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Clinical Trials on Alpha-1 AT Deficiency in Korea, Democratic People's Republic of
Total 47 results
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CSL BehringRecruitingAcute-graft-versus-host DiseaseUnited States, Korea, Republic of, Spain, Australia, Germany, Italy, Turkey, Japan
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Daewoong Pharmaceutical Co. LTD.CompletedGrowth Hormone DeficiencyKorea, Republic of
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Genexine, Inc.CompletedAdult Growth Hormone DeficiencyKorea, Republic of
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Helixmith Co., Ltd.UnknownChronic Granulomatous DiseaseKorea, Republic of
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Kyowa Kirin Korea Co., Ltd.RecruitingFGF23-related Hypophosphataemic Rickets and OsteomalaciaKorea, Republic of
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Seoul National University HospitalRecruitingDuchenne Muscular Dystrophy | Scoliosis Neuromuscular | Lordosis LumbarKorea, Republic of
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan, Korea, Republic of
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The Korean Society of Pediatric Hematology OncologyCompletedWiskott-Aldrich SyndromeKorea, Republic of
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Cellatoz Therapeutics, IncActive, not recruitingCharcot Marie Tooth Disease, Type 1Korea, Republic of
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Seoul National University HospitalUnknownChronic Granulomatous DiseaseKorea, Republic of
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LG ChemRecruitingGrowth Hormone Deficiency | Chronic Renal Failure | Turner Syndrome | Small for Gestational Age | Idiopathic Short StatureKorea, Republic of
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Kyowa Kirin Co., Ltd.CompletedTumor-Induced Osteomalacia or Epidermal Nevus SyndromeJapan, Korea, Republic of
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Dong-A ST Co., Ltd.RecruitingGrowth Hormone Deficiency | Turner Syndrome | Small for Gestational Age | Idiopathic Short StatureKorea, Republic of
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LG Life SciencesCompletedGrowth Hormone Deficiency | Chronic Renal Failure | Turner Syndrome | Infant, Small for Gestational Age | Short Stature, IdiopathicKorea, Republic of
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Kyowa Kirin Co., Ltd.CompletedA Study of KRN23 in Adult and Pediatric Patients With X-linked Hypophosphatemic Rickets/OsteomalaciaXLHJapan, Korea, Republic of
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Shahid Beheshti UniversityUnknownMaxillary DeficiencyIran, Islamic Republic of
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Shahid Beheshti University of Medical SciencesCompletedMaxillary DeficiencyIran, Islamic Republic of
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AryoGen Pharmed Co.CompletedFactor VII DeficiencyIran, Islamic Republic of
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OctapharmaCompletedCongenital Fibrinogen DeficiencyIndia, Iran, Islamic Republic of, Lebanon
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CinnagenCompletedMucopolysaccharidosis Type 1Iran, Islamic Republic of
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Shahid Beheshti University of Medical SciencesCompletedCkd-MbdIran, Islamic Republic of
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | HAEFrance, North Macedonia, Poland, Korea, Republic of, Slovakia, South Africa, Czechia
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AryoGen Pharmed Co.CompletedFactor VII Deficiency | Hemophilia A With Inhibitor | Hemophilia B With Inhibitor | Glanzmann's ThrombastheniaIran, Islamic Republic of
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OctapharmaCompletedCongenital Fibrinogen Deficiency | AfibrinogenemiaIran, Islamic Republic of, United States, Bulgaria, India, Switzerland, United Kingdom
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
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OctapharmaCompletedCongenital Fibrinogen DeficiencyUnited States, Bulgaria, India, Iran, Islamic Republic of, Lebanon, Russian Federation, Saudi Arabia, Turkey, United Kingdom
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Japan, Ireland, United Kingdom, France, Italy
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Canada, Czechia, Italy, Macedonia, The Former Yugoslav Republic of, Romania, Serbia
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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Ascendis Pharma Endocrinology Division A/SActive, not recruitingEndocrine System Diseases | Adult Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Greece, Ukraine, Australia, Canada, France, Israel, Italy, Japan, Malaysia, Poland, Romania, Serbia, Slovakia, Spain, Turkey, United Kingdom, Germany, Korea, Republic of
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OPKO Health, Inc.Active, not recruitingSafety and Efficacy Phase 3 Study of Long-acting hGH (MOD-4023) in Growth Hormone Deficient ChildrenPediatric Growth Hormone DeficiencyIsrael, United States, India, Korea, Republic of, Australia, Taiwan, Spain, Argentina, Belarus, Bulgaria, Canada, Colombia, Georgia, Greece, Mexico, New Zealand, Poland, Russian Federation, Ukraine, United Kingdom
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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Gilead SciencesActive, not recruitingHIV-1-infectionUnited States, Spain, France, Taiwan, Japan, Thailand, Dominican Republic, Germany, Canada, Italy, South Africa
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CSL BehringCompletedHereditary AngioedemaBulgaria, United States, Poland, Spain, Hungary, United Kingdom, Russian Federation, Macedonia, The Former Yugoslav Republic of, Argentina, Australia, Canada, Czech Republic, Israel, Romania, Sweden
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Bioverativ, a Sanofi companyCompletedFactor VIII DeficiencyUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, France, Germany, Greece, Hungary, Italy, Japan, Korea, Republic of, Mexico, Netherlands, Spain, Taiwan, United Kingdom
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Bulgaria, Canada, Hungary, Israel, Italy, Macedonia, The Former Yugoslav Republic of, Poland, Romania, Serbia, South Africa
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Spain, Japan, Canada, United Kingdom, Korea, Republic of, Ireland, Thailand, Italy, Turkey, Denmark, Brazil, France, Germany, Netherlands, Switzerland
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Agios Pharmaceuticals, Inc.RecruitingPyruvate Kinase DeficiencyUnited States, Germany, Spain, Italy, United Kingdom, Czechia, France, Canada, Korea, Republic of, Netherlands, Turkey, Portugal, Denmark, Ireland, Switzerland, Thailand
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Novo Nordisk A/SActive, not recruitingGrowth Hormone Deficiency in ChildrenUnited States, Korea, Republic of, United Kingdom, Canada, Russian Federation, India, Spain, Italy, Algeria, Austria, France, Ireland, Israel, Japan, Latvia, Poland, Serbia, Thailand, Ukraine, Germany, Slovenia, Switzerland
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, Spain, Switzerland, Turkey, Germany, France, United Kingdom, Japan, Netherlands, Brazil, Canada, Czechia, Denmark, Italy, Korea, Republic of, Thailand
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Ascendis Pharma Endocrinology Division A/SCompletedEndocrine System Diseases | Growth Hormone Deficiency | Hormone DeficiencyUnited States, Armenia, Georgia, Turkey, Ukraine, Australia, Canada, Denmark, France, Germany, Greece, Israel, Italy, Japan, Korea, Republic of, Malaysia, Netherlands, New Zealand, Poland, Romania, Serbia, Slovakia, Spain, United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan