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Clinical Trials on Alpha Thalassemia
Total 622 results
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Ain Shams UniversityUnknownThalassemia Major | Iron Chelation | Vitamin cEgypt
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Hospices Civils de LyonCompletedChildren With a Deficiency of Alpha-1 AntitrypsinFrance
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Michael Campos, MDCSL BehringCompletedAlpha 1 Antitrypsin DeficiencyUnited States
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CSL BehringCompletedCystic FibrosisBulgaria, Hungary, Poland, United Kingdom
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Novartis PharmaceuticalsCompletedIron Overload After Hematopoietic Stem Cell Transplantation (HSCT) in Patients With Beta-thalassemia MajorTurkey
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Wolfson Medical CenterUnknownPatients With Thalassemia Intermedia, | Congenital Dyserythropoietic Anemia Type I
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Lo.Li.Pharma s.r.lCompletedDysbiosis | Microbiota | Alpha-lactalbuminItaly
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Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
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Timothy OlsonActive, not recruitingSickle Cell Disease | Thalassemia MajorUnited States
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Arog Pharmaceuticals, Inc.AvailableFLT3-ITD Mutation | FLT3/TKD Mutation | PDGFR-Alpha D842V | PDGFRA Gene AmplificationItaly
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityNot yet recruitingAcute Leukemia | Thalassemia MajorChina
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Anemia | Beta ThalassemiaUnited States
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Columbia UniversityActive, not recruitingSickle Cell Disease | Beta ThalassemiaUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedAnemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Hemoglobin SC Disease | Thalassemia MajorUnited States
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Rambam Health Care CampusHadassah Medical Organization; Tel-Aviv Sourasky Medical Center; Soroka University...CompletedGVHD | Bone Marrow Transplant Failure | Alpha 1-AntitrypsinIsrael
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha 1 Antitrypsin Deficiency | AATDUnited States
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Ain Shams UniversityCompletedBeta-thalassemia Major Complicated With DiabetesEgypt
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404 General Military Hospital, LarissaUnknownCoronary Artery Disease | Beta-Thalassemia TraitGreece
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Iron Overload | Hemoglobinopathies | Thalassemia | Beta-Thalassemia | Hemochromatosis | Anemia (Iron-Loading)
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Novartis PharmaceuticalsCompletedIron Overload | Hemosiderosis | Beta-thalassemia Major | Rare AnemiaEgypt, Oman, Saudi Arabia, Syrian Arab Republic, Lebanon
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); N... and other collaboratorsTerminatedLiver Cirrhosis | Alpha-1-antitrypsin DeficiencyUnited States
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Alnylam PharmaceuticalsTerminatedZZ Type Alpha-1 Antitrypsin Deficiency Liver DiseaseUnited Kingdom
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruitingPortal Hypertension | Cholestasis | Liver Fibrosis | Biliary Atresia | Alagille Syndrome | Alpha1 Anti-Trypsin DeficiencyUnited States, Canada
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CSL BehringCompletedEmphysema | Alpha1-proteinase Inhibitor DeficiencyAustralia, Russian Federation, United States, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden, Canada, Czech Republic
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Ente Ospedaliero Ospedali GallieraCompletedPulmonary Arterial Hypertension | Thalassemia Major | Thalassemia IntermediaItaly
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Assiut UniversityCompletedHemolysis | Pulmonary Hypertension | Thalassemia in ChildrenEgypt
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Assiut UniversityNot yet recruitingThalassemia Major
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Ain Shams UniversityRecruitingHCV Infection | Beta Thalassemia MajorEgypt
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Silence Therapeutics plcCompletedNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic Syndrome | Very-Low Risk Myelodysplastic SyndromeThailand, Israel, Jordan, United Kingdom, Germany, Italy, Malaysia
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Azienda Ospedaliero-Universitaria di ModenaRecruitingIron Overload | Hemochromatosis | Thalassemia Major | Thalassemia Intermedia | EndocrinopathyItaly
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CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Israel, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, Lebanon, China, Netherlands
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Beta-ThalassemiaHungary
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Beni-Suef UniversityCompletedThalassemia MajorEgypt
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HaEmek Medical Center, IsraelUnknownThalassemia | Brain Function (Measured by ERP Level)Israel
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University of Campinas, BrazilFundação de Amparo à Pesquisa do Estado de São PauloCompletedIron Overload | ThalassemiaBrazil
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Chiesi Farmaceutici S.p.A.Completed
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Zymenex A/SCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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Zymenex A/SEuropean CommissionCompletedAlpha-MannosidosisBelgium, Denmark, Spain, United Kingdom
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Heidelberg UniversityTerminatedHereditary Emphysema (Alpha 1-antitrypsin Deficiency)Germany
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Grifols Therapeutics LLCCompletedEmphysema | Alpha 1-antitrypsin Deficiency (AATD)United States
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University of Campinas, BrazilFundação de Amparo à Pesquisa do Estado de São PauloCompleted
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Beni-Suef UniversityUniversity of Arizona; Maternity and Children Hospital, Makkah; Beni-Suef Health...CompletedIron Overload | Oxidative Stress | Thalassemia MajorEgypt, Saudi Arabia
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Chiesi Farmaceutici S.p.A.Not yet recruiting
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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Chiesi Farmaceutici S.p.A.Withdrawn