada, France, Israel, Italy, Japan, Malaysia, Poland, Romania, Serbia, Slovakia, Spain, Turkey, United Kingdom, Germany, Korea, Republic of
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ShireCompletedHereditary Angioedema (HAE)United States, Jordan, Italy
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Marinus PharmaceuticalsCompletedCDKL5 Deficiency DisorderUnited States, Australia, France, Israel, Italy, Poland, Russian Federation, United Kingdom
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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ShireTakeda Development Center Americas, Inc.Active, not recruitingHereditary Angioedema (HAE)Germany, Switzerland, Spain, Israel, Italy, Austria, Portugal, Kuwait
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Novartis PharmaceuticalsRecruitingNLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 MutationsSpain, France, United States, Canada, Japan, United Kingdom, Turkey, Czechia, Italy
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Canada, United Kingdom, Germany, Spain, Australia, Hungary, Italy, Austria, North Macedonia, Denmark, Switzerland
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Universitätsklinikum Hamburg-EppendorfCharite University, Berlin, Germany; Deutsches Zentrum für Herz-Kreislauf-Forschung...CompletedIron Deficiency | Systolic Heart FailureGermany, Serbia, Hungary, Italy, Poland, Portugal, Slovenia, Spain
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Quince Therapeutics S.p.A.BiotrialNot yet recruitingAtaxia TelangiectasiaBelgium, United States, Denmark, Germany, Italy, Norway, Poland, Spain, United Kingdom
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Andres J. M. FerreriCompletedHIV | Burkitt's LymphomaItaly
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Boehringer IngelheimCompleted
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Pharming Technologies B.V.CompletedHereditary AngioedemaIsrael, Italy, United States, Czechia, Germany, Hungary, Poland, Romania, Slovakia, North Macedonia
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Cytheris SACompletedHIV Infections | LymphopeniaUnited States, France, Canada, Italy
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CSL BehringCompleted
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ViiV HealthcareCompletedHIV Infection | Infection, Human Immunodeficiency Virus IUnited States, Italy
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BioCryst PharmaceuticalsCompletedHereditary Angioedema (HAE)Austria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Romania, Switzerland, United Kingdom
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ErydelRecruitingAtaxia TelangiectasiaUnited States, Australia, Belgium, Germany, India, Italy, Poland, Spain, Tunisia
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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Agios Pharmaceuticals, Inc.RecruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Germany, Netherlands, Canada, France, Israel, Switzerland, Italy
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Janssen-Cilag S.p.A.CompletedHuman Immunodeficiency Virus (HIV)Italy
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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AEterna ZentarisNovo Nordisk A/SActive, not recruitingGrowth Hormone DeficiencyUnited States, Italy, Turkey, Georgia, Romania, Poland, Armenia, Germany, Serbia, Slovakia, Slovenia
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Teva Branded Pharmaceutical Products R&D, Inc.TerminatedGrowth Hormone DeficiencyUnited States, Austria, Czechia, Greece, Hungary, Italy, Slovakia, Spain
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Catholic University of the Sacred HeartCompleted
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Kedrion S.p.A.RecruitingPrimary Immunodeficiency DiseaseItaly, United States, Portugal, Hungary, Russian Federation, Slovakia
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Radboud University Medical CenterBristol-Myers Squibb; Merck Sharp & Dohme LLC; Gilead Sciences; ViiV Healthcare; Janssen... and other collaboratorsRecruitingHIV InfectionsGermany, United Kingdom, Netherlands, Belgium, Ireland, Italy, Spain
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ASST Fatebenefratelli SaccoElisa Colella, M.D.; Valentina Di Cristo, M.D.; Massimo Galli, M.D.Completed
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ShireJerini AGCompletedHereditary AngioedemaSpain, Argentina, Austria, Denmark, France, Germany, Israel, Italy, Switzerland, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencySpain, United States, Canada, Italy, United Kingdom, Hungary
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ASST Fatebenefratelli SaccoCompleted
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CENTOGENE GmbH RostockCompletedAbdominal Pain | Functional Abdominal PainUnited Kingdom, Germany, Turkey, Poland, Italy, Japan
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Ann-Sofie BackmanThe Swedish Research CouncilRecruitingLynch Syndrome | Colon Cancer | Colon NeoplasmSweden, Denmark, Italy, Poland
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Bulgaria, Canada, Hungary, Israel, Italy, Macedonia, The Former Yugoslav Republic of, Poland, Romania, Serbia, South Africa
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Australia, Austria, Colombia, Germany, Hungary, Israel, Italy, Spain
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Austria, Czechia, Germany, Hungary, Italy, Netherlands, North Macedonia, Poland, United Kingdom
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Japan, Ireland, United Kingdom, France, Italy
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Merck KGaA, Darmstadt, GermanyMerck Serono S.A., GenevaCompletedTurner Syndrome | Idiopathic Growth Hormone DeficiencySpain, France, Canada, United Kingdom, Czech Republic, Argentina, Germany, Italy, Sweden
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rEVO BiologicsCompletedAntithrombin III DeficiencyUnited States, France, United Kingdom, Germany, Canada, Austria, Australia, Italy
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CSL BehringCompletedCommon Variable Immunodeficiency | X-linked Agammaglobulinemia | Autosomal Recessive AgammaglobulinemiaGermany, United Kingdom, France, Italy, Poland, Romania, Spain, Sweden, Switzerland
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ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEFrance, United Kingdom, Germany, United States, Belgium, Hungary, Italy, Canada
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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Germans Trias i Pujol HospitalFundación FLS de Lucha Contra el Sida, las Enfermedades Infecciosas y la...Completed
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Noonan Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Adult Growth Hormone Deficiency | Genetic Disorder | Foetal Growth Problem | Small for Gestational AgeIsrael, Saudi Arabia, Spain, Argentina, Russian Federation, Germany, Netherlands, Italy, Belgium, United Kingdom, Slovenia, Ireland, Sweden, Denmark, Hungary, Finland, Norway, France, Czechia, Lithuania, Luxembourg, Serbia, Switzerland
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Ascendis Pharma Endocrinology Division A/SCompletedEndocrine System Diseases | Pituitary Diseases | Hormones | Growth Hormone Deficiency, Pediatric | hGH (Human Growth Hormone)United States, Armenia, Australia, Belarus, Bulgaria, Georgia, Greece, Italy, New Zealand, Poland, Romania, Russian Federation, Turkey, Ukraine
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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ViiV HealthcareCompletedHIV InfectionsSpain, France, United States, Germany, Italy, South Africa
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Germany, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom