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Clinical Trials on Alpha-1 AT Deficiency in Korea, Republic of
Total 165 results
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Thomayer University HospitalMasaryk UniversityRecruiting
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Grifols Therapeutics LLCRecruiting
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CSL BehringCompletedEmphysema | Alpha 1-proteinase Inhibitor DeficiencyAustralia, Canada, Czech Republic, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden
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Inhibrx, Inc.CompletedAlpha-1 Antitrypsin Deficiency | AATDUnited States, New Zealand, United Kingdom
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CSL BehringCompletedEmphysema | Alpha1-proteinase Inhibitor DeficiencyAustralia, Russian Federation, United States, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden, Canada, Czech Republic
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CSL BehringRecruitingAcute-graft-versus-host DiseaseUnited States, Korea, Republic of, Spain, Australia, Germany, Italy, Turkey, Japan
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Daewoong Pharmaceutical Co. LTD.CompletedGrowth Hormone DeficiencyKorea, Republic of
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Genexine, Inc.CompletedAdult Growth Hormone DeficiencyKorea, Republic of
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Helixmith Co., Ltd.UnknownChronic Granulomatous DiseaseKorea, Republic of
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Kyowa Kirin Korea Co., Ltd.RecruitingFGF23-related Hypophosphataemic Rickets and OsteomalaciaKorea, Republic of
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Seoul National University HospitalRecruitingDuchenne Muscular Dystrophy | Scoliosis Neuromuscular | Lordosis LumbarKorea, Republic of
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan, Korea, Republic of
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The Korean Society of Pediatric Hematology OncologyCompletedWiskott-Aldrich SyndromeKorea, Republic of
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Cellatoz Therapeutics, IncActive, not recruitingCharcot Marie Tooth Disease, Type 1Korea, Republic of
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Seoul National University HospitalUnknownChronic Granulomatous DiseaseKorea, Republic of
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LG ChemRecruitingGrowth Hormone Deficiency | Chronic Renal Failure | Turner Syndrome | Small for Gestational Age | Idiopathic Short StatureKorea, Republic of
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Kyowa Kirin Co., Ltd.CompletedTumor-Induced Osteomalacia or Epidermal Nevus SyndromeJapan, Korea, Republic of
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Dong-A ST Co., Ltd.RecruitingGrowth Hormone Deficiency | Turner Syndrome | Small for Gestational Age | Idiopathic Short StatureKorea, Republic of
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LG Life SciencesCompletedGrowth Hormone Deficiency | Chronic Renal Failure | Turner Syndrome | Infant, Small for Gestational Age | Short Stature, IdiopathicKorea, Republic of
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Kyowa Kirin Co., Ltd.CompletedA Study of KRN23 in Adult and Pediatric Patients With X-linked Hypophosphatemic Rickets/OsteomalaciaXLHJapan, Korea, Republic of
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Shahid Beheshti UniversityUnknownMaxillary DeficiencyIran, Islamic Republic of
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Shahid Beheshti University of Medical SciencesCompletedMaxillary DeficiencyIran, Islamic Republic of
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Baylor College of MedicineChildren's National Research InstituteRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Carbamyl Phosphate Synthetase Deficiency | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS Deficiency | NAGS DeficiencyUnited States
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AryoGen Pharmed Co.CompletedFactor VII DeficiencyIran, Islamic Republic of
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OctapharmaCompletedCongenital Fibrinogen DeficiencyIndia, Iran, Islamic Republic of, Lebanon
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CinnagenCompletedMucopolysaccharidosis Type 1Iran, Islamic Republic of
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Shahid Beheshti University of Medical SciencesCompletedCkd-MbdIran, Islamic Republic of
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | HAEFrance, North Macedonia, Poland, Korea, Republic of, Slovakia, South Africa, Czechia
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AryoGen Pharmed Co.CompletedFactor VII Deficiency | Hemophilia A With Inhibitor | Hemophilia B With Inhibitor | Glanzmann's ThrombastheniaIran, Islamic Republic of
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Baylor College of MedicineChildren's Hospital of Philadelphia; Children's Hospital Colorado; Seattle Children... and other collaboratorsRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS DeficiencyUnited States
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OctapharmaCompletedCongenital Fibrinogen Deficiency | AfibrinogenemiaIran, Islamic Republic of, United States, Bulgaria, India, Switzerland, United Kingdom
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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OctapharmaCompletedCongenital Fibrinogen DeficiencyUnited States, Bulgaria, India, Iran, Islamic Republic of, Lebanon, Russian Federation, Saudi Arabia, Turkey, United Kingdom
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Peking UniversityNational Natural Science Foundation of China; Institute of reproductive and...CompletedHyperhomocysteinemiaChina
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Nicholas Ah MewIcahn School of Medicine at Mount Sinai; Boston Children's HospitalRecruitingN-acetylglutamate Synthase (NAGS) DeficiencyUnited States
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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Janssen Sciences Ireland UCCompletedImmunodeficiency Virus Type 1, HumanUnited States, France, Poland, United Kingdom, Belgium, Germany, Spain, Canada, Russian Federation, Puerto Rico
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Japan, Ireland, United Kingdom, France, Italy
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National Institute of Allergy and Infectious Diseases...National Institute of Mental Health (NIMH)RecruitingPrimary Immunodeficiency | Atopy | Autoinflammation | AutoimmunityUnited States
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Canada, Czechia, Italy, Macedonia, The Former Yugoslav Republic of, Romania, Serbia
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde | Dehydrogenase Deficiency | DiseasesUnited States
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National Institute of Neurological Disorders and...CompletedSuccinic Semialdehyde Dehydrogenase Deficiency | SSADH DeficiencyUnited States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedChronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Leukocyte Adhesion Deficiency | Chronic Active Epstein-Barr Virus Infection | HIGM-1 | IPEXUnited States, Canada
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Damascus UniversityCompletedClass II Division 1 Malocclusion | Protrusion, Incisor | Maxillary PrognathismSyrian Arab Republic
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ShireCompletedAngioedemaUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingPrimary Immunodeficiency DisordersUnited States