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Clinical Trials on APRT Deficiency in Italy
Total 396 results
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Associazione Italiana per lo Studio del PancreasRecruitingLynch Syndrome | BRCA1 Mutation | BRCA2 Mutation | Familial Pancreatic Cancer | Hereditary Pancreatitis | Peutz-Jeghers Syndrome | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeItaly
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Eli Lilly and CompanyCompletedHypopituitarismUnited States, France, Germany, Italy, Puerto Rico, United Kingdom
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TakedaTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, Spain, Netherlands, Hungary, Italy, Canada, Germany, France, Japan, Poland
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Baxalta now part of ShireAmerican Thrombosis and Hemostasis Network; UDC Rare Bleeding and Clotting...CompletedProtein C DeficiencyUnited States, United Kingdom, Germany, Italy, Netherlands, Austria
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Quince Therapeutics S.p.A.CompletedGenetic Syndrome | Nervous System DiseaseIndia, United States, Australia, Germany, Italy, Norway, Poland, Spain, Tunisia, United Kingdom, Israel, Belgium
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CSL BehringCompletedHereditary Angioedema Types I and IIUnited States, Spain, Australia, Canada, Czechia, Hungary, Israel, Italy, Romania, United Kingdom
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Hoffmann-La RocheTrimerisCompletedHIV InfectionsSwitzerland, Spain, United Kingdom, Germany, Belgium, Australia, Sweden, Italy, Netherlands
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ShireCompletedHereditary Angioedema (HAE)United States, United Kingdom, Germany, Canada, Italy, Jordan, Puerto Rico
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ShireDyax Corp.CompletedHereditary Angioedema (HAE)United States, Canada, Germany, Italy, Jordan, Puerto Rico, United Kingdom
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Novo Nordisk A/SActive, not recruitingGrowth Hormone Deficiency in ChildrenUnited States, Korea, Republic of, United Kingdom, Canada, Russian Federation, India, Spain, Italy, Algeria, Austria, France, Ireland, Israel, Japan, Latvia, Poland, Serbia, Thailand, Ukraine, Germany, Slovenia, Switzerland
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Ascendis Pharma Endocrinology Division A/SCompletedEndocrine System Diseases | Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Turkey, Ukraine, Australia, Canada, Denmark, France, Germany, Greece, Israel, Italy, Japan, Korea, Republic of, Malaysia, Netherlands, New Zealand, Poland, Romania, Serbia, Slovakia, Spain, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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KalVista Pharmaceuticals, Ltd.TerminatedAngioedema, Hereditary, Types I and IIUnited States, Czechia, Germany, Hungary, Italy, North Macedonia, United Kingdom, Australia, Bulgaria, Canada, France, New Zealand, Puerto Rico
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, United Kingdom, Netherlands, Canada, Denmark, France, Italy, Ireland, Thailand
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD)United States, United Kingdom, France, Canada, Czech Republic, Italy, Poland, Switzerland
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medac GmbHSyneos Health; Celerion; Venn Life SciencesCompletedBone Marrow Failure Syndromes | Inborn Errors of Metabolism | Primary Immunodeficiencies | HaemoglobinopathiesPoland, Czechia, Germany, Italy
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ShireTakeda Development Center Americas, Inc.RecruitingHereditary Angioedema (HAE)France, Austria, Australia, Spain, Czechia, Italy, United Kingdom, Germany, Israel, Ireland, Brazil, Denmark, Greece, Sweden
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Boehringer IngelheimTerminatedHIV InfectionsUnited States, Argentina, Brazil, France, Germany, Italy, Spain
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Canada, Netherlands, United Kingdom, France, Italy
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
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NEAT ID FoundationGilead Sciences; Janssen PharmaceuticalsActive, not recruitingHIV/AIDSSpain, Ireland, France, United Kingdom, Germany, Italy, Belgium
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ViiV HealthcareNot yet recruitingHIV InfectionsUnited States, Greece, Italy, Argentina, Poland
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Hoffmann-La RocheCompletedHIV InfectionsFrance, Germany, Spain, Italy, United States, Switzerland, Netherlands, Mexico, Canada, Israel
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsUnited States, Puerto Rico, Italy
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Bristol-Myers SquibbCompletedHIV InfectionsSpain, Italy, United Kingdom, France, Russian Federation, Ireland, Germany, Latvia, Estonia, Portugal
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Catalyst BiosciencesTerminatedFactor VII Deficiency | Hemophilia A With Inhibitor | Glanzmann ThrombastheniaUnited States, India, Italy, Russian Federation, Ukraine
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ViiV HealthcareGlaxoSmithKlineRecruitingHIV InfectionsUnited States, Spain, Canada, Italy, Argentina, Mexico
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ViiV HealthcareGlaxoSmithKlineNo longer availableInfection, Human Immunodeficiency VirusBelgium, Russian Federation, Italy, South Africa, Argentina, Switzerland, Poland
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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Boehringer IngelheimCompletedHIV InfectionsUnited States, Argentina, Brazil, Canada, France, Germany, Italy, Mexico, Puerto Rico, Spain
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Bristol-Myers SquibbCompletedHIV InfectionsUnited States, France, Canada, Italy, Germany
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Boehringer IngelheimTerminatedHIV InfectionsUnited States, Argentina, Brazil, Canada, Germany, Italy, Spain
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ANRS, Emerging Infectious DiseasesNEAT - European AIDS Treatment NetworkCompletedHIV InfectionsIreland, United Kingdom, Netherlands, France, Spain, Greece, Belgium, Germany, Denmark, Sweden, Italy, Portugal, Austria, Hungary, Poland
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Gilead SciencesCompletedHIV InfectionsFrance, Spain, United Kingdom, Belgium, Italy, Germany, Netherlands, Portugal, Austria, Ireland, Poland, Sweden, Switzerland
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TakedaRecruitingMultiple Myeloma | Secondary Immunodeficiency (SID)Greece, Spain, Italy, Romania, Argentina, Czechia, France, Germany, Poland, Sweden, Turkey
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ViiV HealthcareCompletedHIV InfectionUnited States, Spain, Portugal, Italy, Romania, Canada, Netherlands
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Boehringer IngelheimTerminatedHIV InfectionsUnited States, Bahamas, Belgium, Canada, France, Germany, Greece, Italy, Portugal, Puerto Rico, Spain, Thailand
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, Austria, Spain, Switzerland, Germany, Canada, France, United Kingdom, Italy, Finland
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PfizerTerminatedGrowth Hormone DeficiencyGermany, Italy, Spain, Denmark, Czech Republic, Belgium, United Kingdom, Netherlands, Poland, Slovakia, Sweden, France
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
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Bioverativ, a Sanofi companyCompletedFactor VIII DeficiencyUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, France, Germany, Greece, Hungary, Italy, Japan, Korea, Republic of, Mexico, Netherlands, Spain, Taiwan, United Kingdom
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom
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AbbottCompletedHIV InfectionsFrance, Spain, United States, Canada, Poland, Argentina, Brazil, Germany, Italy, Puerto Rico, United Kingdom
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AbbottCompletedHIV InfectionsSpain, United Kingdom, United States, Canada, France, Poland, Argentina, Brazil, Italy, Puerto Rico
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ViiV HealthcareSyneos HealthTerminatedHIV InfectionsGermany, Spain, United States, Canada, France, Italy, South Africa, Argentina, Portugal, Puerto Rico
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ViiV HealthcareGlaxoSmithKlineCompletedInfection, Human Immunodeficiency VirusUnited States, Spain, France, United Kingdom, Chile, Brazil, Italy, Portugal