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Clinical Trials on Alpha Thalassemia Major
Total 3388 results
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Chiesi Farmaceutici S.p.A.Completed
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Zymenex A/SCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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Zymenex A/SEuropean CommissionCompletedAlpha-MannosidosisBelgium, Denmark, Spain, United Kingdom
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Heidelberg UniversityTerminatedHereditary Emphysema (Alpha 1-antitrypsin Deficiency)Germany
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Grifols Therapeutics LLCCompletedEmphysema | Alpha 1-antitrypsin Deficiency (AATD)United States
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CelgeneRecruitingBeta-thalassemia | Myelodysplastic Syndromes (MDS) | Myeloproliferative Neoplasm(MPN)-Associated MyelofibrosisUnited States, Japan, Israel, United Kingdom, Turkey, Greece, France, Australia, Belgium, Bulgaria, Canada, Germany, Italy, Malaysia, Spain, Sweden, Taiwan, Thailand, Tunisia, China, Lebanon, Netherlands
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Beta-ThalassemiaHungary
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HaEmek Medical Center, IsraelUnknownThalassemia | Brain Function (Measured by ERP Level)Israel
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Chiesi Farmaceutici S.p.A.Not yet recruiting
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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Chiesi Farmaceutici S.p.A.Withdrawn
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Chiesi Farmaceutici S.p.A.CompletedAlpha-MannosidosisFrance
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Zymenex A/SEuropean CommissionCompletedA Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-MannosidosisAlpha-MannosidosisDenmark, United Kingdom, France, Germany, Poland
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Sangamo TherapeuticsEnrolling by invitationBlood and Lymphatic DiseasesUnited States
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University Hospital of FerraraRecruiting
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Tanta UniversityCompletedHepatitis C | Beta-ThalassemiaEgypt
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University of ThessalyCompletedDiabetes Mellitus, Type 2 | Insulin Resistance | PreDiabetes | Beta-ThalassemiaGreece
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Grifols Therapeutics LLCActive, not recruitingPulmonary Emphysema in Alpha-1 PI DeficiencyUnited States, Australia, Denmark, New Zealand, Estonia, Poland, Russian Federation, Sweden, Brazil, Canada, France, Finland
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Schön Klinik Berchtesgadener LandGrifols Therapeutics LLC; Alpha-1 FoundationCompletedChronic Obstructive Pulmonary Disease | Alpha-1-antitrypsin-deficiencyGermany
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Bristol-Myers SquibbRecruitingMyelodysplastic Syndrome | Beta ThalassemiaKorea, Republic of
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Xiang Guang-daCompletedCytokines | Endothelial Function | Contrast Agent | Apoptosis of Endothelial Progenitor Cell | Free Radical | Alpha-lipoic AcidChina
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Grifols Therapeutics LLCEnrolling by invitationPulmonary Emphysema in Alpha-1 Antitrypsin DeficiencyUnited States, New Zealand, Denmark, Australia, Finland, Estonia, Canada, Poland, Russian Federation, Sweden, France
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Ain Shams UniversityUnknownDNA Damage | Endocrine Disease | Fertility Decreased MaleEgypt
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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HaEmek Medical Center, IsraelUnknownIron Deficiency | ThalassemiaIsrael
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University Hospital, SaarlandWithdrawnEmphysema | Chronic Obstructive Lung Disease | Alpha-1-Antitrypsin DeficiencyDenmark, Germany
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health Clinical Center (CC); National Cancer Institute...RecruitingStem Cell Transplantation | Sickle Cell Disease | Thalassemia | Graft vs Host DiseaseUnited States
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
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Assiut UniversityUnknown
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Impatients N.V. trading as myTomorrowsKamada, Ltd.No longer availableAlpha 1-Antitrypsin Deficiency | Graft Vs Host Disease | Graft-versus-host-disease | Acute-graft-versus-host Disease | Steroid Refractory Acute Graft Versus Host Disease | Alpha-1 Proteinase Inhibitor | Alpha-1 Protease Inhibitor Deficiency | Acute Graft-Versus-Host Reaction Following Bone Marrow...
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Bangabandhu Sheikh Mujib Medical University, Dhaka...CompletedTransfusion-dependent ThalassemiaBangladesh
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Terumo BCTbioUnited States Department of Defense; U.S. Army Medical Research and Development... and other collaboratorsTerminatedTransfusion Dependent ThalassemiaUnited States, Israel, Italy, Turkey
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Universiti Kebangsaan Malaysia Medical CentreInstitue of Microengineering and Nanoelectronics (IMEN), Universiti Kebangsaan... and other collaboratorsCompletedThalassemia in ChildrenMalaysia
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Novartis PharmaceuticalsWithdrawnThalassemia (Transfusion Delendent)
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Washington University School of MedicineHealthCore-NERI; Pediatric Blood and Marrow Transplant ConsortiumCompletedSevere ThalassemiaUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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Grifols Therapeutics LLCTerminatedCOVID-19United States, Brazil, Chile, Colombia, Mexico
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Wave Life Sciences Ltd.Not yet recruiting
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyUnited Kingdom
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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Alpha-1 FoundationRecruiting
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CSL BehringActive, not recruitingAlpha-1 Antitrypsin DeficiencyFrance
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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Laboratoire français de Fractionnement et de BiotechnologiesCompletedAlpha 1-Antitrypsin Deficiency